JP2020506714A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2020506714A5 JP2020506714A5 JP2019542703A JP2019542703A JP2020506714A5 JP 2020506714 A5 JP2020506714 A5 JP 2020506714A5 JP 2019542703 A JP2019542703 A JP 2019542703A JP 2019542703 A JP2019542703 A JP 2019542703A JP 2020506714 A5 JP2020506714 A5 JP 2020506714A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- nucleic acid
- ids
- apoeii
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GBGB1701968.8A GB201701968D0 (en) | 2017-02-07 | 2017-02-07 | Gene therapy |
| GB1701968.8 | 2017-02-07 | ||
| PCT/GB2018/050347 WO2018146473A1 (en) | 2017-02-07 | 2018-02-07 | Gene therapy |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020506714A JP2020506714A (ja) | 2020-03-05 |
| JP2020506714A5 true JP2020506714A5 (enExample) | 2021-03-25 |
| JP7237364B2 JP7237364B2 (ja) | 2023-03-13 |
Family
ID=58462471
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019542703A Active JP7237364B2 (ja) | 2017-02-07 | 2018-02-07 | 遺伝子治療 |
Country Status (6)
| Country | Link |
|---|---|
| US (2) | US11701390B2 (enExample) |
| EP (2) | EP3960188B1 (enExample) |
| JP (1) | JP7237364B2 (enExample) |
| ES (2) | ES3035262T3 (enExample) |
| GB (1) | GB201701968D0 (enExample) |
| WO (1) | WO2018146473A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201701968D0 (en) * | 2017-02-07 | 2017-03-22 | Univ Manchester | Gene therapy |
| BR112020005271A2 (pt) | 2017-10-02 | 2020-09-15 | Denali Therapeutics Inc. | proteína, polipeptídeo, polinucleotídeo, vetor, célula hospedeira, método para produção de um polipeptídeo, métodos de tratamento de um distúrbio, de diminuição do acúmulo, de monitoramento, de transporte de um agente e de tratamento de um lsd e composição farmacêutica |
| WO2024096738A1 (en) | 2022-11-01 | 2024-05-10 | Erasmus University Medical Center Rotterdam | Gene therapy constructs for metabolic disorders |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003286870A1 (en) | 2003-06-05 | 2005-01-04 | Salk Institute For Biological Studies | Targeting polypeptides to the central nervous system |
| EP1694345A1 (en) | 2003-12-04 | 2006-08-30 | Regents Of The University Of Minnesota | Compositions and methods for the treatment of lysosomal storage disorders |
| US10227387B2 (en) | 2011-05-18 | 2019-03-12 | Children's Hospital Medical Center | Targeted delivery of proteins across the blood-brain barrier |
| US20140335163A1 (en) | 2011-12-01 | 2014-11-13 | Angiochem Inc. | Targeted iduronate-2-sulfatase compounds |
| JP2017534640A (ja) * | 2014-11-10 | 2017-11-24 | アレクシオン ファーマシューティカルズ， インコーポレイテッド | アルファ−ｌ−イズロニダーゼ、イズロン酸−２−スルファターゼおよびアルファガラクトシダーゼａの治療用組成物ならびにそれらの使用方法 |
| GB201701968D0 (en) * | 2017-02-07 | 2017-03-22 | Univ Manchester | Gene therapy |
-
2017
- 2017-02-07 GB GBGB1701968.8A patent/GB201701968D0/en not_active Ceased
-
2018
- 2018-02-07 ES ES21187825T patent/ES3035262T3/es active Active
- 2018-02-07 EP EP21187825.1A patent/EP3960188B1/en active Active
- 2018-02-07 JP JP2019542703A patent/JP7237364B2/ja active Active
- 2018-02-07 ES ES18705462T patent/ES2895263T3/es active Active
- 2018-02-07 WO PCT/GB2018/050347 patent/WO2018146473A1/en not_active Ceased
- 2018-02-07 EP EP18705462.2A patent/EP3579849B1/en active Active
- 2018-02-07 US US16/484,311 patent/US11701390B2/en active Active
-
2022
- 2022-12-22 US US18/086,719 patent/US20230390340A1/en active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| Luoni et al. | Whole brain delivery of an instability-prone Mecp2 transgene improves behavioral and molecular pathological defects in mouse models of Rett syndrome | |
| Rashnonejad et al. | Fetal gene therapy using a single injection of recombinant AAV9 rescued SMA phenotype in mice | |
| Rhein et al. | Interferon-γ inhibits Ebola virus infection | |
| CN111658670B (zh) | 溶瘤腺病毒载体与过继t细胞治疗组合物及其用途 | |
| JP7376018B2 (ja) | 内皮特異的核酸調節エレメントならびにその方法および使用 | |
| Marten et al. | MHV infection of the CNS: mechanisms of immune-mediated control | |
| JP2023115125A (ja) | フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター | |
| JP2022507454A5 (enExample) | ||
| Wang et al. | Treating tumors with a vaccinia virus expressing IFNβ illustrates the complex relationships between oncolytic ability and immunogenicity | |
| Yang et al. | Systemic administration of AAV-Slc25a46 mitigates mitochondrial neuropathy in Slc25a46−/− mice | |
| JP2017523802A (ja) | リソソーム蓄積症処置用のアデノ随伴ウイルスベクター | |
| JP2019520841A5 (enExample) | ||
| JP2020515572A (ja) | 横隔膜特異的核酸調節エレメントならびにその方法および使用 | |
| JP2019517815A (ja) | 細胞傷害性免疫細胞による攻撃に対してがん細胞を増感させるためのｎｋｇ２ｄ活性化リガンドタンパク質の発現 | |
| WO2021042944A1 (zh) | 肌肉靶向的微环dna基因治疗 | |
| Danaeifar | Recent advances in gene therapy: genetic bullets to the root of the problem | |
| Jo et al. | Therapeutic adenine base editing corrects nonsense mutation and improves visual function in a mouse model of Leber congenital amaurosis | |
| Hamana et al. | Amelioration of experimental autoimmune encephalomyelitis in mice by interferon-beta gene therapy, using a long-term expression plasmid vector | |
| Burnet et al. | Hemin treatment drives viral reactivation and plasma cell differentiation of EBV latently infected B cells | |
| Lundstrom | Application of viruses for gene therapy and vaccine development | |
| JP2023548118A5 (enExample) | ||
| Barreto et al. | Animal models for depression associated with HIV-1 infection | |
| TW202440138A (zh) | Pah調節系統及方法 | |
| US20220290157A1 (en) | Compositions and methods for treating amyotrophic lateral sclerosis | |
| US20240318147A1 (en) | Recombinant oncolytic virus, and construction method therefor and use thereof |