JP2024514110A5 - - Google Patents

Info

Publication number
JP2024514110A5
JP2024514110A5 JP2023561167A JP2023561167A JP2024514110A5 JP 2024514110 A5 JP2024514110 A5 JP 2024514110A5 JP 2023561167 A JP2023561167 A JP 2023561167A JP 2023561167 A JP2023561167 A JP 2023561167A JP 2024514110 A5 JP2024514110 A5 JP 2024514110A5
Authority
JP
Japan
Prior art keywords
promoter
seq
nucleic acid
sequence
capsid protein
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023561167A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024514110A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/024478 external-priority patent/WO2022221320A1/en
Publication of JP2024514110A publication Critical patent/JP2024514110A/ja
Publication of JP2024514110A5 publication Critical patent/JP2024514110A5/ja
Pending legal-status Critical Current

Links

JP2023561167A 2021-04-12 2022-04-12 不整脈原性右心室心筋症に対する遺伝子療法 Pending JP2024514110A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163173527P 2021-04-12 2021-04-12
US63/173,527 2021-04-12
PCT/US2022/024478 WO2022221320A1 (en) 2021-04-12 2022-04-12 Gene therapy for arrhythmogenic right ventricular cardiomyopathy

Publications (2)

Publication Number Publication Date
JP2024514110A JP2024514110A (ja) 2024-03-28
JP2024514110A5 true JP2024514110A5 (enExample) 2025-04-11

Family

ID=83640995

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023561167A Pending JP2024514110A (ja) 2021-04-12 2022-04-12 不整脈原性右心室心筋症に対する遺伝子療法

Country Status (12)

Country Link
US (1) US20240216541A1 (enExample)
EP (1) EP4323534A4 (enExample)
JP (1) JP2024514110A (enExample)
KR (1) KR20230170686A (enExample)
CN (1) CN117178057A (enExample)
AU (1) AU2022258329A1 (enExample)
BR (1) BR112023021037A2 (enExample)
CA (1) CA3213231A1 (enExample)
CO (1) CO2023014900A2 (enExample)
IL (1) IL307506A (enExample)
MX (1) MX2023011875A (enExample)
WO (1) WO2022221320A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR20230043869A (ko) 2020-08-07 2023-03-31 스페이스크래프트 세븐, 엘엘씨 Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20040142325A1 (en) * 2001-09-14 2004-07-22 Liat Mintz Methods and systems for annotating biomolecular sequences
US7960100B1 (en) * 2004-04-30 2011-06-14 Celera Corporation Colon cancer targets and uses thereof
US20070072175A1 (en) * 2005-05-13 2007-03-29 Biogen Idec Ma Inc. Nucleotide array containing polynucleotide probes complementary to, or fragments of, cynomolgus monkey genes and the use thereof
WO2013151665A2 (en) * 2012-04-02 2013-10-10 modeRNA Therapeutics Modified polynucleotides for the production of proteins associated with human disease
AU2013293270B2 (en) * 2012-07-25 2018-08-16 Massachusetts Institute Of Technology Inducible DNA binding proteins and genome perturbation tools and applications thereof
TWI897882B (zh) * 2019-09-20 2025-09-21 英商Ucl商業有限責任公司 右心室心律失常性心肌病之基因療法組合物及治療
KR20230043869A (ko) * 2020-08-07 2023-03-31 스페이스크래프트 세븐, 엘엘씨 Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법

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