JP2023530072A5 - - Google Patents

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Publication number
JP2023530072A5
JP2023530072A5 JP2022570473A JP2022570473A JP2023530072A5 JP 2023530072 A5 JP2023530072 A5 JP 2023530072A5 JP 2022570473 A JP2022570473 A JP 2022570473A JP 2022570473 A JP2022570473 A JP 2022570473A JP 2023530072 A5 JP2023530072 A5 JP 2023530072A5
Authority
JP
Japan
Prior art keywords
nucleic acid
modified oligonucleotide
modified
oligomer
acid base
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022570473A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023530072A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/038126 external-priority patent/WO2021258011A1/en
Publication of JP2023530072A publication Critical patent/JP2023530072A/ja
Publication of JP2023530072A5 publication Critical patent/JP2023530072A5/ja
Pending legal-status Critical Current

Links

JP2022570473A 2020-06-19 2021-06-18 Ｐｍｐ２２を調節するための化合物及び方法 Pending JP2023530072A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063041474P 2020-06-19 2020-06-19
US202063041643P 2020-06-19 2020-06-19
US63/041,474 2020-06-19
US63/041,643 2020-06-19
PCT/US2021/038126 WO2021258011A1 (en) 2020-06-19 2021-06-18 Compounds and methods for modulating pmp22

Publications (2)

Publication Number Publication Date
JP2023530072A JP2023530072A (ja) 2023-07-13
JP2023530072A5 true JP2023530072A5 (enExample) 2024-06-24

Family

ID=79025354

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022570473A Pending JP2023530072A (ja) 2020-06-19 2021-06-18 Ｐｍｐ２２を調節するための化合物及び方法

Country Status (4)

Country Link
US (1) US20230374519A1 (enExample)
EP (1) EP4168549A4 (enExample)
JP (1) JP2023530072A (enExample)
WO (1) WO2021258011A1 (enExample)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2017156242A1 (en) 2016-03-09 2017-09-14 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting pmp22 expression
WO2025150052A1 (en) * 2024-01-12 2025-07-17 Potentia Ltd. Targeted delivery of drug conjugates to schwann cells and treatment methods in schwann cell-related diseases

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2601204B1 (en) * 2010-04-28 2016-09-07 Ionis Pharmaceuticals, Inc. Modified nucleosides and oligomeric compounds prepared therefrom
US20180305689A1 (en) * 2015-04-22 2018-10-25 Mina Therapeutics Limited Sarna compositions and methods of use
WO2017156242A1 (en) * 2016-03-09 2017-09-14 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting pmp22 expression
WO2019157531A1 (en) * 2018-02-12 2019-08-15 Ionis Pharmaceuticals, Inc. Modified compounds and uses thereof
EP3628735A1 (en) * 2018-09-25 2020-04-01 Centre National De La Recherche Scientifique Antisense rna targeting pmp22 for the treatment of charcot-marie-tooth 1a disease
JP7561129B2 (ja) * 2018-12-21 2024-10-03 アイオーニス ファーマシューティカルズ， インコーポレーテッド Ｐｍｐ２２の発現を低減するための化合物及び方法
JP2023501352A (ja) * 2019-11-08 2023-01-18 アイオーニス ファーマシューティカルズ， インコーポレーテッド Ｓｐｄｅｆ発現を低減するための化合物及び方法

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