JP2023515692A5 - - Google Patents

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Publication number
JP2023515692A5
JP2023515692A5 JP2022552651A JP2022552651A JP2023515692A5 JP 2023515692 A5 JP2023515692 A5 JP 2023515692A5 JP 2022552651 A JP2022552651 A JP 2022552651A JP 2022552651 A JP2022552651 A JP 2022552651A JP 2023515692 A5 JP2023515692 A5 JP 2023515692A5
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JP
Japan
Prior art keywords
deficiency
sequence
nucleic acid
vector
acid sequence
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Granted
Application number
JP2022552651A
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English (en)
Japanese (ja)
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JP7817176B2 (ja
JP2023515692A (ja
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Application filed filed Critical
Priority claimed from PCT/US2021/020929 external-priority patent/WO2021178707A1/en
Publication of JP2023515692A publication Critical patent/JP2023515692A/ja
Publication of JP2023515692A5 publication Critical patent/JP2023515692A5/ja
Application granted granted Critical
Publication of JP7817176B2 publication Critical patent/JP7817176B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2022552651A 2020-03-04 2021-03-04 代謝性肝障害の治療のための組成物と方法 Active JP7817176B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202062985047P 2020-03-04 2020-03-04
US62/985,047 2020-03-04
US202063121488P 2020-12-04 2020-12-04
US63/121,488 2020-12-04
PCT/US2021/020929 WO2021178707A1 (en) 2020-03-04 2021-03-04 Compositions and methods for the treatment of metabolic liver disorders

Publications (3)

Publication Number Publication Date
JP2023515692A JP2023515692A (ja) 2023-04-13
JP2023515692A5 true JP2023515692A5 (enExample) 2024-03-12
JP7817176B2 JP7817176B2 (ja) 2026-02-18

Family

ID=75267602

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022552651A Active JP7817176B2 (ja) 2020-03-04 2021-03-04 代謝性肝障害の治療のための組成物と方法

Country Status (8)

Country Link
US (1) US12540335B2 (enExample)
EP (1) EP4114469A1 (enExample)
JP (1) JP7817176B2 (enExample)
KR (1) KR20220149588A (enExample)
CN (1) CN115515646A (enExample)
AU (1) AU2021230361A1 (enExample)
CA (1) CA3169529A1 (enExample)
WO (1) WO2021178707A1 (enExample)

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CA3094859A1 (en) * 2020-10-01 2022-04-01 Entos Pharmaceuticals Inc. Proteolipid vesicles formulated with fusion associated small transmembrane proteins
WO2022187671A1 (en) * 2021-03-04 2022-09-09 Poseida Therapeutics, Inc. Compositions and methods for the treatment of hemophilia
GB202205606D0 (en) * 2022-04-14 2022-06-01 Genespire S R L Lentiviral vector
KR20250155027A (ko) * 2023-02-21 2025-10-29 포세이다 테라퓨틱스, 인크. Aav piggybac 트랜스포존 폴리뉴클레오티드 조성물 및 이의 사용 방법
EP4689090A1 (en) * 2023-04-05 2026-02-11 Poseida Therapeutics, Inc. Transposase polynucleotides and uses thereof
IL325133A (en) * 2023-06-07 2026-02-01 Res Inst Nationwide Childrens Hospital Gene therapy for lysosomal acid lipase deficiency (LAL-D)
WO2025171163A1 (en) * 2024-02-06 2025-08-14 Duke University Compositions for and methods of treating lysosomal storage diseases

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