JP2023524010A5 - - Google Patents
Info
- Publication number
- JP2023524010A5 JP2023524010A5 JP2022565920A JP2022565920A JP2023524010A5 JP 2023524010 A5 JP2023524010 A5 JP 2023524010A5 JP 2022565920 A JP2022565920 A JP 2022565920A JP 2022565920 A JP2022565920 A JP 2022565920A JP 2023524010 A5 JP2023524010 A5 JP 2023524010A5
- Authority
- JP
- Japan
- Prior art keywords
- mirna
- item
- delivery system
- viral vector
- vector delivery
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063016968P | 2020-04-28 | 2020-04-28 | |
| US63/016,968 | 2020-04-28 | ||
| PCT/US2021/029757 WO2021222476A2 (en) | 2020-04-28 | 2021-04-28 | High efficiency gene delivery system |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023524010A JP2023524010A (ja) | 2023-06-08 |
| JP2023524010A5 true JP2023524010A5 (https=) | 2024-05-10 |
Family
ID=78374241
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022565920A Pending JP2023524010A (ja) | 2020-04-28 | 2021-04-28 | 高効率遺伝子送達系 |
Country Status (4)
| Country | Link |
|---|---|
| US (2) | US20220193262A1 (https=) |
| EP (1) | EP4142758A4 (https=) |
| JP (1) | JP2023524010A (https=) |
| WO (1) | WO2021222476A2 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20240002459A1 (en) * | 2016-07-14 | 2024-01-04 | Emory University | Granulin Compositions and Uses Related Thereto |
| CN114085872A (zh) * | 2021-11-10 | 2022-02-25 | 中国科学院深圳先进技术研究院 | 一种表达tva的小鼠模型的构建方法和应用 |
| CN115029346B (zh) * | 2022-04-22 | 2024-01-02 | 复旦大学附属眼耳鼻喉科医院 | 用于靶向敲降Htra2转录本的sgRNA、CRISPR/CasRx系统及应用 |
| WO2024057339A1 (en) * | 2022-09-16 | 2024-03-21 | National Institute Of Immunology | Itch mutants for the treatment of memory and learning defects |
| WO2025094056A1 (en) * | 2023-10-31 | 2025-05-08 | Children's Medical Research Institute | Gene therapy constructs and methods of use therefor |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20110185440A1 (en) * | 2006-10-03 | 2011-07-28 | National Yang-Ming University | CISD2-Knockout Mice and Uses Thereof |
| EP3318635A1 (en) * | 2011-04-21 | 2018-05-09 | University of Massachusetts | Raav-based compositions and methods for treating alpha-1 anti-trypsin deficiencies |
| TWI614031B (zh) * | 2011-11-03 | 2018-02-11 | 國立陽明大學 | 防止皮膚老化相關症狀的醫藥組合物及其使用方法 |
| EP2692868A1 (en) * | 2012-08-02 | 2014-02-05 | Universitat Autònoma De Barcelona | Adeno-associated viral (AAV) vectors useful for transducing adipose tissue |
| WO2016077706A1 (en) * | 2014-11-13 | 2016-05-19 | Washington University | Treatment for wolfram syndrome and other endoplasmic reticulum stress disorders |
| US20160362692A1 (en) * | 2015-06-15 | 2016-12-15 | Isis Innovation Limited | Treatment of retinitis pigmentosa |
| MX2018014256A (es) * | 2016-05-20 | 2019-08-16 | Harvard College | Metodos de terapia genica para enfermedades y condiciones relacionadas con la edad. |
| MA51915A (fr) * | 2018-02-22 | 2020-12-30 | Generation Bio Co | Expression régulée de transgènes à l'aide de vecteurs adn à extrémités fermées (cedna) |
-
2021
- 2021-04-28 EP EP21796199.4A patent/EP4142758A4/en active Pending
- 2021-04-28 JP JP2022565920A patent/JP2023524010A/ja active Pending
- 2021-04-28 WO PCT/US2021/029757 patent/WO2021222476A2/en not_active Ceased
-
2022
- 2022-02-07 US US17/666,543 patent/US20220193262A1/en not_active Abandoned
-
2025
- 2025-02-13 US US19/053,116 patent/US20250325701A1/en active Pending
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