JP2024529899A5 - - Google Patents

Info

Publication number
JP2024529899A5
JP2024529899A5 JP2024502462A JP2024502462A JP2024529899A5 JP 2024529899 A5 JP2024529899 A5 JP 2024529899A5 JP 2024502462 A JP2024502462 A JP 2024502462A JP 2024502462 A JP2024502462 A JP 2024502462A JP 2024529899 A5 JP2024529899 A5 JP 2024529899A5
Authority
JP
Japan
Prior art keywords
glycero
rna
guide
guide rna
phosphocholine
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024502462A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024529899A (ja
Filing date
Publication date
Priority claimed from PCT/US2021/042100 external-priority patent/WO2022016121A2/en
Application filed filed Critical
Priority claimed from PCT/US2022/037490 external-priority patent/WO2023288135A2/en
Publication of JP2024529899A publication Critical patent/JP2024529899A/ja
Publication of JP2024529899A5 publication Critical patent/JP2024529899A5/ja
Pending legal-status Critical Current

Links

JP2024502462A 2021-07-16 2022-07-18 関節機能を改善する遺伝子編集 Pending JP2024529899A (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
USPCT/US2021/042100 2021-07-16
PCT/US2021/042100 WO2022016121A2 (en) 2020-07-16 2021-07-16 Gene editing to improve joint function
US202163222972P 2021-07-17 2021-07-17
US63/222,972 2021-07-17
US202263300822P 2022-01-19 2022-01-19
US63/300,822 2022-01-19
US202263326571P 2022-04-01 2022-04-01
US63/326,571 2022-04-01
PCT/US2022/037490 WO2023288135A2 (en) 2021-07-16 2022-07-18 Gene editing to improve joint function

Publications (2)

Publication Number Publication Date
JP2024529899A JP2024529899A (ja) 2024-08-14
JP2024529899A5 true JP2024529899A5 (enExample) 2025-07-24

Family

ID=84919676

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024502462A Pending JP2024529899A (ja) 2021-07-16 2022-07-18 関節機能を改善する遺伝子編集

Country Status (10)

Country Link
US (1) US20230235321A1 (enExample)
EP (1) EP4370165A4 (enExample)
JP (1) JP2024529899A (enExample)
KR (1) KR20240095529A (enExample)
CN (1) CN119110732A (enExample)
AU (1) AU2022311936A1 (enExample)
CA (1) CA3226089A1 (enExample)
IL (1) IL310118A (enExample)
MX (1) MX2024000821A (enExample)
WO (1) WO2023288135A2 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024215959A2 (en) * 2023-04-11 2024-10-17 Orthobio Therapeutics, Inc. Lipid nanoparticles for gene editing systems

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20050282198A1 (en) * 1997-05-29 2005-12-22 Interleukin Genetics, Inc. Diagnostics and therapeutics for diseases associated with an IL-1 inflammatory haplotype
EP3230452B1 (en) * 2014-12-12 2025-06-11 The Broad Institute, Inc. Dead guides for crispr transcription factors
EP3374494A4 (en) * 2015-11-11 2019-05-01 Coda Biotherapeutics, Inc. CRISPR COMPOSITIONS AND METHODS OF USE THEREOF FOR GENE THERAPY
ES3030658T3 (en) * 2016-03-30 2025-07-01 Intellia Therapeutics Inc Lipid nanoparticle formulations for crispr/cas components
US11807850B2 (en) * 2017-12-06 2023-11-07 Klogenix Llc Compositions and methods for modulating gene expression
CN112533942A (zh) * 2018-06-01 2021-03-19 华盛顿大学 嵌合抗原受体细胞疗法中细胞因子释放综合征的抑制
CA3121191A1 (en) * 2018-11-28 2020-06-04 Crispr Therapeutics Ag Optimized mrna encoding cas9 for use in lnps
WO2020150633A1 (en) * 2019-01-18 2020-07-23 Orthobio Therapeutics, Inc. Gene editing to improve joint function
CA3144356A1 (en) * 2019-06-21 2020-12-24 Function Oncology, Inc. A genetic pharmacopeia for comprehensive functional profiling of human cancers

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