JP2021530227A - 非症候性感音性聴力喪失の治療方法 - Google Patents

非症候性感音性聴力喪失の治療方法 Download PDF

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JP2021530227A
JP2021530227A JP2021500888A JP2021500888A JP2021530227A JP 2021530227 A JP2021530227 A JP 2021530227A JP 2021500888 A JP2021500888 A JP 2021500888A JP 2021500888 A JP2021500888 A JP 2021500888A JP 2021530227 A JP2021530227 A JP 2021530227A
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nucleotides
amino acids
amino acid
acid substitutions
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JP2021530227A5 (https=
JPWO2020014625A5 (https=
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ロバート ング，
エマニュエル ジェイ． サイモンズ，
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アコーオス インコーポレイテッド
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JP2021500888A 2018-07-13 2019-07-12 非症候性感音性聴力喪失の治療方法 Pending JP2021530227A (ja)

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US201862697652P 2018-07-13 2018-07-13
US62/697,652 2018-07-13
PCT/US2019/041625 WO2020014625A1 (en) 2018-07-13 2019-07-12 Methods of treating non-syndromic sensorineural hearing loss

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WO2020014625A1 (en) 2018-07-13 2020-01-16 Akouos, Inc. Methods of treating non-syndromic sensorineural hearing loss
JP7846626B2 (ja) * 2020-02-07 2026-04-15 ザ チルドレンズ メディカル センター コーポレーション 大型遺伝子ベクターならびにその送達および使用の方法
US11946065B2 (en) * 2020-07-29 2024-04-02 The Board Of Regents Of The University Of Texas System Transgene cassettes, AAV vectors, and AAV viral vectors for expression of human codon-optimized CSTB
JP2024517843A (ja) * 2021-05-05 2024-04-23 デシベル セラピューティクス インコーポレイテッド ステレオシリン二重ベクター系を使用して感音性難聴を治療するための組成物及び方法
IL308328A (en) * 2021-05-14 2024-01-01 Rescue Hearing Inc Structures and methods of gene therapy to treat hearing loss
EP4416294A2 (en) * 2021-10-12 2024-08-21 Decibel Therapeutics, Inc. Stereocilin promoters and uses thereof

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