JP2021533126A5 - - Google Patents

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Publication number
JP2021533126A5
JP2021533126A5 JP2021505674A JP2021505674A JP2021533126A5 JP 2021533126 A5 JP2021533126 A5 JP 2021533126A5 JP 2021505674 A JP2021505674 A JP 2021505674A JP 2021505674 A JP2021505674 A JP 2021505674A JP 2021533126 A5 JP2021533126 A5 JP 2021533126A5
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JP
Japan
Prior art keywords
pharmaceutical product
product according
raav
mammal
viral vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021505674A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021533126A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/044290 external-priority patent/WO2020028466A1/en
Publication of JP2021533126A publication Critical patent/JP2021533126A/ja
Publication of JP2021533126A5 publication Critical patent/JP2021533126A5/ja
Priority to JP2024001612A priority Critical patent/JP2024041871A/ja
Pending legal-status Critical Current

Links

JP2021505674A 2018-07-31 2019-07-31 臓器機能を制御するための遺伝子治療方法 Pending JP2021533126A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024001612A JP2024041871A (ja) 2018-07-31 2024-01-10 臓器機能を制御するための遺伝子治療方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862712669P 2018-07-31 2018-07-31
US62/712,669 2018-07-31
PCT/US2019/044290 WO2020028466A1 (en) 2018-07-31 2019-07-31 Gene therapy methods to control organ function

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024001612A Division JP2024041871A (ja) 2018-07-31 2024-01-10 臓器機能を制御するための遺伝子治療方法

Publications (2)

Publication Number Publication Date
JP2021533126A JP2021533126A (ja) 2021-12-02
JP2021533126A5 true JP2021533126A5 (enExample) 2022-08-01

Family

ID=69230802

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021505674A Pending JP2021533126A (ja) 2018-07-31 2019-07-31 臓器機能を制御するための遺伝子治療方法
JP2024001612A Pending JP2024041871A (ja) 2018-07-31 2024-01-10 臓器機能を制御するための遺伝子治療方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024001612A Pending JP2024041871A (ja) 2018-07-31 2024-01-10 臓器機能を制御するための遺伝子治療方法

Country Status (14)

Country Link
US (1) US20210301306A1 (enExample)
EP (1) EP3829718A4 (enExample)
JP (2) JP2021533126A (enExample)
KR (1) KR20210052450A (enExample)
CN (1) CN113301956B (enExample)
AU (1) AU2019315445A1 (enExample)
BR (1) BR112021001878A2 (enExample)
CA (1) CA3108324A1 (enExample)
EA (1) EA202190358A1 (enExample)
IL (1) IL280531A (enExample)
MX (1) MX2021001336A (enExample)
PH (1) PH12021550243A1 (enExample)
SG (1) SG11202101042SA (enExample)
WO (1) WO2020028466A1 (enExample)

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US20150111918A1 (en) 2012-03-08 2015-04-23 Medtronic Ardian Luxembourg S.a.r.l Immune system neuromodulation and associated systems and methods
EP3226795B1 (en) 2014-12-03 2020-08-26 Metavention, Inc. Systems for modulating nerves or other tissue
US10524859B2 (en) 2016-06-07 2020-01-07 Metavention, Inc. Therapeutic tissue modulation devices and methods
CN115707773A (zh) * 2021-08-20 2023-02-21 中国科学院深圳先进技术研究院 一种利用交感神经控制血管内皮细胞异质性的方法
WO2023019565A1 (zh) * 2021-08-20 2023-02-23 中国科学院深圳先进技术研究院 一种利用交感神经控制血管内皮细胞异质性的方法
CN116019909B (zh) * 2022-09-16 2025-07-29 上海市第十人民医院 一种CRISPR/Cas9纳米系统
CN116115758B (zh) * 2022-11-22 2024-12-03 上海市内分泌代谢病研究所 Gabaa受体作为靶点在制备或筛选降血脂、治疗肥胖和/或改善代谢的药物中的应用
CN121313878A (zh) * 2024-12-04 2026-01-13 良渚实验室 治疗帕金森病的化学遗传学基因治疗新方案

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US4797368A (en) 1985-03-15 1989-01-10 The United States Of America As Represented By The Department Of Health And Human Services Adeno-associated virus as eukaryotic expression vector
US4863457A (en) 1986-11-24 1989-09-05 Lee David A Drug delivery device
US5378475A (en) 1991-02-21 1995-01-03 University Of Kentucky Research Foundation Sustained release drug delivery devices
US5814618A (en) 1993-06-14 1998-09-29 Basf Aktiengesellschaft Methods for regulating gene expression
US5464758A (en) 1993-06-14 1995-11-07 Gossen; Manfred Tight control of gene expression in eucaryotic cells by tetracycline-responsive promoters
US5443505A (en) 1993-11-15 1995-08-22 Oculex Pharmaceuticals, Inc. Biocompatible ocular implants
US6342390B1 (en) 1994-11-23 2002-01-29 The United States Of America As Represented By The Secretary Of Health And Human Services Lipid vesicles containing adeno-associated virus rep protein for transgene integration and gene therapy
FR2814642B1 (fr) 2000-10-03 2005-07-01 Ass Pour Le Dev De La Rech En Souris transgenique pour la recombinaison ciblee mediee par la cre-er modifiee
US6723551B2 (en) 2001-11-09 2004-04-20 The United States Of America As Represented By The Department Of Health And Human Services Production of adeno-associated virus in insect cells
JP2009523006A (ja) * 2004-05-07 2009-06-18 アプレラ コーポレイション 脈管疾患に関連する遺伝的多型、その検出方法および使用
ES2525067T3 (es) * 2005-04-07 2014-12-17 The Trustees Of The University Of Pennsylvania Método de incremento de la función de un vector de AAV
EP2561073B1 (en) * 2010-04-23 2016-08-24 University of Massachusetts Cns targeting aav vectors and methods of use thereof
KR20150020250A (ko) * 2012-06-19 2015-02-25 유니버시티 오브 플로리다 리서치 파운데이션, 인코포레이티드 당뇨병을 치료하기 위한 조성물 및 방법
GB201403684D0 (en) * 2014-03-03 2014-04-16 King S College London Vector
EP3200830B1 (en) * 2014-10-03 2020-09-09 University of Massachusetts High efficiency library-identified aav vectors
AU2016324317A1 (en) * 2015-09-17 2018-03-08 Coda Biotherapeutics, Inc. Compositions and methods for treating neurological disorders
CA3011939A1 (en) * 2016-02-02 2017-08-10 University Of Massachusetts Method to enhance the efficiency of systemic aav gene delivery to the central nervous system
US20170218842A1 (en) * 2016-02-02 2017-08-03 General Electric Company Adjusting Airflow Distortion in Gas Turbine Engine
CA3014732A1 (en) * 2016-03-09 2017-09-14 Fadi ASSAF Using dreadd for neuronal modulation in treating neuronal
MA44546B1 (fr) * 2016-06-15 2021-03-31 Univ California Virus adéno-associés variants et procédés d'utilisation
WO2018008770A1 (ja) * 2016-07-06 2018-01-11 国立研究開発法人国立循環器病研究センター 末梢神経を操作する方法、脳および脊髄を除く臓器などにおいて神経細胞機能を変化させる機能を発生させる方法、および新規疾病の予防または治療方法、ならびに末梢神経投与用医薬
MX2022004812A (es) * 2019-10-22 2023-02-23 Applied Genetic Tech Corporation Sistemas de virus adeno-asociados (aav) para el tratamiento de enfermedades o trastornos neurodegenerativos asociados a la progranulina.

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