JP2022552254A5 - - Google Patents
Info
- Publication number
- JP2022552254A5 JP2022552254A5 JP2022521217A JP2022521217A JP2022552254A5 JP 2022552254 A5 JP2022552254 A5 JP 2022552254A5 JP 2022521217 A JP2022521217 A JP 2022521217A JP 2022521217 A JP2022521217 A JP 2022521217A JP 2022552254 A5 JP2022552254 A5 JP 2022552254A5
- Authority
- JP
- Japan
- Prior art keywords
- disease
- nucleic acid
- acid construct
- construct according
- type
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025167212A JP2026021331A (ja) | 2019-10-10 | 2025-10-03 | バリアントｉｇｆ２構築体 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962913677P | 2019-10-10 | 2019-10-10 | |
| US62/913,677 | 2019-10-10 | ||
| US201962929054P | 2019-10-31 | 2019-10-31 | |
| US62/929,054 | 2019-10-31 | ||
| PCT/US2020/055251 WO2021072372A1 (en) | 2019-10-10 | 2020-10-12 | Variant igf2 constructs |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025167212A Division JP2026021331A (ja) | 2019-10-10 | 2025-10-03 | バリアントｉｇｆ２構築体 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022552254A JP2022552254A (ja) | 2022-12-15 |
| JP2022552254A5 true JP2022552254A5 (https=) | 2023-10-20 |
Family
ID=75438187
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022521217A Pending JP2022552254A (ja) | 2019-10-10 | 2020-10-12 | バリアントｉｇｆ２構築体 |
| JP2025167212A Pending JP2026021331A (ja) | 2019-10-10 | 2025-10-03 | バリアントｉｇｆ２構築体 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025167212A Pending JP2026021331A (ja) | 2019-10-10 | 2025-10-03 | バリアントｉｇｆ２構築体 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20240091321A1 (https=) |
| EP (1) | EP4041284A4 (https=) |
| JP (2) | JP2022552254A (https=) |
| KR (1) | KR20220077921A (https=) |
| CN (1) | CN115087458A (https=) |
| AU (2) | AU2020361703A1 (https=) |
| BR (1) | BR112022006842A2 (https=) |
| CA (1) | CA3154189A1 (https=) |
| IL (1) | IL292065A (https=) |
| MX (1) | MX2022004345A (https=) |
| TW (1) | TW202128740A (https=) |
| WO (1) | WO2021072372A1 (https=) |
Families Citing this family (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| BR112020021962A2 (pt) * | 2018-04-30 | 2021-01-26 | Amicus Therapeutics, Inc. | construtos para terapia gênica e métodos de uso |
| CN115379850A (zh) | 2019-12-24 | 2022-11-22 | 裘美娜治疗公司 | 再生性多肽及其用途 |
| IL303239A (en) | 2020-12-01 | 2023-07-01 | Univ Pennsylvania | Compositions and their uses for the treatment of Engelmann syndrome |
| WO2022271466A1 (en) | 2021-06-21 | 2022-12-29 | Juvena Therapeutics, Inc. | Regenerative polypeptides and uses thereof |
| WO2022271981A2 (en) | 2021-06-23 | 2022-12-29 | Lycia Therapeutics, Inc. | Bifunctional compounds containing igf-2 polypeptides |
| JP2025524569A (ja) * | 2022-07-06 | 2025-07-30 | リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル | Ｃｌｎ１ポリヌクレオチドのアデノ随伴ウイルス送達 |
| WO2024151982A1 (en) * | 2023-01-13 | 2024-07-18 | Amicus Therapeutics, Inc. | Gene therapy constructs for the treatment of pompe disease |
| KR20250161626A (ko) * | 2023-03-20 | 2025-11-17 | 스파크 테라퓨틱스, 인코포레이티드 | Ppt1 유전자 치료 |
| US20240360431A1 (en) * | 2023-04-30 | 2024-10-31 | Sichuan Real&Best Biotech Co., Ltd. | Engineered alpha-galactosidase a (a-gal a) peptides and functional variants thereof and associated methods of treating fabry disease |
| PL445164A1 (pl) * | 2023-06-07 | 2024-12-09 | Recepton Spółka Z Ograniczoną Odpowiedzialnością | Cząsteczki indukujące internalizację receptorów i białek zewnątrzkomórkowych |
| WO2025108375A1 (zh) * | 2023-11-21 | 2025-05-30 | 深圳湾实验室 | 用于蛋白降解的构建体及其应用 |
| WO2025259950A1 (en) * | 2024-06-14 | 2025-12-18 | Cz Biohub Sf, Llc | Genetically encoded lysosome targeting chimeras for cell-mediated delivery |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2002087510A2 (en) * | 2001-04-30 | 2002-11-07 | Symbiontics, Inc. | Subcellular targeting of therapeutic proteins |
| US7560424B2 (en) * | 2001-04-30 | 2009-07-14 | Zystor Therapeutics, Inc. | Targeted therapeutic proteins |
| CA2553955C (en) * | 2004-02-10 | 2012-08-28 | Zystor Therapeutics, Inc. | Acid alpha-glucosidase and fragments thereof |
| JP4988599B2 (ja) * | 2005-01-07 | 2012-08-01 | リジェネロン・ファーマシューティカルズ・インコーポレイテッド | Ｉｇｆ−１融合ポリペプチドおよびその治療的使用 |
| HRP20180291T1 (hr) * | 2011-05-27 | 2018-03-23 | Amicus Therapeutics, Inc. | Postupci za sparivanje ciljajućeg peptida na rekombinantne lizosomalne enzime za poboljšano liječenje lizosomskih bolesti nakupljanja |
| WO2014082080A2 (en) * | 2012-11-26 | 2014-05-30 | Callidus Biopharma, Inc. | Methods for coupling targeting peptides onto recombinant lysosomal enzymes for improved treatments of lysosomal storage diseases |
| ES2729997T3 (es) * | 2012-11-27 | 2019-11-07 | Biomarin Pharm Inc | Proteínas de fusión terapéuticas dirigidas de enzima lisosómica y usos de las mismas |
| AU2014228231B2 (en) * | 2013-03-15 | 2019-02-21 | Amicus Therapeutics, Inc. | Chemical crosslinkers |
| MA40460A (fr) * | 2014-08-11 | 2016-02-18 | Shire Human Genetic Therapies | Ciblage lysosomial et utilisation correspondante |
| EP3374504B1 (en) * | 2015-11-09 | 2025-03-19 | CureVac SE | Optimized nucleic acid molecules |
| AU2017315328A1 (en) * | 2016-08-24 | 2019-03-21 | Immunexpress Pty Ltd | Systemic inflammatory and pathogen biomarkers and uses therefor |
| BR112020021962A2 (pt) * | 2018-04-30 | 2021-01-26 | Amicus Therapeutics, Inc. | construtos para terapia gênica e métodos de uso |
| JP7585233B2 (ja) * | 2019-04-30 | 2024-11-18 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | ポンペ病の治療のために有用な組成物 |
-
2020
- 2020-10-12 KR KR1020227015116A patent/KR20220077921A/ko active Pending
- 2020-10-12 CA CA3154189A patent/CA3154189A1/en active Pending
- 2020-10-12 TW TW109135159A patent/TW202128740A/zh unknown
- 2020-10-12 US US17/767,803 patent/US20240091321A1/en active Pending
- 2020-10-12 EP EP20875073.7A patent/EP4041284A4/en active Pending
- 2020-10-12 AU AU2020361703A patent/AU2020361703A1/en not_active Abandoned
- 2020-10-12 MX MX2022004345A patent/MX2022004345A/es unknown
- 2020-10-12 CN CN202080081564.6A patent/CN115087458A/zh active Pending
- 2020-10-12 BR BR112022006842A patent/BR112022006842A2/pt not_active Application Discontinuation
- 2020-10-12 WO PCT/US2020/055251 patent/WO2021072372A1/en not_active Ceased
- 2020-10-12 JP JP2022521217A patent/JP2022552254A/ja active Pending
-
2022
- 2022-04-07 IL IL292065A patent/IL292065A/en unknown
-
2025
- 2025-02-01 AU AU2025200698A patent/AU2025200698A1/en active Pending
- 2025-10-03 JP JP2025167212A patent/JP2026021331A/ja active Pending
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