JP2023537603A5 - - Google Patents

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Publication number
JP2023537603A5
JP2023537603A5 JP2023510354A JP2023510354A JP2023537603A5 JP 2023537603 A5 JP2023537603 A5 JP 2023537603A5 JP 2023510354 A JP2023510354 A JP 2023510354A JP 2023510354 A JP2023510354 A JP 2023510354A JP 2023537603 A5 JP2023537603 A5 JP 2023537603A5
Authority
JP
Japan
Prior art keywords
ehgt
seq
wpre3
bghpa
gene encoding
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023510354A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023537603A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/045995 external-priority patent/WO2022036255A1/en
Publication of JP2023537603A publication Critical patent/JP2023537603A/ja
Publication of JP2023537603A5 publication Critical patent/JP2023537603A5/ja
Pending legal-status Critical Current

Links

JP2023510354A 2020-08-14 2021-08-13 線条体ニューロンにおける遺伝子発現の調節のための人工発現構築物 Pending JP2023537603A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063066008P 2020-08-14 2020-08-14
US63/066,008 2020-08-14
PCT/US2021/045995 WO2022036255A1 (en) 2020-08-14 2021-08-13 Artificial expression constructs for modulating gene expression in striatal neurons

Publications (2)

Publication Number Publication Date
JP2023537603A JP2023537603A (ja) 2023-09-04
JP2023537603A5 true JP2023537603A5 (https=) 2024-08-21

Family

ID=80248198

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023510354A Pending JP2023537603A (ja) 2020-08-14 2021-08-13 線条体ニューロンにおける遺伝子発現の調節のための人工発現構築物

Country Status (6)

Country Link
US (1) US20230302158A1 (https=)
EP (1) EP4196583A4 (https=)
JP (1) JP2023537603A (https=)
AU (1) AU2021324975A1 (https=)
CA (1) CA3186367A1 (https=)
WO (1) WO2022036255A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20250302918A1 (en) * 2022-05-20 2025-10-02 President And Fellows Of Harvard College Methods and compositions relating to treatment of cns diseases
WO2025059552A1 (en) * 2023-09-14 2025-03-20 Allen Institute Artificial expression constructs for modulating gene expression in the basal ganglia
WO2025137554A1 (en) * 2023-12-22 2025-06-26 Allen Institute Artificial expression constructs for modulating gene expression in serotonergic neurons

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2005054467A1 (ja) * 2003-12-03 2005-06-16 Chugai Seiyaku Kabushiki Kaisha 哺乳類βアクチンプロモーターを利用した発現系
CA2680060A1 (en) * 2007-03-07 2008-09-12 Nventa Biopharmaceuticals Corporation Double-stranded locked nucleic acid compositions
JP2010022241A (ja) * 2008-07-16 2010-02-04 Institute Of Physical & Chemical Research Meis2遺伝子のエンハンサー
WO2013155222A2 (en) * 2012-04-10 2013-10-17 The Regents Of The University Of California Brain-specific enhancers for cell-based therapy
US10682424B2 (en) * 2015-03-31 2020-06-16 New York University Compositions and method for reducing seizures
US9790490B2 (en) * 2015-06-18 2017-10-17 The Broad Institute Inc. CRISPR enzymes and systems
WO2020076614A1 (en) * 2018-10-08 2020-04-16 Allen Institute Artificial expression constructs for selectively modulating gene expression in interneurons
WO2020097121A1 (en) * 2018-11-05 2020-05-14 Allen Institute Artificial expression constructs for selectively modulating gene expression in excitatory cortical neurons

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