JP2020532546A5 - - Google Patents

Download PDF

Info

Publication number
JP2020532546A5
JP2020532546A5 JP2020512589A JP2020512589A JP2020532546A5 JP 2020532546 A5 JP2020532546 A5 JP 2020532546A5 JP 2020512589 A JP2020512589 A JP 2020512589A JP 2020512589 A JP2020512589 A JP 2020512589A JP 2020532546 A5 JP2020532546 A5 JP 2020532546A5
Authority
JP
Japan
Prior art keywords
lipid
composition
molar ratio
cationic lipid
approximately
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2020512589A
Other languages
English (en)
Japanese (ja)
Other versions
JP7379325B2 (ja
JP2020532546A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2018/042555 external-priority patent/WO2019045897A1/en
Publication of JP2020532546A publication Critical patent/JP2020532546A/ja
Publication of JP2020532546A5 publication Critical patent/JP2020532546A5/ja
Priority to JP2023115742A priority Critical patent/JP2023138526A/ja
Application granted granted Critical
Publication of JP7379325B2 publication Critical patent/JP7379325B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2020512589A 2017-08-31 2018-07-17 組織特異的送達用のカチオン性脂質組成物 Active JP7379325B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023115742A JP2023138526A (ja) 2017-08-31 2023-07-14 組織特異的送達用のカチオン性脂質組成物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762552783P 2017-08-31 2017-08-31
US62/552,783 2017-08-31
PCT/US2018/042555 WO2019045897A1 (en) 2017-08-31 2018-07-17 CATIONIC LIPIDIC COMPOSITIONS FOR TISSUE-SPECIFIC ADMINISTRATION

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023115742A Division JP2023138526A (ja) 2017-08-31 2023-07-14 組織特異的送達用のカチオン性脂質組成物

Publications (3)

Publication Number Publication Date
JP2020532546A JP2020532546A (ja) 2020-11-12
JP2020532546A5 true JP2020532546A5 (enExample) 2022-12-09
JP7379325B2 JP7379325B2 (ja) 2023-11-14

Family

ID=63104088

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020512589A Active JP7379325B2 (ja) 2017-08-31 2018-07-17 組織特異的送達用のカチオン性脂質組成物
JP2023115742A Pending JP2023138526A (ja) 2017-08-31 2023-07-14 組織特異的送達用のカチオン性脂質組成物

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023115742A Pending JP2023138526A (ja) 2017-08-31 2023-07-14 組織特異的送達用のカチオン性脂質組成物

Country Status (8)

Country Link
US (3) US20190060482A1 (enExample)
EP (1) EP3675826B1 (enExample)
JP (2) JP7379325B2 (enExample)
CN (1) CN111065377A (enExample)
AU (1) AU2018324345B2 (enExample)
CA (1) CA3073851A1 (enExample)
LT (1) LT3675826T (enExample)
WO (1) WO2019045897A1 (enExample)

Families Citing this family (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11690921B2 (en) * 2018-05-18 2023-07-04 Sangamo Therapeutics, Inc. Delivery of target specific nucleases
PT4223886T (pt) 2019-04-16 2024-12-20 Genfit Composições e métodos para a estabilização de micro-arn
JP7699552B2 (ja) * 2019-07-03 2025-06-27 ファクター バイオサイエンス インコーポレイテッド カチオン性脂質及びその使用
US10501404B1 (en) 2019-07-30 2019-12-10 Factor Bioscience Inc. Cationic lipids and transfection methods
EP3865122A1 (en) * 2020-02-11 2021-08-18 Pantherna Therapeutics GmbH Lipid composition and use thereof for delivery of a therapeutically active agent to endothelium
JP2025524562A (ja) 2022-06-30 2025-07-30 ライフ テクノロジーズ コーポレーション インビボ送達のための脂質組成物
US20240263196A1 (en) 2022-12-29 2024-08-08 Life Technologies Corporation Lipid Compositions and Methods for Delivery to Immune Cells
CN119997938A (zh) * 2023-06-05 2025-05-13 安徽医科大学第一附属医院 肺靶向纳米胶束、制备方法及应用
TW202543585A (zh) 2024-03-08 2025-11-16 美商健臻公司 脂質奈米粒子
WO2026030375A2 (en) 2024-07-30 2026-02-05 Genzyme Corporation Lipid nanoparticles and methods of manufacture and use thereof
CN118576568B (zh) * 2024-08-06 2024-11-26 北京悦康科创医药科技股份有限公司 一种药物组合物及其制备方法和应用

Family Cites Families (24)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5034506A (en) 1985-03-15 1991-07-23 Anti-Gene Development Group Uncharged morpholino-based polymers having achiral intersubunit linkages
US5235033A (en) 1985-03-15 1993-08-10 Anti-Gene Development Group Alpha-morpholino ribonucleoside derivatives and polymers thereof
US6028077A (en) 1997-04-15 2000-02-22 Rinehart; Kenneth L. Crambescidin compounds
EP1829856A3 (en) * 1998-11-12 2009-02-25 Invitrogen Corporation Transfection reagents
JP2004512345A (ja) 2000-11-02 2004-04-22 スミスクライン・ビーチャム・コーポレイション 受容体アンタゴニスト−脂質コンジュゲートおよびそれを含有するデリバリービヒクル
AU2002360762A1 (en) 2001-12-19 2003-07-09 Alza Corporation Liposomal tumor necrosis factor compositions
WO2005120152A2 (en) 2004-06-07 2005-12-22 Protiva Biotherapeutics, Inc. Cationic lipids and methods of use
US20130189364A1 (en) 2004-07-09 2013-07-25 Robert Sabin Compositions and methods of potentiating adjuvant pharmaceuticals targeting latent viral infections
GB0418172D0 (en) 2004-08-13 2004-09-15 Ic Vec Ltd Vector
WO2009111088A2 (en) * 2008-01-02 2009-09-11 The Johns Hopkins University Antitumor immunization by liposomal delivery of vaccine to the spleen
EP2464336A4 (en) * 2009-08-14 2013-11-20 Alnylam Pharmaceuticals Inc COMPOSITIONS FORMULATED IN LIPIDS AND METHODS OF INHIBITING THE EXPRESSION OF EBOLA VIRUS GENE
AU2010334911A1 (en) * 2009-12-23 2012-07-12 Novartis Ag Lipids, lipid compositions, and methods of using them
JP2014508102A (ja) * 2010-11-15 2014-04-03 ライフ テクノロジーズ コーポレーション アミン含有トランスフェクション試薬ならびにそれを生成および使用するための方法
PT2717893T (pt) * 2011-06-08 2019-08-20 Translate Bio Inc Composições de nanopartículas lipídicas e métodos para transferência de arnm
GR1008018B (el) 2012-09-06 2013-10-29 Ιδρυμα Ιατροβιολογικων Ερευνων Ακαδημιας Αθηνων, Λιπιδικα συμπλοκα αποτελουμενα απο ανιονικα λυσο-λιπιδια και η εφαρμογη αυτων
CN103296033B (zh) 2013-05-28 2016-05-11 京东方科技集团股份有限公司 一种阵列基板及其制作方法
JP2016528890A (ja) * 2013-07-09 2016-09-23 プレジデント アンド フェローズ オブ ハーバード カレッジ CRISPR/Cas系を用いるゲノム編集の治療用の使用
SG10201811729PA (en) 2013-12-12 2019-02-27 Life Technologies Corp Membrane-penetrating peptides to enhance transfection and compositions and methods for using same
WO2016011203A1 (en) * 2014-07-15 2016-01-21 Life Technologies Corporation Compositions with lipid aggregates and methods for efficient delivery of molecules to cells
ES2949540T3 (es) 2015-06-19 2023-09-29 Massachusetts Inst Technology 2,5-piperazinadionas sustituidas con alquenilo y su uso en composiciones para suministrar un agente a un sujeto o una célula
JP6715325B2 (ja) * 2015-06-26 2020-07-01 スーチョウ リボ ライフ サイエンス カンパニー、リミテッドSuzhou Ribo Life Science Co., Ltd. siRNA、siRNAを含む医薬組成物及び結合体、並びにそれらの応用
US10829787B2 (en) 2015-10-14 2020-11-10 Life Technologies Corporation Ribonucleoprotein transfection agents
US11690921B2 (en) * 2018-05-18 2023-07-04 Sangamo Therapeutics, Inc. Delivery of target specific nucleases
EP3846822A4 (en) * 2018-09-04 2022-07-06 The Board Of Regents Of The University Of Texas System COMPOSITIONS AND METHODS FOR ORGAN-SPECIFIC DELIVERY OF NUCLEIC ACIDS

Similar Documents

Publication Publication Date Title
JP7641308B2 (ja) Rna送達のためのイオン化可能なカチオン性脂質
US20260108623A1 (en) Cationic lipid compositions for tissue-specific delivery
JP7778711B2 (ja) ポリサルコシンを含むrna粒子
JP2024534697A5 (enExample)
CN104428005A (zh) 用于反义寡核苷酸递送的脂质纳米颗粒组合物
CN1295465A (zh) 脂质体组合物和喹诺酮的给药方法
CN108024960A (zh) 含有阴离子药物的药物组合物及其制备方法
US20190328665A1 (en) Liposome compositions encapsulating modified cyclodextrin complexes and uses thereof
JP7821776B2 (ja) 効率的な核酸送達のための担体
JP7829485B2 (ja) がんの処置において有用なToll様受容体(「TLR」)アゴニストプロドラッグを含有する製剤化および/または共製剤化リポソーム組成物ならびにその方法
US20240209397A1 (en) Thermally Stable Lipid-Nucleic Acid Molecule Formulations Utilising Metal Organic Framework (MOF) Shells
JP2023518944A5 (enExample)
WO2023246218A1 (zh) 用于核酸递送的可电离脂质及其组合物
JP2025501905A (ja) イオン化脂質、脂質ナノ粒子、及びこれらの使用
KR102921785B1 (ko) 핵산 전달용 사이클로알칸계 지질 화합물 및 이를 포함하는 지질 나노입자
WO2024017254A1 (zh) 氨基脂质化合物、其制备方法和应用
WO2014030601A1 (ja) アニオン性を有する新規ナノバブルポリ-リポ・プレックスの製造方法
JP2025516637A5 (enExample)
US12064512B2 (en) Silyl lipids suitable for enhanced delivery of anti-viral therapeutics
US20220378936A1 (en) Delivery system complexes comprising a precipitate of an active agent and methods of use
JP2003522203A (ja) 天然に存在しない核酸組成物、核酸を細胞中にトランスフェクションするのに有用な処方物の調製のためのそれらの使用、および応用
KR20260071091A (ko) 신규 이온화 지질 및 이를 포함하는 지질 나노입자
CN119424366A (zh) 靶向次级淋巴器官的脂质纳米颗粒及其制备方法和用途
CA3258341A1 (en) Nucleic acids encoding a constituently active cyclic GMP-AMP synthase and associated immunogenic delivery vehicles
WO2023239593A1 (en) Method for sustained delivery of mrna vaccines