JP2023528801A5 - - Google Patents

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Publication number
JP2023528801A5
JP2023528801A5 JP2022573159A JP2022573159A JP2023528801A5 JP 2023528801 A5 JP2023528801 A5 JP 2023528801A5 JP 2022573159 A JP2022573159 A JP 2022573159A JP 2022573159 A JP2022573159 A JP 2022573159A JP 2023528801 A5 JP2023528801 A5 JP 2023528801A5
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JP
Japan
Prior art keywords
cells
promoter
retinal
raav
amino acids
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022573159A
Other languages
English (en)
Japanese (ja)
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JP2023528801A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/034624 external-priority patent/WO2021243085A2/en
Publication of JP2023528801A publication Critical patent/JP2023528801A/ja
Publication of JP2023528801A5 publication Critical patent/JP2023528801A5/ja
Pending legal-status Critical Current

Links

JP2022573159A 2020-05-29 2021-05-27 バリアントキャプシドを有するアデノ随伴ウイルスビリオン及びその使用方法 Pending JP2023528801A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063032206P 2020-05-29 2020-05-29
US63/032,206 2020-05-29
US202163187154P 2021-05-11 2021-05-11
US63/187,154 2021-05-11
PCT/US2021/034624 WO2021243085A2 (en) 2020-05-29 2021-05-27 Adeno-associated virus virions with variant capsids and methods of use thereof

Publications (2)

Publication Number Publication Date
JP2023528801A JP2023528801A (ja) 2023-07-06
JP2023528801A5 true JP2023528801A5 (enExample) 2024-05-29

Family

ID=78706867

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022573159A Pending JP2023528801A (ja) 2020-05-29 2021-05-27 バリアントキャプシドを有するアデノ随伴ウイルスビリオン及びその使用方法

Country Status (9)

Country Link
US (1) US12031147B2 (enExample)
EP (1) EP4157299A4 (enExample)
JP (1) JP2023528801A (enExample)
KR (1) KR20230043794A (enExample)
CN (1) CN116249772A (enExample)
AU (1) AU2021280317A1 (enExample)
CA (1) CA3179597A1 (enExample)
MX (1) MX2022015048A (enExample)
WO (1) WO2021243085A2 (enExample)

Families Citing this family (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2022150776A1 (en) 2021-01-11 2022-07-14 Vedere Bio Ii, Inc. OPTOGENETIC COMPOSITIONS COMPRISING A CBh PROMOTER SEQUENCE AND METHODS FOR USE
KR20240095539A (ko) 2021-10-08 2024-06-25 디노 테라퓨틱스, 인코포레이티드 캡시드 변이체 및 이의 사용 방법
WO2024191778A1 (en) 2023-03-10 2024-09-19 Dyno Therapeutics, Inc. Capsid polypeptides and methods of use thereof
CN118791624B (zh) * 2023-04-11 2026-04-03 苏州星明优健生物技术有限公司 用于治疗视网膜神经退行性疾病的新型gpcr嵌合视蛋白
AU2024332181A1 (en) 2023-08-31 2026-02-12 Dyno Therapeutics, Inc. Capsid polypeptides and methods of use thereof
TW202545971A (zh) 2024-02-08 2025-12-01 美商戴諾治療公司 殼體多肽及其使用方法
WO2026064442A2 (en) 2024-09-18 2026-03-26 Dyno Therapeutics, Inc. Capsid polypeptides and methods of use thereof
CN118955654B (zh) * 2024-10-15 2025-05-16 朗信启昇(苏州)生物制药有限公司 具有变异衣壳的腺相关病毒病毒体及其用途

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8663624B2 (en) * 2010-10-06 2014-03-04 The Regents Of The University Of California Adeno-associated virus virions with variant capsid and methods of use thereof
CN105755044A (zh) 2011-04-22 2016-07-13 加利福尼亚大学董事会 具有变异衣壳的腺相关病毒病毒体及其使用方法
US11021519B2 (en) * 2015-03-02 2021-06-01 Adverum Biotechnologies, Inc. Compositions and methods for intravitreal delivery of polynucleotides to retinal cones
JP6836999B2 (ja) 2015-03-24 2021-03-03 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニアThe Regents Of The University Of California アデノ随伴ウイルス変異体及びその使用方法
US11364308B2 (en) * 2016-05-13 2022-06-21 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and methods of use thereof
AU2017302013B2 (en) 2016-07-29 2022-05-26 The Regents Of The University Of California Adeno-associated virus virions with variant capsid and methods of use thereof
CA3040179A1 (en) * 2016-10-19 2018-04-26 Adverum Biotechnologies, Inc. Modified aav capsids and uses thereof
WO2018134168A1 (en) * 2017-01-17 2018-07-26 INSERM (Institut National de la Santé et de la Recherche Médicale) Methods of expressing a polynucleotide of interest in the cone photoreceptors
CA3053154A1 (en) * 2017-06-30 2019-01-03 The Regents Of The University Of California Adeno-associated virus virions with variant capsids and methods of use thereof
JP2020534788A (ja) 2017-08-28 2020-12-03 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア アデノ随伴ウイルスカプシド変異体及びその使用方法
US20230049217A1 (en) * 2021-05-21 2023-02-16 Novartis Ag Compositions and methods for enhancing visual function

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