JP2023540806A5 - - Google Patents
Info
- Publication number
- JP2023540806A5 JP2023540806A5 JP2023516110A JP2023516110A JP2023540806A5 JP 2023540806 A5 JP2023540806 A5 JP 2023540806A5 JP 2023516110 A JP2023516110 A JP 2023516110A JP 2023516110 A JP2023516110 A JP 2023516110A JP 2023540806 A5 JP2023540806 A5 JP 2023540806A5
- Authority
- JP
- Japan
- Prior art keywords
- delivery vehicle
- vehicle according
- muscular dystrophy
- modulator
- indicates
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063077141P | 2020-09-11 | 2020-09-11 | |
| US63/077,141 | 2020-09-11 | ||
| US202163214747P | 2021-06-24 | 2021-06-24 | |
| US63/214,747 | 2021-06-24 | ||
| US202163230381P | 2021-08-06 | 2021-08-06 | |
| US63/230,381 | 2021-08-06 | ||
| PCT/US2021/049889 WO2022056277A1 (en) | 2020-09-11 | 2021-09-10 | Skeletal muscle delivery platforms and methods of use |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023540806A JP2023540806A (ja) | 2023-09-26 |
| JP2023540806A5 true JP2023540806A5 (https=) | 2024-09-19 |
Family
ID=78135129
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023516110A Pending JP2023540806A (ja) | 2020-09-11 | 2021-09-10 | 骨格筋への送達プラットフォームおよび使用の方法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20230265429A1 (https=) |
| EP (1) | EP4210763A1 (https=) |
| JP (1) | JP2023540806A (https=) |
| KR (1) | KR20230066588A (https=) |
| AU (1) | AU2021340710A1 (https=) |
| CA (1) | CA3189077A1 (https=) |
| CL (1) | CL2023000663A1 (https=) |
| IL (1) | IL301186A (https=) |
| MX (1) | MX2023002939A (https=) |
| TW (1) | TW202218687A (https=) |
| UY (1) | UY39422A (https=) |
| WO (1) | WO2022056277A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP4522742A2 (en) | 2022-05-13 | 2025-03-19 | Alnylam Pharmaceuticals, Inc. | Single-stranded loop oligonucleotides |
| EP4709855A2 (en) | 2023-05-12 | 2026-03-18 | Alnylam Pharmaceuticals, Inc. | Single-stranded loop oligonucleotides |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE60040274D1 (de) | 1999-03-10 | 2008-10-30 | Phogen Ltd | Verabreichung von nukleinsäuren und proteinen an zellen |
| EP1855694B1 (en) * | 2005-02-09 | 2020-12-02 | Sarepta Therapeutics, Inc. | Antisense composition for treating muscle atrophy |
| CN101500548A (zh) | 2006-08-18 | 2009-08-05 | 弗·哈夫曼-拉罗切有限公司 | 用于体内递送多核苷酸的多缀合物 |
| SI2539451T1 (sl) | 2010-02-24 | 2016-04-29 | Arrowhead Research Corporation | Sestavki za ciljano dostavo sirna |
| US8501930B2 (en) | 2010-12-17 | 2013-08-06 | Arrowhead Madison Inc. | Peptide-based in vivo siRNA delivery system |
| WO2013032829A1 (en) | 2011-08-26 | 2013-03-07 | Arrowhead Research Corporation | Poly(vinyl ester) polymers for in vivo nucleic acid delivery |
| CA2842041A1 (en) | 2012-04-18 | 2013-10-24 | Arrowhead Research Corporation | Poly(acrylate) polymers for in vivo nucleic acid delivery |
| US10004814B2 (en) * | 2013-11-11 | 2018-06-26 | Sirna Therapeutics, Inc. | Systemic delivery of myostatin short interfering nucleic acids (siNA) conjugated to a lipophilic moiety |
| SI3535397T1 (sl) * | 2016-11-01 | 2022-04-29 | Arrowhead Pharmaceuticals, Inc. | Ligandi alfa-V beta-6 integrina in njihove uporabe |
| WO2019089765A1 (en) * | 2017-11-01 | 2019-05-09 | Arrowhead Pharmcaceuticals, Inc. | Integrin ligands and uses thereof |
| JP7420727B2 (ja) * | 2018-02-17 | 2024-01-23 | アローヘッド ファーマシューティカルズ インコーポレイテッド | トリアルキン結合剤及び使用方法 |
| MX2020011570A (es) * | 2018-05-07 | 2020-11-24 | Alnylam Pharmaceuticals Inc | Administracion extrahepatica. |
-
2021
- 2021-09-10 MX MX2023002939A patent/MX2023002939A/es unknown
- 2021-09-10 JP JP2023516110A patent/JP2023540806A/ja active Pending
- 2021-09-10 AU AU2021340710A patent/AU2021340710A1/en active Pending
- 2021-09-10 KR KR1020237011808A patent/KR20230066588A/ko active Pending
- 2021-09-10 CA CA3189077A patent/CA3189077A1/en active Pending
- 2021-09-10 IL IL301186A patent/IL301186A/en unknown
- 2021-09-10 TW TW110133856A patent/TW202218687A/zh unknown
- 2021-09-10 UY UY0001039422A patent/UY39422A/es unknown
- 2021-09-10 EP EP21791108.0A patent/EP4210763A1/en active Pending
- 2021-09-10 WO PCT/US2021/049889 patent/WO2022056277A1/en not_active Ceased
-
2023
- 2023-03-03 US US18/178,179 patent/US20230265429A1/en active Pending
- 2023-03-08 CL CL2023000663A patent/CL2023000663A1/es unknown
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