JP2023514204A5 - - Google Patents

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Publication number
JP2023514204A5
JP2023514204A5 JP2022548652A JP2022548652A JP2023514204A5 JP 2023514204 A5 JP2023514204 A5 JP 2023514204A5 JP 2022548652 A JP2022548652 A JP 2022548652A JP 2022548652 A JP2022548652 A JP 2022548652A JP 2023514204 A5 JP2023514204 A5 JP 2023514204A5
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JP
Japan
Application number
JP2022548652A
Other languages
Japanese (ja)
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JP2023514204A (ja
JPWO2021163322A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/017656 external-priority patent/WO2021163322A1/en
Publication of JP2023514204A publication Critical patent/JP2023514204A/ja
Publication of JP2023514204A5 publication Critical patent/JP2023514204A5/ja
Publication of JPWO2021163322A5 publication Critical patent/JPWO2021163322A5/ja
Pending legal-status Critical Current

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JP2022548652A 2020-02-14 2021-02-11 Cdkl5欠損障害を処置するための遺伝子治療 Pending JP2023514204A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202062976483P 2020-02-14 2020-02-14
US62/976,483 2020-02-14
US202063090492P 2020-10-12 2020-10-12
US63/090,492 2020-10-12
PCT/US2021/017656 WO2021163322A1 (en) 2020-02-14 2021-02-11 Gene therapy for treating cdkl5 deficiency disorder

Publications (3)

Publication Number Publication Date
JP2023514204A JP2023514204A (ja) 2023-04-05
JP2023514204A5 true JP2023514204A5 (https=) 2024-02-20
JPWO2021163322A5 JPWO2021163322A5 (https=) 2024-02-20

Family

ID=74873804

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022548652A Pending JP2023514204A (ja) 2020-02-14 2021-02-11 Cdkl5欠損障害を処置するための遺伝子治療

Country Status (12)

Country Link
US (1) US20230054144A1 (https=)
EP (1) EP4103724A1 (https=)
JP (1) JP2023514204A (https=)
KR (1) KR20220140537A (https=)
CN (1) CN115151648A (https=)
AU (1) AU2021218703A1 (https=)
BR (1) BR112022015921A2 (https=)
CA (1) CA3164714A1 (https=)
IL (1) IL294781A (https=)
MX (1) MX2022009982A (https=)
TW (1) TWI904135B (https=)
WO (1) WO2021163322A1 (https=)

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WO2022225978A1 (en) * 2021-04-21 2022-10-27 The Regents Of The University Of California Use of a split dcas fusion protein system for epigenetic editing
EP4387641A4 (en) * 2021-08-18 2025-07-09 Ultragenyx Pharmaceutical Inc RECOMBINANT AAV FORMULATIONS
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CN116377050A (zh) * 2022-12-16 2023-07-04 湖南家辉生物技术有限公司 一种发育性癫痫性脑病2型致病基因cdkl5突变位点的应用及其检测试剂和应用
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WO2025122548A1 (en) * 2023-12-05 2025-06-12 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to cdkl5 deficiency
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