JP2023544633A5 - - Google Patents
Info
- Publication number
- JP2023544633A5 JP2023544633A5 JP2023521740A JP2023521740A JP2023544633A5 JP 2023544633 A5 JP2023544633 A5 JP 2023544633A5 JP 2023521740 A JP2023521740 A JP 2023521740A JP 2023521740 A JP2023521740 A JP 2023521740A JP 2023544633 A5 JP2023544633 A5 JP 2023544633A5
- Authority
- JP
- Japan
- Prior art keywords
- homologous
- region
- nucleotide sequence
- cells
- rag1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GBGB2016139.4A GB202016139D0 (en) | 2020-10-12 | 2020-10-12 | Polynucleotide |
| GB2016139.4 | 2020-10-12 | ||
| AU2021202657A AU2021202657A1 (en) | 2021-04-28 | 2021-04-28 | Polynucleotide |
| AU2021202657 | 2021-04-28 | ||
| PCT/EP2021/078222 WO2022079054A1 (en) | 2020-10-12 | 2021-10-12 | Replacement of rag1 for use in therapy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023544633A JP2023544633A (ja) | 2023-10-24 |
| JP2023544633A5 true JP2023544633A5 (https=) | 2024-10-22 |
Family
ID=78413971
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023521740A Pending JP2023544633A (ja) | 2020-10-12 | 2021-10-12 | 治療における使用のためのｒａｇ１の置き換え |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20230365996A1 (https=) |
| EP (1) | EP4225900A1 (https=) |
| JP (1) | JP2023544633A (https=) |
| AU (1) | AU2021359781A1 (https=) |
| IL (1) | IL302031A (https=) |
| WO (1) | WO2022079054A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2024538769A (ja) * | 2021-10-12 | 2024-10-23 | オスペダーレ サン ラファエレ エス．アール．エル | Ｒａｇ１遺伝子における突然変異を修正するのに有用なポリヌクレオチド |
| GB202206346D0 (en) * | 2022-04-29 | 2022-06-15 | Ospedale San Raffaele Srl | Gene therapy |
| WO2025073293A1 (en) * | 2023-10-02 | 2025-04-10 | Consorcio Centro De Investigación Biomédica En Red | Gene editing methods for cd34+ cells to achieve clinically relevant efficacies |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| PT904392E (pt) | 1996-10-17 | 2001-06-29 | Oxford Biomedica Ltd | Vectores retrovirais |
| US20190038771A1 (en) * | 2016-02-02 | 2019-02-07 | Crispr Therapeutics Ag | Materials and methods for treatment of severe combined immunodeficiency (scid) or omenn syndrome |
| AU2019294294A1 (en) | 2018-06-25 | 2021-02-11 | Fondazione Telethon Ets | Gene therapy |
-
2021
- 2021-10-12 JP JP2023521740A patent/JP2023544633A/ja active Pending
- 2021-10-12 AU AU2021359781A patent/AU2021359781A1/en not_active Abandoned
- 2021-10-12 EP EP21798950.8A patent/EP4225900A1/en active Pending
- 2021-10-12 IL IL302031A patent/IL302031A/en unknown
- 2021-10-12 US US18/030,711 patent/US20230365996A1/en active Pending
- 2021-10-12 WO PCT/EP2021/078222 patent/WO2022079054A1/en not_active Ceased
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