JP2023544702A5 - - Google Patents

Info

Publication number
JP2023544702A5
JP2023544702A5 JP2023519419A JP2023519419A JP2023544702A5 JP 2023544702 A5 JP2023544702 A5 JP 2023544702A5 JP 2023519419 A JP2023519419 A JP 2023519419A JP 2023519419 A JP2023519419 A JP 2023519419A JP 2023544702 A5 JP2023544702 A5 JP 2023544702A5
Authority
JP
Japan
Prior art keywords
nucleic acid
recombinant nucleic
acid according
vector
tcf4
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2023519419A
Other languages
English (en)
Japanese (ja)
Other versions
JP7786750B2 (ja
JP2023544702A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/052987 external-priority patent/WO2022072709A1/en
Publication of JP2023544702A publication Critical patent/JP2023544702A/ja
Publication of JP2023544702A5 publication Critical patent/JP2023544702A5/ja
Application granted granted Critical
Publication of JP7786750B2 publication Critical patent/JP7786750B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2023519419A 2020-09-30 2021-09-30 Tcf4遺伝子発現を調節するため、およびピット・ホプキンス症候群を治療するための組成物および方法 Active JP7786750B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063085878P 2020-09-30 2020-09-30
US63/085,878 2020-09-30
PCT/US2021/052987 WO2022072709A1 (en) 2020-09-30 2021-09-30 Compositions and methods for modulating tcf4 gene expression and treating pitt hopkins syndrome

Publications (3)

Publication Number Publication Date
JP2023544702A JP2023544702A (ja) 2023-10-25
JP2023544702A5 true JP2023544702A5 (https=) 2024-08-13
JP7786750B2 JP7786750B2 (ja) 2025-12-16

Family

ID=80951835

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023519419A Active JP7786750B2 (ja) 2020-09-30 2021-09-30 Tcf4遺伝子発現を調節するため、およびピット・ホプキンス症候群を治療するための組成物および方法

Country Status (9)

Country Link
US (1) US20230372542A1 (https=)
EP (1) EP4222268A4 (https=)
JP (1) JP7786750B2 (https=)
KR (1) KR20230079190A (https=)
CN (1) CN116670769A (https=)
AU (1) AU2021351512A1 (https=)
CA (1) CA3194085A1 (https=)
IL (1) IL301610A (https=)
WO (1) WO2022072709A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN117298153B (zh) * 2023-08-30 2024-03-08 济宁市第一人民医院 脑内皮细胞来源的细胞外囊泡在神经炎症中的应用
CN117476101B (zh) * 2023-11-22 2025-10-10 浙江大学 一种多组学单细胞测序数据区分恶性细胞的方法、系统、设备和介质
WO2025213093A1 (en) * 2024-04-04 2025-10-09 Lundquist Institute For Biomedical Innovation At Harbor-Ucla Medical Center Antisense oligonucleotides for treating pitt hopkin syndrome

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4683195A (en) 1986-01-30 1987-07-28 Cetus Corporation Process for amplifying, detecting, and/or-cloning nucleic acid sequences
US20180305689A1 (en) * 2015-04-22 2018-10-25 Mina Therapeutics Limited Sarna compositions and methods of use

Similar Documents

Publication Publication Date Title
JP2023544702A5 (https=)
US10369232B2 (en) Allele selective gene editing and uses thereof
JP2023532663A5 (https=)
JP2022540446A5 (https=)
RU2017142006A (ru) Векторы на основе аденоассоциированных вирусов для лечения мукополисахаридозов
JP2023070682A5 (https=)
PT851934E (pt) Plantas que sintetizam um amido modificado, processo para a sua produção e amido modificado
JP2015521465A5 (https=)
JP2019528793A5 (https=)
WO2019168950A1 (en) Methods and compositions for treating angelman syndrome
JP2024523394A5 (https=)
JP2015532097A5 (https=)
JP2023542211A5 (https=)
JP2021525531A5 (https=)
JP2023544633A5 (https=)
JP2021534794A5 (https=)
JP2020127419A5 (https=)
JP2022522166A5 (https=)
BR112012010537A2 (pt) "clonagem, expressão e uso de fosfolipases ácidas"
KR20240012370A (ko) 아밀로-알파-1, 6-글루코시다제, 4-알파-글루카노트랜스퍼라제를 인코딩하는 dna 분자의 조성물, 이를 제조하는 방법 및 이를 사용하는 방법
JP2023510186A5 (https=)
WO2020144611A4 (en) Double stranded rna and uses thereof
JP2022530168A5 (https=)
WO2023138502A1 (en) Oligonucleotide modulators activating utrophin expression
WO2024211376A2 (en) Compositions and methods for treating cag repeat diseases