IL302031A - Replacement of rag1 for use in therapy - Google Patents
Replacement of rag1 for use in therapyInfo
- Publication number
- IL302031A IL302031A IL302031A IL30203123A IL302031A IL 302031 A IL302031 A IL 302031A IL 302031 A IL302031 A IL 302031A IL 30203123 A IL30203123 A IL 30203123A IL 302031 A IL302031 A IL 302031A
- Authority
- IL
- Israel
- Prior art keywords
- identity
- region
- cells
- chr
- homologous
- Prior art date
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| GBGB2016139.4A GB202016139D0 (en) | 2020-10-12 | 2020-10-12 | Polynucleotide |
| AU2021202657A AU2021202657A1 (en) | 2021-04-28 | 2021-04-28 | Polynucleotide |
| PCT/EP2021/078222 WO2022079054A1 (en) | 2020-10-12 | 2021-10-12 | Replacement of rag1 for use in therapy |
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| EP (1) | EP4225900A1 (https=) |
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| AU (1) | AU2021359781A1 (https=) |
| IL (1) | IL302031A (https=) |
| WO (1) | WO2022079054A1 (https=) |
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| JP2024538769A (ja) * | 2021-10-12 | 2024-10-23 | オスペダーレ サン ラファエレ エス．アール．エル | Ｒａｇ１遺伝子における突然変異を修正するのに有用なポリヌクレオチド |
| GB202206346D0 (en) * | 2022-04-29 | 2022-06-15 | Ospedale San Raffaele Srl | Gene therapy |
| WO2025073293A1 (en) * | 2023-10-02 | 2025-04-10 | Consorcio Centro De Investigación Biomédica En Red | Gene editing methods for cd34+ cells to achieve clinically relevant efficacies |
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| PT904392E (pt) | 1996-10-17 | 2001-06-29 | Oxford Biomedica Ltd | Vectores retrovirais |
| US20190038771A1 (en) * | 2016-02-02 | 2019-02-07 | Crispr Therapeutics Ag | Materials and methods for treatment of severe combined immunodeficiency (scid) or omenn syndrome |
| AU2019294294A1 (en) | 2018-06-25 | 2021-02-11 | Fondazione Telethon Ets | Gene therapy |
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2021
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- 2021-10-12 AU AU2021359781A patent/AU2021359781A1/en not_active Abandoned
- 2021-10-12 EP EP21798950.8A patent/EP4225900A1/en active Pending
- 2021-10-12 IL IL302031A patent/IL302031A/en unknown
- 2021-10-12 US US18/030,711 patent/US20230365996A1/en active Pending
- 2021-10-12 WO PCT/EP2021/078222 patent/WO2022079054A1/en not_active Ceased
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| EP4225900A1 (en) | 2023-08-16 |
| US20230365996A1 (en) | 2023-11-16 |
| AU2021359781A1 (en) | 2023-06-15 |
| WO2022079054A1 (en) | 2022-04-21 |
| JP2023544633A (ja) | 2023-10-24 |
| AU2021359781A9 (en) | 2025-04-10 |
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