JP2020511991A5 - - Google Patents
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- Publication number
- JP2020511991A5 JP2020511991A5 JP2019553350A JP2019553350A JP2020511991A5 JP 2020511991 A5 JP2020511991 A5 JP 2020511991A5 JP 2019553350 A JP2019553350 A JP 2019553350A JP 2019553350 A JP2019553350 A JP 2019553350A JP 2020511991 A5 JP2020511991 A5 JP 2020511991A5
- Authority
- JP
- Japan
- Prior art keywords
- lentiviral vector
- item
- vector according
- cell
- hiv
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023005869A JP2023033551A (ja) | 2017-03-29 | 2023-01-18 | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762478375P | 2017-03-29 | 2017-03-29 | |
| US62/478,375 | 2017-03-29 | ||
| US201762489149P | 2017-04-24 | 2017-04-24 | |
| US62/489,149 | 2017-04-24 | ||
| PCT/US2018/025165 WO2018183692A1 (en) | 2017-03-29 | 2018-03-29 | Vectors and compositions for treating hemoglobinopathies |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023005869A Division JP2023033551A (ja) | 2017-03-29 | 2023-01-18 | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020511991A JP2020511991A (ja) | 2020-04-23 |
| JP2020511991A5 true JP2020511991A5 (https=) | 2021-04-30 |
| JP7228523B2 JP7228523B2 (ja) | 2023-02-24 |
Family
ID=63677097
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019553350A Active JP7228523B2 (ja) | 2017-03-29 | 2018-03-29 | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
| JP2023005869A Withdrawn JP2023033551A (ja) | 2017-03-29 | 2023-01-18 | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023005869A Withdrawn JP2023033551A (ja) | 2017-03-29 | 2023-01-18 | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20220259594A1 (https=) |
| EP (1) | EP3600448A4 (https=) |
| JP (2) | JP7228523B2 (https=) |
| CN (1) | CN110582305A (https=) |
| AU (1) | AU2018243293A1 (https=) |
| BR (1) | BR112019020322A2 (https=) |
| CA (1) | CA3057862A1 (https=) |
| IL (1) | IL269551A (https=) |
| SG (1) | SG11201908844YA (https=) |
| WO (1) | WO2018183692A1 (https=) |
Families Citing this family (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US11008561B2 (en) | 2014-06-30 | 2021-05-18 | Bioverativ Therapeutics Inc. | Optimized factor IX gene |
| JP7228523B2 (ja) * | 2017-03-29 | 2023-02-24 | ブルーバード バイオ， インコーポレイテッド | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
| US20220160788A1 (en) * | 2019-03-22 | 2022-05-26 | INSERM (Institut National de la Santé et de la Recherche Médicale) | Bifunctional vectors allowing bcl11a silencing and expression of an anti-sickling hbb and uses thereof for gene therapy of b-hemoglobinopathies |
| EP3980549A4 (en) * | 2019-06-05 | 2023-07-26 | Orchard Therapeutics (Europe) Limited | COMPOSITIONS AND METHODS FOR MODIFYING EUKARYOT CELLS |
| KR20220097891A (ko) * | 2019-09-30 | 2022-07-08 | 바이오버라티브 테라퓨틱스 인크. | 렌티바이러스 벡터 제형 |
| CN117384967A (zh) * | 2020-04-24 | 2024-01-12 | 康霖生物科技（杭州）有限公司 | 一种核酸构建体 |
| US20240350664A1 (en) * | 2020-11-23 | 2024-10-24 | Intas Pharmaceuticals Ltd. | Gene therapy based administration of lentivirus vector for treating hemoglobinopathies |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8383604B2 (en) * | 2008-09-15 | 2013-02-26 | Children's Medical Center Corporation | Modulation of BCL11A for treatment of hemoglobinopathies |
| ES2769270T3 (es) * | 2011-09-30 | 2020-06-25 | Bluebird Bio Inc | Compuestos para transducción viral mejorada |
| WO2014093965A1 (en) * | 2012-12-14 | 2014-06-19 | Case Western Reserve University | Genomic rna packaging enhancer element |
| MX375592B (es) * | 2014-04-25 | 2025-03-06 | The Children´S Medical Center Corp | Composiciones y su uso para tratar hemoglobinopatias. |
| PL3134432T3 (pl) * | 2014-04-25 | 2020-10-19 | Bluebird Bio, Inc. | Promotor mnd chimeryczne receptory antygenowe |
| US20170049819A1 (en) * | 2014-04-25 | 2017-02-23 | Bluebird Bio, Inc. | Kappa/lambda chimeric antigen receptors |
| EP3620521B1 (en) | 2014-09-04 | 2024-05-29 | Memorial Sloan-Kettering Cancer Center | Globin gene therapy for treating hemoglobinopathies |
| HRP20191873T1 (hr) * | 2014-12-12 | 2020-01-24 | Bluebird Bio, Inc. | Kimerni antigenski receptori |
| LT3277807T (lt) | 2015-03-31 | 2020-01-10 | Glycotope Gmbh | Eukariotiniai ekspresijos vektoriai, apimantys globino genų klasterių reguliavimo elementus |
| WO2017040529A1 (en) | 2015-08-31 | 2017-03-09 | Bluebird Bio, Inc. | Anti-sialyl tn chimeric antigen receptors |
| JP7228523B2 (ja) * | 2017-03-29 | 2023-02-24 | ブルーバード バイオ， インコーポレイテッド | ヘモグロビン異常症を治療するためのベクターおよび組成物 |
| US11261441B2 (en) * | 2017-03-29 | 2022-03-01 | Bluebird Bio, Inc. | Vectors and compositions for treating hemoglobinopathies |
-
2018
- 2018-03-29 JP JP2019553350A patent/JP7228523B2/ja active Active
- 2018-03-29 AU AU2018243293A patent/AU2018243293A1/en not_active Abandoned
- 2018-03-29 SG SG11201908844Y patent/SG11201908844YA/en unknown
- 2018-03-29 WO PCT/US2018/025165 patent/WO2018183692A1/en not_active Ceased
- 2018-03-29 EP EP18775163.1A patent/EP3600448A4/en active Pending
- 2018-03-29 CA CA3057862A patent/CA3057862A1/en active Pending
- 2018-03-29 BR BR112019020322-2A patent/BR112019020322A2/pt not_active Application Discontinuation
- 2018-03-29 CN CN201880027694.4A patent/CN110582305A/zh active Pending
-
2019
- 2019-09-23 IL IL26955119A patent/IL269551A/en unknown
-
2022
- 2022-01-28 US US17/587,999 patent/US20220259594A1/en active Pending
-
2023
- 2023-01-18 JP JP2023005869A patent/JP2023033551A/ja not_active Withdrawn
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