JP2023539700A5 - - Google Patents

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Publication number
JP2023539700A5
JP2023539700A5 JP2023537888A JP2023537888A JP2023539700A5 JP 2023539700 A5 JP2023539700 A5 JP 2023539700A5 JP 2023537888 A JP2023537888 A JP 2023537888A JP 2023537888 A JP2023537888 A JP 2023537888A JP 2023539700 A5 JP2023539700 A5 JP 2023539700A5
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JP
Japan
Prior art keywords
human
itr
aav
cells
capsid protein
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Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023537888A
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English (en)
Japanese (ja)
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JP2023539700A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/048741 external-priority patent/WO2022051418A1/en
Publication of JP2023539700A publication Critical patent/JP2023539700A/ja
Publication of JP2023539700A5 publication Critical patent/JP2023539700A5/ja
Pending legal-status Critical Current

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JP2023537888A 2020-09-01 2021-09-01 哺乳動物細胞及びその改変方法 Pending JP2023539700A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063073365P 2020-09-01 2020-09-01
US63/073,365 2020-09-01
US202063111238P 2020-11-09 2020-11-09
US63/111,238 2020-11-09
PCT/US2021/048741 WO2022051418A1 (en) 2020-09-01 2021-09-01 Mammalian cells and methods for engineering the same

Publications (2)

Publication Number Publication Date
JP2023539700A JP2023539700A (ja) 2023-09-15
JP2023539700A5 true JP2023539700A5 (https=) 2024-09-10

Family

ID=78086890

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023537888A Pending JP2023539700A (ja) 2020-09-01 2021-09-01 哺乳動物細胞及びその改変方法

Country Status (7)

Country Link
US (2) US20240052341A1 (https=)
EP (1) EP4208547A1 (https=)
JP (1) JP2023539700A (https=)
AU (1) AU2021338299A1 (https=)
CA (1) CA3191396A1 (https=)
IL (1) IL301021A (https=)
WO (1) WO2022051418A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL301021A (en) 2020-09-01 2023-05-01 64 X Inc Mammalian cells and methods for engineering the same
US20240263143A1 (en) * 2023-02-02 2024-08-08 Agathos Biologics Baby Hamster Kidney (BHK) Cells Transformed with the Adenoviral E1 Gene for Production of Recombinant Adeno-Associated Virus
WO2024220789A1 (en) * 2023-04-21 2024-10-24 Regents Of The University Of Minnesota Cell lines and methods for producing recombinant adeno-associated virus

Family Cites Families (19)

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US5168062A (en) 1985-01-30 1992-12-01 University Of Iowa Research Foundation Transfer vectors and microorganisms containing human cytomegalovirus immediate-early promoter-regulatory DNA sequence
US6001650A (en) 1995-08-03 1999-12-14 Avigen, Inc. High-efficiency wild-type-free AAV helper functions
WO2008060510A2 (en) 2006-11-13 2008-05-22 Sangamo Biosciences, Inc. Zinc finger nuclease for targeting the human glucocorticoid receptor locus
WO2009146179A1 (en) 2008-04-15 2009-12-03 University Of Iowa Research Foundation Zinc finger nuclease for the cftr gene and methods of use thereof
CN102174576A (zh) 2011-01-25 2011-09-07 西北农林科技大学 一种由锌指核酸酶介导的哺乳动物内源基因定向敲除的方法和该锌指核酸酶及其表达载体
WO2013163628A2 (en) 2012-04-27 2013-10-31 Duke University Genetic correction of mutated genes
CN103668470B (zh) 2012-09-12 2015-07-29 上海斯丹赛生物技术有限公司 一种dna文库及构建转录激活子样效应因子核酸酶质粒的方法
WO2014134412A1 (en) 2013-03-01 2014-09-04 Regents Of The University Of Minnesota Talen-based gene correction
EP4464338A3 (en) 2014-11-07 2025-02-12 Editas Medicine, Inc. Systems for improving crispr/cas-mediated genome-editing
US9790490B2 (en) 2015-06-18 2017-10-17 The Broad Institute Inc. CRISPR enzymes and systems
KR102598289B1 (ko) 2016-04-16 2023-11-06 유니버시티 오브 플로리다 리서치 파운데이션, 인코포레이티드 바큘로바이러스 시스템-생산된 재조합 아데노-연관 바이러스의 생물학적 효력을 증진시키는 방법
KR20260004568A (ko) 2016-04-19 2026-01-08 더 브로드 인스티튜트, 인코퍼레이티드 신규한 crispr 효소 및 시스템
CN111344403B (zh) 2017-09-15 2025-05-06 利兰斯坦福初级大学董事会 遗传工程细胞的多元性产生和条形码编制
WO2019084046A1 (en) * 2017-10-23 2019-05-02 The Broad Institute, Inc. ENRICHING SINGLE CELL CELLULAR CONSTITUENT OF BARCODE SEQUENCING LIBRARY
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US20220073905A1 (en) * 2018-12-28 2022-03-10 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods and materials for single cell transcriptome-based development of aav vectors and promoters
US11633436B2 (en) * 2019-09-20 2023-04-25 The Broad Institute, Inc. Cholesterol reducing compositions and methods of use thereof
IL301021A (en) 2020-09-01 2023-05-01 64 X Inc Mammalian cells and methods for engineering the same
JP2025507849A (ja) 2022-03-01 2025-03-21 64-エックス, インコーポレイテッド 昆虫細胞及びその改変方法

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