JP2022512784A5 - - Google Patents

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Publication number
JP2022512784A5
JP2022512784A5 JP2021521854A JP2021521854A JP2022512784A5 JP 2022512784 A5 JP2022512784 A5 JP 2022512784A5 JP 2021521854 A JP2021521854 A JP 2021521854A JP 2021521854 A JP2021521854 A JP 2021521854A JP 2022512784 A5 JP2022512784 A5 JP 2022512784A5
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JP
Japan
Prior art keywords
nucleic acid
acid molecule
isolated nucleic
vector
isolated
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Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
JP2021521854A
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English (en)
Japanese (ja)
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JP2022512784A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/IB2019/059091 external-priority patent/WO2020084540A1/en
Publication of JP2022512784A publication Critical patent/JP2022512784A/ja
Publication of JP2022512784A5 publication Critical patent/JP2022512784A5/ja
Withdrawn legal-status Critical Current

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JP2021521854A 2018-10-25 2019-10-24 網膜神経節細胞中の遺伝子の特異的発現のためのプロモーターSynP78(ProA27) Withdrawn JP2022512784A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP18202537 2018-10-25
EP18202537.9 2018-10-25
PCT/IB2019/059091 WO2020084540A1 (en) 2018-10-25 2019-10-24 Synp78 (proa27), a promoter for the specific expression of genes in retinal ganglion cells

Publications (2)

Publication Number Publication Date
JP2022512784A JP2022512784A (ja) 2022-02-07
JP2022512784A5 true JP2022512784A5 (https=) 2022-10-31

Family

ID=63998566

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021521854A Withdrawn JP2022512784A (ja) 2018-10-25 2019-10-24 網膜神経節細胞中の遺伝子の特異的発現のためのプロモーターSynP78(ProA27)

Country Status (5)

Country Link
US (1) US20210355505A1 (https=)
EP (1) EP3870240A1 (https=)
JP (1) JP2022512784A (https=)
CN (1) CN112930201A (https=)
WO (1) WO2020084540A1 (https=)

Families Citing this family (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2010011467A (es) 2008-04-18 2011-02-15 Novartis Forschungsstiftung Novedosas herramientas y metodos terapeuticos para tratar la ceguera.
US10941417B2 (en) 2015-04-30 2021-03-09 Friedrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in Müller cells
US10857241B2 (en) 2015-09-15 2020-12-08 Friedrich Miescher Institute For Biomedical Research Therapeutical tools and methods for treating blindness by targeting photoreceptors
WO2017064642A1 (en) 2015-10-14 2017-04-20 Fredrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in retinal endothelial cells
EP3383440B1 (en) 2015-12-03 2021-06-30 Friedrich Miescher Institute for Biomedical Research Synp162, a promoter for the specific expression of genes in rod photoreceptors
ES2909444T3 (es) 2015-12-03 2022-05-06 Friedrich Miescher Institute For Biomedical Res Synp159, un promotor para la expresión específica de genes en los fotorreceptores de los bastones
WO2017093934A1 (en) 2015-12-03 2017-06-08 Friedrich Miescher Institute For Biomedical Research Synp160, a promoter for the specific expression of genes in rod photoreceptors
EP3383439B1 (en) 2015-12-03 2019-09-25 Friedrich Miescher Institute for Biomedical Research Synp161, a promoter for the specific expression of genes in rod photoreceptors
RU2766353C2 (ru) 2016-11-02 2022-03-15 Фридрих Мишер Инститьют Фор Байомедикал Рисерч Synp198, промотор для специфической экспрессии генов в ганглионарных клетках сетчатки, избирательных в отношении направления
WO2018146588A1 (en) 2017-02-08 2018-08-16 Friedrich Miescher Institute For Biomedical Research Synp88, a promoter for the specific expression of genes in retinal ganglion cells
MX2020005033A (es) 2017-11-15 2020-10-28 Friedrich Miescher Institute For Biomedical Res Promotor especifico de las celulas del epitelio pigmentario retinal en primates.
SG11202005024QA (en) 2017-11-30 2020-06-29 Friedrich Miescher Institute For Biomedical Res Synpiii, a promoter for the specific expression of genes in retinal pigment epithelium

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2002082904A2 (en) * 2001-04-13 2002-10-24 The Trustees Of The University Of Pennsylvania Method of treating or retarding the development of blindness
US9567376B2 (en) * 2013-02-08 2017-02-14 The Trustees Of The University Of Pennsylvania Enhanced AAV-mediated gene transfer for retinal therapies
EP3383440B1 (en) * 2015-12-03 2021-06-30 Friedrich Miescher Institute for Biomedical Research Synp162, a promoter for the specific expression of genes in rod photoreceptors
EP3176177A1 (en) * 2015-12-03 2017-06-07 Friedrich Miescher Institute for Biomedical Research Synp157, a promoter for the specific expression of genes in rod photoreceptors

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