JP2022547197A - アデノ随伴ウイルス(aav)の生体内分布の変更に向けた、aavとaav受容体(aavr)との間の相互作用を調節するための方法および組成物 - Google Patents

アデノ随伴ウイルス(aav)の生体内分布の変更に向けた、aavとaav受容体(aavr)との間の相互作用を調節するための方法および組成物 Download PDF

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JP2022547197A
JP2022547197A JP2022515606A JP2022515606A JP2022547197A JP 2022547197 A JP2022547197 A JP 2022547197A JP 2022515606 A JP2022515606 A JP 2022515606A JP 2022515606 A JP2022515606 A JP 2022515606A JP 2022547197 A JP2022547197 A JP 2022547197A
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ジン,エリック
ティッパー,クリストファー
エイチ. ヴァンデンバーグ,リュク
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マサチューセッツ アイ アンド イヤー インファーマリー
ザ スケペンス アイ リサーチ インスティテュート,インコーポレイテッド
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JP2022515606A 2019-09-09 2020-09-09 アデノ随伴ウイルス(aav)の生体内分布の変更に向けた、aavとaav受容体(aavr)との間の相互作用を調節するための方法および組成物 Pending JP2022547197A (ja)

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US201962897973P 2019-09-09 2019-09-09
US62/897,973 2019-09-09
US201962934996P 2019-11-13 2019-11-13
US62/934,996 2019-11-13
PCT/US2020/050027 WO2021050614A2 (en) 2019-09-09 2020-09-09 Methods and compositions for modulating the interaction between adeno-associated virus (aav) and the aav receptor (aavr) for altered bio-distribution of aav

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JP2022547197A true JP2022547197A (ja) 2022-11-10
JP2022547197A5 JP2022547197A5 (https=) 2023-09-15

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CN (1) CN114667349A (https=)
AU (1) AU2020347165A1 (https=)
BR (1) BR112022004183A2 (https=)
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WO2022150634A2 (en) * 2021-01-08 2022-07-14 Massachusetts Eye And Ear Infirmary Methods and compositions for modulating the interaction between adeno-associated virus (aav) and the aav receptor (aavr) for altered bio-distribution of aav
US20240352077A1 (en) * 2021-08-25 2024-10-24 Children's Medical Research Institute Modified aav capsids and vectors
US20240425549A1 (en) * 2021-08-25 2024-12-26 Children's Medical Research Institute Modified aav capsid polypeptides and vectors
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WO2023095034A1 (en) * 2021-11-24 2023-06-01 Novartis Ag Modulators of adeno-associated virus transduction and uses thereof
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WO2024238807A2 (en) 2023-05-16 2024-11-21 Affinia Therapeutics Inc. Recombinant aavs with improved tropism and specificity
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IL291136A (en) 2022-05-01
US12570998B2 (en) 2026-03-10
AU2020347165A1 (en) 2022-03-31
WO2021050614A3 (en) 2021-05-20
EP4028531A2 (en) 2022-07-20
KR20220054435A (ko) 2022-05-02
CN114667349A (zh) 2022-06-24
WO2021050614A2 (en) 2021-03-18
US20220411820A1 (en) 2022-12-29
BR112022004183A2 (pt) 2022-05-31

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