JP2024514962A5 - - Google Patents
Info
- Publication number
- JP2024514962A5 JP2024514962A5 JP2023565307A JP2023565307A JP2024514962A5 JP 2024514962 A5 JP2024514962 A5 JP 2024514962A5 JP 2023565307 A JP2023565307 A JP 2023565307A JP 2023565307 A JP2023565307 A JP 2023565307A JP 2024514962 A5 JP2024514962 A5 JP 2024514962A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- use according
- sequence
- optionally
- aavrh74
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163179097P | 2021-04-23 | 2021-04-23 | |
| US63/179,097 | 2021-04-23 | ||
| US202263327410P | 2022-04-05 | 2022-04-05 | |
| US63/327,410 | 2022-04-05 | ||
| PCT/US2022/025916 WO2022226289A2 (en) | 2021-04-23 | 2022-04-22 | Aavrh74 vectors for gene therapy of muscular dystrophies |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024514962A JP2024514962A (ja) | 2024-04-03 |
| JP2024514962A5 true JP2024514962A5 (https=) | 2025-05-01 |
Family
ID=81648417
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023565307A Pending JP2024514962A (ja) | 2021-04-23 | 2022-04-22 | 筋ジストロフィーの遺伝子治療のためのａａｖｒｈ７４ベクター |
Country Status (13)
| Country | Link |
|---|---|
| US (2) | US20240181083A1 (https=) |
| EP (1) | EP4326857A2 (https=) |
| JP (1) | JP2024514962A (https=) |
| KR (1) | KR20240000542A (https=) |
| AU (1) | AU2022262407A1 (https=) |
| BR (1) | BR112023021495A2 (https=) |
| CA (1) | CA3217649A1 (https=) |
| CL (2) | CL2023003102A1 (https=) |
| CO (1) | CO2023015911A2 (https=) |
| IL (1) | IL307881A (https=) |
| MX (1) | MX2023012509A (https=) |
| TW (1) | TW202304954A (https=) |
| WO (1) | WO2022226289A2 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2714007T3 (es) | 2007-04-09 | 2019-05-24 | Univ Florida | Composiciones de vectores rAAV que tienen proteínas de la cápside modificadas en tirosina y métodos para su uso |
| US10294281B2 (en) | 2012-05-15 | 2019-05-21 | University Of Florida Research Foundation, Incorporated | High-transduction-efficiency rAAV vectors, compositions, and methods of use |
| US12358954B2 (en) | 2012-05-15 | 2025-07-15 | University Of Florida Research Foundation, Incorporated | Capsid-modified rAAV vector compositions and methods therefor |
| KR20240095539A (ko) | 2021-10-08 | 2024-06-25 | 디노 테라퓨틱스, 인코포레이티드 | 캡시드 변이체 및 이의 사용 방법 |
| WO2024184781A1 (en) * | 2023-03-03 | 2024-09-12 | Universitat Heidelberg | Engineered aav capsids |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| NZ701693A (en) * | 2012-04-18 | 2017-02-24 | The Children’S Hospital Of Philadelphia | Composition and methods for highly efficient gene transfer using aav capsid variants |
| US10900053B2 (en) | 2014-11-21 | 2021-01-26 | University Of Florida Research Foundation, Incorporated | Genome-modified recombinant adeno-associated virus vectors |
| WO2021030764A1 (en) * | 2019-08-14 | 2021-02-18 | University Of Florida Research Foundation, Incorporated | Aav capsid variants for gene therapy |
-
2022
- 2022-04-22 JP JP2023565307A patent/JP2024514962A/ja active Pending
- 2022-04-22 BR BR112023021495A patent/BR112023021495A2/pt unknown
- 2022-04-22 TW TW111115475A patent/TW202304954A/zh unknown
- 2022-04-22 IL IL307881A patent/IL307881A/en unknown
- 2022-04-22 MX MX2023012509A patent/MX2023012509A/es unknown
- 2022-04-22 AU AU2022262407A patent/AU2022262407A1/en active Pending
- 2022-04-22 CA CA3217649A patent/CA3217649A1/en active Pending
- 2022-04-22 WO PCT/US2022/025916 patent/WO2022226289A2/en not_active Ceased
- 2022-04-22 US US18/287,711 patent/US20240181083A1/en active Pending
- 2022-04-22 US US17/727,007 patent/US20220347317A1/en not_active Abandoned
- 2022-04-22 KR KR1020237039756A patent/KR20240000542A/ko active Pending
- 2022-04-22 EP EP22723290.7A patent/EP4326857A2/en active Pending
-
2023
- 2023-10-18 CL CL2023003102A patent/CL2023003102A1/es unknown
- 2023-11-22 CO CONC2023/0015911A patent/CO2023015911A2/es unknown
-
2024
- 2024-08-27 CL CL2024002556A patent/CL2024002556A1/es unknown
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