JP2023531679A5 - - Google Patents

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Publication number
JP2023531679A5
JP2023531679A5 JP2022578970A JP2022578970A JP2023531679A5 JP 2023531679 A5 JP2023531679 A5 JP 2023531679A5 JP 2022578970 A JP2022578970 A JP 2022578970A JP 2022578970 A JP2022578970 A JP 2022578970A JP 2023531679 A5 JP2023531679 A5 JP 2023531679A5
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JP
Japan
Prior art keywords
pharmaceutical composition
patient
composition according
inhibitor
approximately
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Pending
Application number
JP2022578970A
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English (en)
Japanese (ja)
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JP2023531679A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/038445 external-priority patent/WO2021262695A1/en
Publication of JP2023531679A publication Critical patent/JP2023531679A/ja
Publication of JP2023531679A5 publication Critical patent/JP2023531679A5/ja
Pending legal-status Critical Current

Links

JP2022578970A 2020-06-22 2021-06-22 血友病を処置するための方法および組成物 Pending JP2023531679A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063042390P 2020-06-22 2020-06-22
US63/042,390 2020-06-22
PCT/US2021/038445 WO2021262695A1 (en) 2020-06-22 2021-06-22 Methods and compositions for treating hemophilia

Publications (2)

Publication Number Publication Date
JP2023531679A JP2023531679A (ja) 2023-07-25
JP2023531679A5 true JP2023531679A5 (https=) 2024-07-02

Family

ID=76943130

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022578970A Pending JP2023531679A (ja) 2020-06-22 2021-06-22 血友病を処置するための方法および組成物

Country Status (12)

Country Link
US (2) US20210393669A1 (https=)
EP (1) EP4168018A1 (https=)
JP (1) JP2023531679A (https=)
KR (1) KR20230027277A (https=)
CN (1) CN115942940A (https=)
AU (1) AU2021296786A1 (https=)
BR (1) BR112022026265A2 (https=)
CA (1) CA3188137A1 (https=)
IL (1) IL299295A (https=)
MX (1) MX2023000164A (https=)
TW (1) TW202216172A (https=)
WO (1) WO2021262695A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20240075001A1 (en) * 2022-05-24 2024-03-07 Darren Rubin Methods to reduce hemorrhage and mortality on the battlefield and applications for trauma patients
US20240000744A1 (en) * 2022-06-08 2024-01-04 Genzyme Corporation Treatment of Hemophilia with Fitusiran
CN118460655B (zh) * 2024-07-10 2025-01-28 凯莱英医药集团(天津)股份有限公司 抑制FXI基因表达的siRNA的制备方法
WO2026012399A1 (zh) * 2024-07-10 2026-01-15 正大天晴药业集团股份有限公司 靶向serpinc1的双链核糖核酸

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9127274B2 (en) 2012-04-26 2015-09-08 Alnylam Pharmaceuticals, Inc. Serpinc1 iRNA compositions and methods of use thereof
KR20180095843A (ko) 2015-12-07 2018-08-28 젠자임 코포레이션 Serpinc1-연관 장애의 치료를 위한 방법 및 조성물
TW202434265A (zh) * 2017-07-10 2024-09-01 美商健贊公司 於患有血友病之個體中治療出血事件之方法及組成物

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