JP2022501060A5 - - Google Patents

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Publication number
JP2022501060A5
JP2022501060A5 JP2021517702A JP2021517702A JP2022501060A5 JP 2022501060 A5 JP2022501060 A5 JP 2022501060A5 JP 2021517702 A JP2021517702 A JP 2021517702A JP 2021517702 A JP2021517702 A JP 2021517702A JP 2022501060 A5 JP2022501060 A5 JP 2022501060A5
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JP
Japan
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optionally
nucleic acid
sequence
promoter
vector
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JP2021517702A
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English (en)
Japanese (ja)
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JP7589997B2 (ja
JP2022501060A (ja
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Priority claimed from PCT/US2019/053492 external-priority patent/WO2020069339A1/en
Publication of JP2022501060A publication Critical patent/JP2022501060A/ja
Publication of JP2022501060A5 publication Critical patent/JP2022501060A5/ja
Application granted granted Critical
Publication of JP7589997B2 publication Critical patent/JP7589997B2/ja
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JP2021517702A 2018-09-28 2019-09-27 遺伝子の発現のための変異体リバーステトラサイクリントランスアクチベーター Active JP7589997B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862738894P 2018-09-28 2018-09-28
US62/738,894 2018-09-28
PCT/US2019/053492 WO2020069339A1 (en) 2018-09-28 2019-09-27 Mutant reverse tetracycline transactivators for expression of genes

Publications (3)

Publication Number Publication Date
JP2022501060A JP2022501060A (ja) 2022-01-06
JP2022501060A5 true JP2022501060A5 (enExample) 2022-10-05
JP7589997B2 JP7589997B2 (ja) 2024-11-26

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ID=68242854

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021517702A Active JP7589997B2 (ja) 2018-09-28 2019-09-27 遺伝子の発現のための変異体リバーステトラサイクリントランスアクチベーター

Country Status (6)

Country Link
US (1) US20210403923A1 (enExample)
EP (1) EP3856260A1 (enExample)
JP (1) JP7589997B2 (enExample)
CN (1) CN113164625B (enExample)
CA (1) CA3113470A1 (enExample)
WO (1) WO2020069339A1 (enExample)

Families Citing this family (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL281470B2 (en) 2018-09-28 2025-08-01 Harvard College Cellular reprogramming to reverse aging and promote organ and tissue regeneration
US12274733B2 (en) 2018-09-28 2025-04-15 President And Fellows Of Harvard College Cellular reprogramming to reverse aging and promote organ and tissue regeneration
CA3159557A1 (en) * 2019-11-05 2021-05-14 Lonza Walkersville, Inc. Allogeneic t-cells and methods for production thereof
GB202103327D0 (en) * 2021-03-10 2021-04-21 Babraham Inst Novel method
US12467917B2 (en) 2021-03-16 2025-11-11 California Institute Of Technology Reconstructing human early embryogenesis in vitro with pluripotent stem cells
EP4355882A2 (en) * 2021-06-15 2024-04-24 Modernatx, Inc. Engineered polynucleotides for cell-type or microenvironment-specific expression
WO2023196851A1 (en) * 2022-04-06 2023-10-12 President And Fellows Of Harvard College Reversing aging of the central nervous system
WO2024012504A1 (zh) * 2022-07-12 2024-01-18 南京瑞初医药有限公司 组合物及其使用方法
WO2024026254A1 (en) * 2022-07-26 2024-02-01 Modernatx, Inc. Engineered polynucleotides for temporal control of expression
CN116004789B (zh) * 2022-08-01 2024-06-04 湖南家辉生物技术有限公司 一种Seckel综合征致病基因CEP152突变位点的应用及其诊断试剂
US12252518B2 (en) 2023-01-06 2025-03-18 Life Biosciences, Inc. Methods of treating non-arteritic anterior ischemic optic neuropathy

Family Cites Families (29)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5549910A (en) 1989-03-31 1996-08-27 The Regents Of The University Of California Preparation of liposome and lipid complex compositions
JP3218637B2 (ja) 1990-07-26 2001-10-15 大正製薬株式会社 安定なリポソーム水懸濁液
JP2958076B2 (ja) 1990-08-27 1999-10-06 株式会社ビタミン研究所 遺伝子導入用多重膜リポソーム及び遺伝子捕捉多重膜リポソーム製剤並びにその製法
US5399363A (en) 1991-01-25 1995-03-21 Eastman Kodak Company Surface modified anticancer nanoparticles
US5543158A (en) 1993-07-23 1996-08-06 Massachusetts Institute Of Technology Biodegradable injectable nanoparticles
US5741516A (en) 1994-06-20 1998-04-21 Inex Pharmaceuticals Corporation Sphingosomes for enhanced drug delivery
AU746850B2 (en) * 1994-07-01 2002-05-02 Tet Systems Holding Gmbh & Co. Kg Tetracycline-regulated transcriptional modulaters
US5795587A (en) 1995-01-23 1998-08-18 University Of Pittsburgh Stable lipid-comprising drug delivery complexes and methods for their production
IE80468B1 (en) 1995-04-04 1998-07-29 Elan Corp Plc Controlled release biodegradable nanoparticles containing insulin
US5738868A (en) 1995-07-18 1998-04-14 Lipogenics Ltd. Liposome compositions and kits therefor
DE19851415B4 (de) * 1998-11-07 2010-11-04 Wolfgang Hillen Mutanter Transaktivator
MX359371B (es) 2001-11-13 2018-09-25 Univ Pennsylvania Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo.
US20030186281A1 (en) * 2001-12-21 2003-10-02 Wolfgang Hillen Modified tetracycline repressor protein compositions and methods of use
GB0327384D0 (en) * 2003-11-25 2003-12-31 Queen Mary & Westfield College Gene therapy
ATE512228T1 (de) * 2005-11-17 2011-06-15 Tet Systems Gmbh & Co Kg Induzierbare expressionssysteme
US9388425B2 (en) * 2006-10-20 2016-07-12 Trustees Of Boston University Tunable genetic switch for regulating gene expression
US8080647B2 (en) * 2006-11-22 2011-12-20 Pioneer Hi Bred International Inc Tetracycline repressor and uses thereof
CN101302553A (zh) * 2008-05-30 2008-11-12 广州华峰生物科技有限公司 基于环介导等温扩增技术的结核分歧杆菌基因快速诊断试剂盒及其检测方法
US8734809B2 (en) 2009-05-28 2014-05-27 University Of Massachusetts AAV's and uses thereof
WO2012071549A2 (en) * 2010-11-24 2012-05-31 Clontech Laboratories, Inc. Inducible expression system transcription modulators comprising a distributed protein transduction domain and methods for using the same
EP2710130B1 (en) * 2011-05-19 2022-06-29 Fundación Pública Andaluza Progreso Y Salud Highly inducible dual-promoter lentiviral tet-on system
CN102816793B (zh) * 2012-08-22 2014-09-10 陕西师范大学 单载体双向启动的Tet-on诱导表达系统及其构建方法和应用
DK2898076T3 (en) * 2012-09-19 2018-06-14 Dsm Ip Assets Bv METHOD OF CELL MODIFICATION USING ESSENTIAL GENES AS MARKERS AND EVEN RECYCLING THESE
KR20150087321A (ko) * 2012-11-21 2015-07-29 메르츠 파마 게엠베하 운트 코. 카가아 보툴리눔 신경독소 생물학적 활성의 결정을 위한 수단 및 방법
US10004765B2 (en) * 2013-03-14 2018-06-26 University Of Massachusetts Dosage compensating transgenes and cells
US11219636B2 (en) * 2015-05-17 2022-01-11 The Medical Research, Infrastructure and Health Services Fund of the Tel Aviv Medical Center Compositions and methods for treating cancer
AU2016315703A1 (en) * 2015-08-31 2018-03-08 The Trustees Of The University Of Pennsylvania Chimeric AAV-anti-VEGF for treating cancer in canines
CN111801345A (zh) * 2017-07-28 2020-10-20 哈佛大学的校长及成员们 使用噬菌体辅助连续进化(pace)的进化碱基编辑器的方法和组合物
WO2019099552A1 (en) * 2017-11-14 2019-05-23 The J. David Gladstone Institutes Methods of generating retinal pigment epithelium (rpe)

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