JP2021534818A5 - - Google Patents

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Publication number
JP2021534818A5
JP2021534818A5 JP2021533393A JP2021533393A JP2021534818A5 JP 2021534818 A5 JP2021534818 A5 JP 2021534818A5 JP 2021533393 A JP2021533393 A JP 2021533393A JP 2021533393 A JP2021533393 A JP 2021533393A JP 2021534818 A5 JP2021534818 A5 JP 2021534818A5
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JP
Japan
Prior art keywords
cells
approximately
cell line
sequence encoding
viral vector
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Application number
JP2021533393A
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English (en)
Japanese (ja)
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JP2021534818A (ja
JP7470119B2 (ja
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Priority claimed from PCT/US2019/047800 external-priority patent/WO2020041647A1/en
Publication of JP2021534818A publication Critical patent/JP2021534818A/ja
Publication of JP2021534818A5 publication Critical patent/JP2021534818A5/ja
Application granted granted Critical
Publication of JP7470119B2 publication Critical patent/JP7470119B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2021533393A 2018-08-24 2019-08-23 無血清培地におけるベクター産生 Active JP7470119B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862722784P 2018-08-24 2018-08-24
US62/722,784 2018-08-24
PCT/US2019/047800 WO2020041647A1 (en) 2018-08-24 2019-08-23 Vector production in serum free media

Publications (3)

Publication Number Publication Date
JP2021534818A JP2021534818A (ja) 2021-12-16
JP2021534818A5 true JP2021534818A5 (enExample) 2022-08-29
JP7470119B2 JP7470119B2 (ja) 2024-04-17

Family

ID=67874545

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021533393A Active JP7470119B2 (ja) 2018-08-24 2019-08-23 無血清培地におけるベクター産生

Country Status (9)

Country Link
US (1) US20210238632A1 (enExample)
EP (1) EP3841212A1 (enExample)
JP (1) JP7470119B2 (enExample)
KR (2) KR102944997B1 (enExample)
CN (1) CN112639109A (enExample)
AU (1) AU2019325609A1 (enExample)
CA (1) CA3109924A1 (enExample)
SG (1) SG11202101594WA (enExample)
WO (1) WO2020041647A1 (enExample)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN113518825A (zh) * 2018-12-23 2021-10-19 美国杰特贝林生物制品有限公司 Wiskott-aldrich综合征的造血干细胞基因疗法
KR20230017799A (ko) * 2020-05-15 2023-02-06 아이벡스솔, 아이엔씨. 세포 및 유전자 요법을 위한 안정한 바이러스 벡터 생산자 세포를 생산하기 위한 조성물 및 방법
CN111808859B (zh) * 2020-07-13 2022-09-13 中国科学院广州生物医药与健康研究院 WAS基因的gRNA及其应用
JP2024539033A (ja) * 2021-10-19 2024-10-28 アムジエン・インコーポレーテツド 組換えレンチウイルス産生のための組成物及び方法
CN114045265A (zh) * 2021-11-17 2022-02-15 深圳知因细胞生物科技有限公司 一种慢病毒体外转染人造血干细胞的试剂和试剂盒
CN114716530B (zh) * 2022-05-05 2023-11-10 明长(上海)生物医药科技有限公司 一种蛋白液、制备方法及应用
JP2025520432A (ja) * 2022-06-15 2025-07-03 シーエスエル・ベーリング・エルエルシー エンベロープ型ウイルスを産生する方法

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US6013516A (en) 1995-10-06 2000-01-11 The Salk Institute For Biological Studies Vector and method of use for nucleic acid delivery to non-dividing cells
ES2291025T3 (es) 1998-05-13 2008-02-16 Genetix Pharmaceuticals Inc. Celulas lentivirales de empaquetamiento.
US9043994B2 (en) 2007-03-13 2015-06-02 Massachusetts Institute Of Technology Cre-lox based gene knockdown constructs and methods of use thereof
WO2012170431A2 (en) 2011-06-06 2012-12-13 Bluebird Bio, Inc. Improved geneswitch systems
WO2014043131A1 (en) * 2012-09-14 2014-03-20 The Regents Of The University Of California Lentiviral vector for stem cell gene therapy of sickle cell disease
CA3229275A1 (en) 2013-12-09 2015-06-18 Sangamo Biosciences, Inc. Methods and compositions for genome engineering
US10072067B2 (en) 2014-01-30 2018-09-11 Children's Hospital Medical Center Fetal hemoglobin for genetic correction of sickle cell disease
US10350245B2 (en) * 2015-01-21 2019-07-16 Fred Hutchinson Cancer Research Center Point-of-care and/or portable platform for gene therapy
DK3294893T5 (da) * 2015-05-13 2024-10-07 Csl Behring Gene Therapy Inc Bioproduktion af lentivirale vektorer
KR20180014051A (ko) 2015-05-28 2018-02-07 코넬 유니버시티 혈관 부종 치료제로서의 아데노-관련 바이러스 매개 c1e1의 전달
CN108463243B (zh) 2015-11-19 2022-06-14 夏尔人类遗传性治疗公司 重组人c1酯酶抑制剂及其用途
US11352631B2 (en) 2015-12-18 2022-06-07 Sangamo Therapeutics, Inc. Targeted disruption of the T cell receptor
US20190241910A1 (en) 2016-03-11 2019-08-08 Bluebird Bio, Inc. Genome edited immune effector cells
KR102014349B1 (ko) 2016-08-17 2019-08-26 서울대학교 산학협력단 Jak 억제제를 포함하는 면역반응 억제용 조성물
MA46018A (fr) 2016-08-19 2019-06-26 Bluebird Bio Inc Activateurs d'édition du génome
AU2018256412B2 (en) 2017-04-21 2025-02-27 Seattle Children's Hospital (dba Seattle Children's Research Institute) Optimized lentiviral vector for XLA gene therapy
CA3070242A1 (en) * 2017-07-18 2019-01-24 Calimmune, Inc. Compositions and methods for treating beta-hemoglobinopathies

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