JP2022536338A5 - - Google Patents
Info
- Publication number
- JP2022536338A5 JP2022536338A5 JP2021573242A JP2021573242A JP2022536338A5 JP 2022536338 A5 JP2022536338 A5 JP 2022536338A5 JP 2021573242 A JP2021573242 A JP 2021573242A JP 2021573242 A JP2021573242 A JP 2021573242A JP 2022536338 A5 JP2022536338 A5 JP 2022536338A5
- Authority
- JP
- Japan
- Prior art keywords
- amino acid
- seq
- capsid protein
- protein corresponding
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (13)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962859539P | 2019-06-10 | 2019-06-10 | |
| US62/859,539 | 2019-06-10 | ||
| US201962866374P | 2019-06-25 | 2019-06-25 | |
| US62/866,374 | 2019-06-25 | ||
| US201962915523P | 2019-10-15 | 2019-10-15 | |
| US62/915,523 | 2019-10-15 | ||
| US202062960487P | 2020-01-13 | 2020-01-13 | |
| US62/960,487 | 2020-01-13 | ||
| US202062987858P | 2020-03-10 | 2020-03-10 | |
| US62/987,858 | 2020-03-10 | ||
| US202063010970P | 2020-04-16 | 2020-04-16 | |
| US63/010,970 | 2020-04-16 | ||
| PCT/US2020/036846 WO2020251954A1 (en) | 2019-06-10 | 2020-06-09 | Adeno-associated virus compositions for arsa gene transfer and methods of use thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022536338A JP2022536338A (ja) | 2022-08-15 |
| JP2022536338A5 true JP2022536338A5 (enExample) | 2023-06-05 |
Family
ID=73782242
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021573242A Pending JP2022536338A (ja) | 2019-06-10 | 2020-06-09 | Ａｒｓａ遺伝子移入のためのアデノ随伴ウイルス組成物およびその使用方法 |
Country Status (15)
| Country | Link |
|---|---|
| US (1) | US20220204991A1 (enExample) |
| EP (1) | EP3980447A4 (enExample) |
| JP (1) | JP2022536338A (enExample) |
| KR (1) | KR20220035107A (enExample) |
| CN (1) | CN114502575A (enExample) |
| AU (1) | AU2020292256B2 (enExample) |
| BR (1) | BR112021024855A2 (enExample) |
| CA (1) | CA3142932A1 (enExample) |
| CL (1) | CL2021003295A1 (enExample) |
| CO (1) | CO2021016797A2 (enExample) |
| IL (1) | IL288863A (enExample) |
| MX (1) | MX2021015076A (enExample) |
| PE (1) | PE20220233A1 (enExample) |
| TW (1) | TW202112807A (enExample) |
| WO (1) | WO2020251954A1 (enExample) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| RU2769577C1 (ru) * | 2021-06-01 | 2022-04-04 | федеральное государственное автономное образовательное учреждение высшего образования "Казанский (Приволжский) федеральный университет" (ФГАОУ ВО КФУ) | Препарат для лечения метахроматической лейкодистрофии и способ ее лечения |
| JP2025521111A (ja) * | 2022-05-16 | 2025-07-08 | ジェンザイム・コーポレーション | 異染性白質ジストロフィーを治療する方法 |
| CA3263388A1 (en) | 2022-07-29 | 2024-02-01 | Regeneron Pharmaceuticals, Inc. | VIRAL PARTICLES RETRIBUTED TO TRANSFERRIN RECEPTOR 1 |
| WO2024036250A2 (en) * | 2022-08-10 | 2024-02-15 | Homology Medicines, Inc. | Adeno-associated virus compositions for arsa gene transfer and methods of use thereof |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9839696B2 (en) * | 2010-04-30 | 2017-12-12 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| WO2012057363A1 (ja) * | 2010-10-27 | 2012-05-03 | 学校法人自治医科大学 | 神経系細胞への遺伝子導入のためのアデノ随伴ウイルスビリオン |
| LT3137497T (lt) * | 2014-05-02 | 2021-07-26 | Genzyme Corporation | Aav vektoriai, skirti tinklainės ir cns genų terapijai |
| MX2017009336A (es) * | 2015-01-16 | 2017-11-15 | Voyager Therapeutics Inc | Polinucleótidos dirigidos al sistema nervioso central. |
| JP6836999B2 (ja) * | 2015-03-24 | 2021-03-03 | ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニアＴｈｅ Ｒｅｇｅｎｔｓ Ｏｆ Ｔｈｅ Ｕｎｉｖｅｒｓｉｔｙ Ｏｆ Ｃａｌｉｆｏｒｎｉａ | アデノ随伴ウイルス変異体及びその使用方法 |
| HK1256341A1 (zh) * | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| TWI906646B (zh) * | 2015-06-18 | 2025-12-01 | 美商博得學院股份有限公司 | 降低脫靶效應的ｃｒｉｓｐｒ酶突變 |
| KR20230065367A (ko) * | 2018-02-01 | 2023-05-11 | 호몰로지 메디슨, 인크. | Pah 유전자 전달을 위한 아데노-연관 바이러스 조성물 및 이의 사용 방법 |
| CN113454232B (zh) * | 2019-02-15 | 2024-10-29 | 世代生物公司 | 封闭端dna（cedna）产生中对rep蛋白活性的调节 |
| KR20220020261A (ko) * | 2019-05-03 | 2022-02-18 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 이염성 백질이영양증의 치료에 유용한 조성물 |
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2020
- 2020-06-09 WO PCT/US2020/036846 patent/WO2020251954A1/en not_active Ceased
- 2020-06-09 BR BR112021024855A patent/BR112021024855A2/pt not_active IP Right Cessation
- 2020-06-09 EP EP20821636.6A patent/EP3980447A4/en not_active Withdrawn
- 2020-06-09 KR KR1020227000707A patent/KR20220035107A/ko not_active Ceased
- 2020-06-09 MX MX2021015076A patent/MX2021015076A/es unknown
- 2020-06-09 AU AU2020292256A patent/AU2020292256B2/en not_active Ceased
- 2020-06-09 JP JP2021573242A patent/JP2022536338A/ja active Pending
- 2020-06-09 PE PE2021002049A patent/PE20220233A1/es unknown
- 2020-06-09 CA CA3142932A patent/CA3142932A1/en active Pending
- 2020-06-09 TW TW109119333A patent/TW202112807A/zh unknown
- 2020-06-09 CN CN202080054069.6A patent/CN114502575A/zh active Pending
-
2021
- 2021-12-09 IL IL288863A patent/IL288863A/en unknown
- 2021-12-10 US US17/643,631 patent/US20220204991A1/en not_active Abandoned
- 2021-12-10 CL CL2021003295A patent/CL2021003295A1/es unknown
- 2021-12-10 CO CONC2021/0016797A patent/CO2021016797A2/es unknown