JP2021505159A - 修飾型閉端ｄｎａ（ｃｅｄｎａ）を使用する遺伝子編集 - Google Patents

修飾型閉端ｄｎａ（ｃｅｄｎａ）を使用する遺伝子編集 Download PDF

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JP2021505159A
JP2021505159A JP2020531057A JP2020531057A JP2021505159A JP 2021505159 A JP2021505159 A JP 2021505159A JP 2020531057 A JP2020531057 A JP 2020531057A JP 2020531057 A JP2020531057 A JP 2020531057A JP 2021505159 A JP2021505159 A JP 2021505159A
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itr
cedna vector
sequence
cedna
nuclease
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JP2021505159A5 (https=
Inventor
ロバート エム． コーティン，
ロバート エム． コーティン，
ダグラス カー，
ダグラス カー，
フィリップ サマヨア，
フィリップ サマヨア，
オザン アルカン，
オザン アルカン，
マシュー ジェイ． シモンズ，
マシュー ジェイ． シモンズ，
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ジェネレーション バイオ カンパニー
ジェネレーション バイオ カンパニー
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Publication of JP2021505159A publication Critical patent/JP2021505159A/ja
Publication of JP2021505159A5 publication Critical patent/JP2021505159A5/ja
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JP2020531057A 2017-12-06 2018-12-06 修飾型閉端ｄｎａ（ｃｅｄｎａ）を使用する遺伝子編集 Pending JP2021505159A (ja)

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JP2023195038A JP2024003220A (ja) 2017-12-06 2023-11-16 修飾型閉端ｄｎａ（ｃｅｄｎａ）を使用する遺伝子編集

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US201762595328P 2017-12-06 2017-12-06
US62/595,328 2017-12-06
US201762607069P 2017-12-18 2017-12-18
US62/607,069 2017-12-18
PCT/US2018/064242 WO2019113310A1 (en) 2017-12-06 2018-12-06 Gene editing using a modified closed-ended dna (cedna)

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JP2023195038A Pending JP2024003220A (ja) 2017-12-06 2023-11-16 修飾型閉端ｄｎａ（ｃｅｄｎａ）を使用する遺伝子編集

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US (1) US20220290186A1 (https=)
EP (1) EP3720952A4 (https=)
JP (2) JP2021505159A (https=)
KR (1) KR20200093635A (https=)
CN (1) CN111527200A (https=)
AU (1) AU2018378672A1 (https=)
BR (1) BR112020009858A2 (https=)
CA (1) CA3084185A1 (https=)
IL (1) IL274845A (https=)
MA (1) MA51113A (https=)
MX (1) MX2020005808A (https=)
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Cited By (3)

* Cited by examiner, † Cited by third party
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JP2022506771A (ja) * 2018-11-09 2022-01-17 ジェネレーション バイオ カンパニー 対称的な修飾型逆位末端反復配列を含む修飾型閉端ｄｎａ（ｃｅｄｎａ）
JP2024511026A (ja) * 2021-03-19 2024-03-12 ジェネレーション バイオ カンパニー Ｐｆｉｃ治療薬を発現させるための非ウイルス性ｄｎａベクター及びその使用
JP2024521679A (ja) * 2021-05-20 2024-06-04 シンテニー セラピューティクス， インコーポレイテッド ゲノムセーフハーバー

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