JP2024528540A5 - - Google Patents

Info

Publication number
JP2024528540A5
JP2024528540A5 JP2023580744A JP2023580744A JP2024528540A5 JP 2024528540 A5 JP2024528540 A5 JP 2024528540A5 JP 2023580744 A JP2023580744 A JP 2023580744A JP 2023580744 A JP2023580744 A JP 2023580744A JP 2024528540 A5 JP2024528540 A5 JP 2024528540A5
Authority
JP
Japan
Prior art keywords
relative
item
rna
mismatch
polynucleotide according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023580744A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024528540A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/035320 external-priority patent/WO2023278449A1/en
Publication of JP2024528540A publication Critical patent/JP2024528540A/ja
Publication of JP2024528540A5 publication Critical patent/JP2024528540A5/ja
Pending legal-status Critical Current

Links

JP2023580744A 2021-06-29 2022-06-28 遺伝子操作されたガイドrna及びポリヌクレオチド Pending JP2024528540A (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US202163216178P 2021-06-29 2021-06-29
US63/216,178 2021-06-29
US202163277701P 2021-11-10 2021-11-10
US63/277,701 2021-11-10
US202263303680P 2022-01-27 2022-01-27
US63/303,680 2022-01-27
US202263345059P 2022-05-24 2022-05-24
US63/345,059 2022-05-24
PCT/US2022/035320 WO2023278449A1 (en) 2021-06-29 2022-06-28 Engineered guide rnas and polynucleotides

Publications (2)

Publication Number Publication Date
JP2024528540A JP2024528540A (ja) 2024-07-30
JP2024528540A5 true JP2024528540A5 (enExample) 2025-08-07

Family

ID=82701937

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023580744A Pending JP2024528540A (ja) 2021-06-29 2022-06-28 遺伝子操作されたガイドrna及びポリヌクレオチド

Country Status (6)

Country Link
US (1) US20240271139A1 (enExample)
EP (1) EP4363579A1 (enExample)
JP (1) JP2024528540A (enExample)
AU (1) AU2022301997A1 (enExample)
CA (1) CA3223109A1 (enExample)
WO (1) WO2023278449A1 (enExample)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4423274A2 (en) * 2021-10-26 2024-09-04 Shape Therapeutics Inc. Rna-editing compositions and methods of use
AU2023407358A1 (en) * 2022-12-23 2025-06-26 Shape Therapeutics Inc. Engineered guide rnas and polynucleotides
WO2026006334A1 (en) * 2024-06-25 2026-01-02 Shape Therapeutics Inc. Dux4 vectors and engineered guide rnas
WO2026006483A1 (en) * 2024-06-25 2026-01-02 Shape Therapeutics Inc. Snca vectors and engineered guide rnas

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2020395113A1 (en) * 2019-12-02 2022-06-09 Shape Therapeutics Inc. Therapeutic editing
CA3177380A1 (en) * 2020-05-26 2021-12-02 Shape Therapeutics Inc. Compositions and methods for modifying target rnas
JP2024500279A (ja) * 2020-11-11 2024-01-09 シェイプ セラピューティクス インコーポレイテッド Rna編集組成物及び使用方法
EP4256050A4 (en) * 2020-12-01 2025-01-22 Shape Therapeutics Inc. High throughput rna-editing screening methods

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