JP2022526643A5 - - Google Patents
Info
- Publication number
- JP2022526643A5 JP2022526643A5 JP2021559779A JP2021559779A JP2022526643A5 JP 2022526643 A5 JP2022526643 A5 JP 2022526643A5 JP 2021559779 A JP2021559779 A JP 2021559779A JP 2021559779 A JP2021559779 A JP 2021559779A JP 2022526643 A5 JP2022526643 A5 JP 2022526643A5
- Authority
- JP
- Japan
- Prior art keywords
- dose
- patient
- hours
- midday
- evening
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025115231A JP2025160227A (ja) | 2019-04-10 | 2025-07-08 | 小児患者においてナンセンス変異が介在するデュシェンヌ型筋ジストロフィーを治療するための方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962831931P | 2019-04-10 | 2019-04-10 | |
| US62/831,931 | 2019-04-10 | ||
| PCT/US2020/027382 WO2020210432A1 (en) | 2019-04-10 | 2020-04-09 | Method for treating nonsense mutation mediated duchenne muscular dystrophy in pediatric patients |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025115231A Division JP2025160227A (ja) | 2019-04-10 | 2025-07-08 | 小児患者においてナンセンス変異が介在するデュシェンヌ型筋ジストロフィーを治療するための方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022526643A JP2022526643A (ja) | 2022-05-25 |
| JP2022526643A5 true JP2022526643A5 (enExample) | 2023-04-18 |
Family
ID=72751530
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021559779A Pending JP2022526643A (ja) | 2019-04-10 | 2020-04-09 | 小児患者においてナンセンス変異が介在するデュシェンヌ型筋ジストロフィーを治療するための方法 |
| JP2025115231A Pending JP2025160227A (ja) | 2019-04-10 | 2025-07-08 | 小児患者においてナンセンス変異が介在するデュシェンヌ型筋ジストロフィーを治療するための方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025115231A Pending JP2025160227A (ja) | 2019-04-10 | 2025-07-08 | 小児患者においてナンセンス変異が介在するデュシェンヌ型筋ジストロフィーを治療するための方法 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US12458629B2 (enExample) |
| EP (2) | EP3952867A4 (enExample) |
| JP (2) | JP2022526643A (enExample) |
| KR (1) | KR20210151131A (enExample) |
| CN (1) | CN114007608A (enExample) |
| CA (1) | CA3135641A1 (enExample) |
| EA (1) | EA202192767A1 (enExample) |
| IL (1) | IL287053A (enExample) |
| MX (1) | MX2021012428A (enExample) |
| WO (1) | WO2020210432A1 (enExample) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR102665711B1 (ko) * | 2021-12-21 | 2024-05-14 | 재단법인 아산사회복지재단 | Ras 활성도를 이용한 신경섬유종증 치료제에 대한 감수성 예측용 바이오마커 조성물 및 Ras 활성 억제제를 포함하는 신경섬유종증 예방 또는 치료용 약학적 조성물 |
| WO2025110781A1 (ko) * | 2023-11-24 | 2025-05-30 | 재단법인 아산사회복지재단 | Ampd3를 포함하는 신경섬유종증 치료제에 대한 감수성 예측용 바이오마커 조성물 및 ampd3 저해제를 포함하는 신경섬유종증 예방 또는 치료용 약학 조성물 |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2887054T3 (es) | 2003-04-11 | 2021-12-21 | Ptc Therapeutics Inc | Compuesto de ácido 1,2,4-oxadiazol benzoico y su uso para la supresión sin sentido y el tratamiento de enfermedades |
| CA2603402C (en) | 2005-04-08 | 2017-10-31 | Ptc Therapeutics, Inc. | Compositions of an orally active 1,2,4-oxadiazole for nonsense mutation suppression therapy |
| DE102005061832A1 (de) | 2005-12-23 | 2007-06-28 | Patent-Treuhand-Gesellschaft für elektrische Glühlampen mbH | Hochdruckentladungslampe mit verbesserter Zündfähigkeit sowie Hochspannungspulsgenerator |
| IN2014CN04406A (enExample) * | 2006-03-30 | 2015-09-04 | Ptc Therapeutics Inc | |
| PT2059513E (pt) | 2006-09-08 | 2013-04-30 | Ptc Therapeutics Inc | Processo para a preparação de ácidos 1,2,4-oxadiazolebenzóicos |
| WO2008130370A1 (en) | 2006-09-25 | 2008-10-30 | Ptc Therapeutics, Inc. | Hydroxylated 1,2,4-oxadiazole benzoic acid compounds, compositions thereof and the use for nonsense suppression |
| SG10201609581TA (en) | 2006-09-25 | 2016-12-29 | Ptc Therapeutics Inc | Crystalline forms of 3-[5-(2-fluorophenyl)-[1,2,4]oxadiazol-3-yl]-benzoic acid |
| CL2007002923A1 (es) | 2006-10-12 | 2008-06-06 | Ptc Therapeutics Inc Soc Organ | Metodo para el tratamiento, prevencion o manejo de una enfermedad asociada con una mutacion sin sentido tal como cancer, diabetes o enfermedad pulmonar, que consiste en administrar a un paciente una cantidad efectiva de acido 3-[5-(2-fluoro-fenil)-[1 |
| EP2203173B1 (en) * | 2007-10-26 | 2015-12-23 | Academisch Ziekenhuis Leiden | Means and methods for counteracting muscle disorders |
| ES2779302T3 (es) * | 2013-09-04 | 2020-08-14 | Cold Spring Harbor Laboratory | Reducción de la degradación de ARNm con mediación sin sentido |
| TWI695717B (zh) * | 2014-03-06 | 2020-06-11 | 美商 Ptc 治療公司 | １,２,４-二唑苯甲酸之鹽及醫藥組合物 |
| CN116196389A (zh) * | 2016-01-06 | 2023-06-02 | 康德生物医疗有限公司 | 用于预防和治疗杜氏肌肉萎缩症的方法和组合物 |
-
2020
- 2020-04-09 JP JP2021559779A patent/JP2022526643A/ja active Pending
- 2020-04-09 KR KR1020217035972A patent/KR20210151131A/ko not_active Ceased
- 2020-04-09 WO PCT/US2020/027382 patent/WO2020210432A1/en not_active Ceased
- 2020-04-09 EP EP20788548.4A patent/EP3952867A4/en not_active Withdrawn
- 2020-04-09 CN CN202080042488.8A patent/CN114007608A/zh active Pending
- 2020-04-09 CA CA3135641A patent/CA3135641A1/en active Pending
- 2020-04-09 EA EA202192767A patent/EA202192767A1/ru unknown
- 2020-04-09 EP EP24207847.5A patent/EP4473971A3/en active Pending
- 2020-04-09 MX MX2021012428A patent/MX2021012428A/es unknown
- 2020-04-09 US US17/602,576 patent/US12458629B2/en active Active
-
2021
- 2021-10-06 IL IL287053A patent/IL287053A/en unknown
-
2025
- 2025-07-08 JP JP2025115231A patent/JP2025160227A/ja active Pending
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