JP2024516164A5 - - Google Patents

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Publication number
JP2024516164A5
JP2024516164A5 JP2023564557A JP2023564557A JP2024516164A5 JP 2024516164 A5 JP2024516164 A5 JP 2024516164A5 JP 2023564557 A JP2023564557 A JP 2023564557A JP 2023564557 A JP2023564557 A JP 2023564557A JP 2024516164 A5 JP2024516164 A5 JP 2024516164A5
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JP
Japan
Prior art keywords
formula
substituted
independently
composition according
alkyl
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Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023564557A
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English (en)
Japanese (ja)
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JP2024516164A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/026001 external-priority patent/WO2022226344A1/en
Publication of JP2024516164A publication Critical patent/JP2024516164A/ja
Publication of JP2024516164A5 publication Critical patent/JP2024516164A5/ja
Pending legal-status Critical Current

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JP2023564557A 2021-04-22 2022-04-22 正確なインビボhdr介在性遺伝子編集を可能にするオールインワンデンドリマーベース脂質ナノ粒子 Pending JP2024516164A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163178453P 2021-04-22 2021-04-22
US63/178,453 2021-04-22
PCT/US2022/026001 WO2022226344A1 (en) 2021-04-22 2022-04-22 All-in-one dendrimer-based lipid nanoparticles enable precise hdr-mediated gene editing in vivo

Publications (2)

Publication Number Publication Date
JP2024516164A JP2024516164A (ja) 2024-04-12
JP2024516164A5 true JP2024516164A5 (https=) 2025-04-23

Family

ID=83722696

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023564557A Pending JP2024516164A (ja) 2021-04-22 2022-04-22 正確なインビボhdr介在性遺伝子編集を可能にするオールインワンデンドリマーベース脂質ナノ粒子

Country Status (8)

Country Link
US (1) US20240207442A1 (https=)
EP (1) EP4326886A4 (https=)
JP (1) JP2024516164A (https=)
CN (1) CN117500933A (https=)
AU (1) AU2022262422A1 (https=)
CA (1) CA3215509A1 (https=)
IL (1) IL307874A (https=)
WO (1) WO2022226344A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2017048789A1 (en) * 2015-09-14 2017-03-23 The Board Of Regents Of The University Of Texas System Lipocationic dendrimers and uses thereof
JP2024511463A (ja) 2021-03-22 2024-03-13 リコード セラピューティクス,インク. 細胞への標的送達のための組成物および方法
EP4547230A1 (en) * 2022-06-29 2025-05-07 Juno Therapeutics, Inc. Lipid nanoparticles for delivery of nucleic acids
US12364773B2 (en) 2023-12-01 2025-07-22 Recode Therapeutics, Inc. Lipid nanoparticle compositions and uses thereof
CN120754284A (zh) * 2025-07-30 2025-10-10 中国医学科学院基础医学研究所 一种用于肝脏靶向联合递送CRISPR-Cas9系统和单链DNA修复模板的脂质纳米颗粒

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JP2024511463A (ja) * 2021-03-22 2024-03-13 リコード セラピューティクス,インク. 細胞への標的送達のための組成物および方法
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