JP2022548031A5 - - Google Patents

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Publication number
JP2022548031A5
JP2022548031A5 JP2022516060A JP2022516060A JP2022548031A5 JP 2022548031 A5 JP2022548031 A5 JP 2022548031A5 JP 2022516060 A JP2022516060 A JP 2022516060A JP 2022516060 A JP2022516060 A JP 2022516060A JP 2022548031 A5 JP2022548031 A5 JP 2022548031A5
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JP
Japan
Prior art keywords
item
protein
sequence
composition according
target gene
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Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022516060A
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English (en)
Japanese (ja)
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JP2022548031A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/050491 external-priority patent/WO2021050940A1/en
Publication of JP2022548031A publication Critical patent/JP2022548031A/ja
Publication of JP2022548031A5 publication Critical patent/JP2022548031A5/ja
Pending legal-status Critical Current

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JP2022516060A 2019-09-13 2020-09-11 脂質ナノ粒子によって送達されるcrispr/casシステムを使用する動物における転写調節 Pending JP2022548031A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962900080P 2019-09-13 2019-09-13
US62/900,080 2019-09-13
US202063042762P 2020-06-23 2020-06-23
US63/042,762 2020-06-23
PCT/US2020/050491 WO2021050940A1 (en) 2019-09-13 2020-09-11 Transcription modulation in animals using crispr/cas systems delivered by lipid nanoparticles

Publications (2)

Publication Number Publication Date
JP2022548031A JP2022548031A (ja) 2022-11-16
JP2022548031A5 true JP2022548031A5 (enExample) 2023-09-08

Family

ID=72659909

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022516060A Pending JP2022548031A (ja) 2019-09-13 2020-09-11 脂質ナノ粒子によって送達されるcrispr/casシステムを使用する動物における転写調節

Country Status (8)

Country Link
US (1) US20210079394A1 (enExample)
EP (1) EP4028063A1 (enExample)
JP (1) JP2022548031A (enExample)
KR (1) KR20220062079A (enExample)
CN (1) CN114616002A (enExample)
AU (1) AU2020346056A1 (enExample)
CA (1) CA3153980A1 (enExample)
WO (1) WO2021050940A1 (enExample)

Families Citing this family (5)

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KR20240038811A (ko) 2018-03-19 2024-03-25 리제너론 파마슈티칼스 인코포레이티드 CRISPR/Cas 시스템을 사용한 동물에서의 전사 조절
WO2022232442A2 (en) * 2021-04-28 2022-11-03 Salk Institute For Biological Studies Multiplex crispr/cas9-mediated target gene activation system
JP2024540086A (ja) * 2021-10-28 2024-10-31 リジェネロン・ファーマシューティカルズ・インコーポレイテッド C5をノックアウトするためのcrispr/cas関連方法及び組成物
MX2024005242A (es) * 2021-11-03 2024-07-02 Intellia Therapeutics Inc Polinucleotidos, composiciones y metodos para la edicion del genoma.
US12582104B2 (en) 2021-12-08 2026-03-24 Regeneron Pharmaceuticals, Inc. Mutant myocilin disease model and uses thereof

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WO2013151663A1 (en) * 2012-04-02 2013-10-10 modeRNA Therapeutics Modified polynucleotides for the production of membrane proteins
LT3401400T (lt) 2012-05-25 2019-06-10 The Regents Of The University Of California Būdai ir kompozicijos, skirtos rnr molekulės nukreipiamai tikslinės dnr modifikacijai ir rnr molekulės nukreipiamam transkripcijos moduliavimui
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