JP2021511020A5 - - Google Patents
Info
- Publication number
- JP2021511020A5 JP2021511020A5 JP2020537156A JP2020537156A JP2021511020A5 JP 2021511020 A5 JP2021511020 A5 JP 2021511020A5 JP 2020537156 A JP2020537156 A JP 2020537156A JP 2020537156 A JP2020537156 A JP 2020537156A JP 2021511020 A5 JP2021511020 A5 JP 2021511020A5
- Authority
- JP
- Japan
- Prior art keywords
- raav
- promoter
- raav vector
- aav
- vector according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023062403A JP2023076698A (ja) | 2018-01-17 | 2023-04-06 | ２１－ヒドロキシラーゼ欠損症のためのアデノ随伴ウイルス遺伝子療法 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862618307P | 2018-01-17 | 2018-01-17 | |
| US62/618,307 | 2018-01-17 | ||
| US201862640311P | 2018-03-08 | 2018-03-08 | |
| US62/640,311 | 2018-03-08 | ||
| PCT/US2019/013991 WO2019143803A1 (en) | 2018-01-17 | 2019-01-17 | Adeno-associated virus gene therapy for 21-hydroxylase deficiency |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023062403A Division JP2023076698A (ja) | 2018-01-17 | 2023-04-06 | ２１－ヒドロキシラーゼ欠損症のためのアデノ随伴ウイルス遺伝子療法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021511020A JP2021511020A (ja) | 2021-05-06 |
| JP2021511020A5 true JP2021511020A5 (https=) | 2022-01-26 |
| JP7569216B2 JP7569216B2 (ja) | 2024-10-17 |
Family
ID=65494499
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020537156A Active JP7569216B2 (ja) | 2018-01-17 | 2019-01-17 | ２１－ヒドロキシラーゼ欠損症のためのアデノ随伴ウイルス遺伝子療法 |
| JP2023062403A Pending JP2023076698A (ja) | 2018-01-17 | 2023-04-06 | ２１－ヒドロキシラーゼ欠損症のためのアデノ随伴ウイルス遺伝子療法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023062403A Pending JP2023076698A (ja) | 2018-01-17 | 2023-04-06 | ２１－ヒドロキシラーゼ欠損症のためのアデノ随伴ウイルス遺伝子療法 |
Country Status (8)
| Country | Link |
|---|---|
| US (2) | US12195767B2 (https=) |
| EP (1) | EP3740244B1 (https=) |
| JP (2) | JP7569216B2 (https=) |
| KR (1) | KR102892243B1 (https=) |
| CN (1) | CN111601620A (https=) |
| BR (1) | BR112020014404A2 (https=) |
| CA (1) | CA3088323A1 (https=) |
| WO (1) | WO2019143803A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2022198038A1 (en) | 2021-03-19 | 2022-09-22 | Adrenas Therapeutics, Inc. | Gene therapies for 21-hydroxylase deficiency |
| AU2022366947A1 (en) | 2021-10-12 | 2024-05-02 | Bridgebio Gene Therapy Llc | Methods and compositions for treating leukodystrophies |
| CN115976004B (zh) * | 2022-12-27 | 2024-07-09 | 天津科技大学 | 一种黄体酮17α-羟化酶突变体及其应用 |
| AU2024317892A1 (en) * | 2023-07-29 | 2025-08-28 | Limited Liability Company «Genetic Technologies» (Llc «Genetic Technologies») | Adeno-associated virus-based expression vectors |
Family Cites Families (15)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5478745A (en) | 1992-12-04 | 1995-12-26 | University Of Pittsburgh | Recombinant viral vector system |
| US6136597A (en) | 1997-09-18 | 2000-10-24 | The Salk Institute For Biological Studies | RNA export element |
| WO1999061601A2 (en) | 1998-05-28 | 1999-12-02 | The Government Of The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Aav5 vector and uses thereof |
| PT1453547T (pt) | 2001-12-17 | 2016-12-28 | Univ Pennsylvania | Sequências do vírus adeno-associado (aav) do serotipo 8, vetores contendo as mesmas, e utilizações destas |
| DK2573170T3 (en) | 2001-12-17 | 2018-04-09 | Univ Pennsylvania | Sequences of adeno-associated virus (AAV) serotype 9, vectors containing them, and their use |
| EP1486567A1 (en) | 2003-06-11 | 2004-12-15 | Deutsches Krebsforschungszentrum Stiftung des öffentlichen Rechts | Improved adeno-associated virus (AAV) vector for gene therapy |
| EP2345731B1 (en) | 2003-09-30 | 2015-10-21 | The Trustees of the University of Pennsylvania | Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof |
| US8865881B2 (en) * | 2011-02-22 | 2014-10-21 | California Institute Of Technology | Delivery of proteins using adeno-associated virus (AAV) vectors |
| IL297919A (en) | 2013-07-22 | 2023-01-01 | Childrens Hospital Philadelphia | Variant aav and compositions, methods and uses for gene transfer to cells, organs and tissues |
| WO2015041718A1 (en) | 2013-09-20 | 2015-03-26 | The General Hospital Corporation | Uses of modified mullerian inhibiting substance (mis) proteins for the treatment of neurodegenerative diseases |
| EP3015550A1 (en) | 2014-10-30 | 2016-05-04 | Sanofi | 21-Hydroxylation of steroids |
| EP3054006A1 (en) | 2015-02-09 | 2016-08-10 | Institut National De La Sante Et De La Recherche Medicale (Inserm) | Recombinant adeno-associated virus particle purification with multiple-step anion exchange chromatography |
| HUE069664T2 (hu) * | 2015-07-10 | 2025-04-28 | Univ Guelph | Madár-adenovírus 9 (FADV-9) vektorrendszer és kapcsolódó módszerek |
| WO2017191274A2 (en) * | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| WO2022198038A1 (en) | 2021-03-19 | 2022-09-22 | Adrenas Therapeutics, Inc. | Gene therapies for 21-hydroxylase deficiency |
-
2019
- 2019-01-17 CA CA3088323A patent/CA3088323A1/en active Pending
- 2019-01-17 EP EP19706059.3A patent/EP3740244B1/en active Active
- 2019-01-17 JP JP2020537156A patent/JP7569216B2/ja active Active
- 2019-01-17 KR KR1020207023328A patent/KR102892243B1/ko active Active
- 2019-01-17 BR BR112020014404-5A patent/BR112020014404A2/pt not_active Application Discontinuation
- 2019-01-17 US US16/962,552 patent/US12195767B2/en active Active
- 2019-01-17 CN CN201980008414.XA patent/CN111601620A/zh active Pending
- 2019-01-17 WO PCT/US2019/013991 patent/WO2019143803A1/en not_active Ceased
-
2023
- 2023-04-06 JP JP2023062403A patent/JP2023076698A/ja active Pending
-
2024
- 2024-11-13 US US18/946,854 patent/US20250304925A1/en active Pending