JP2019531754A5 - - Google Patents

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JP2019531754A5
JP2019531754A5 JP2019522537A JP2019522537A JP2019531754A5 JP 2019531754 A5 JP2019531754 A5 JP 2019531754A5 JP 2019522537 A JP2019522537 A JP 2019522537A JP 2019522537 A JP2019522537 A JP 2019522537A JP 2019531754 A5 JP2019531754 A5 JP 2019531754A5
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cell
nuclease
cell according
endogenous
endogenous il2rg
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JP2019522537A
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JP2019531754A (ja
JP7108608B2 (ja
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Priority claimed from PCT/US2017/059197 external-priority patent/WO2018081775A1/en
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Priority to JP2022083035A priority Critical patent/JP2022105621A/ja
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JP2019522537A 2016-10-31 2017-10-31 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正 Expired - Fee Related JP7108608B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2022083035A JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662415056P 2016-10-31 2016-10-31
US62/415,056 2016-10-31
PCT/US2017/059197 WO2018081775A1 (en) 2016-10-31 2017-10-31 Gene correction of scid-related genes in hematopoietic stem and progenitor cells

Related Child Applications (1)

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JP2022083035A Division JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

Publications (3)

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JP2019531754A JP2019531754A (ja) 2019-11-07
JP2019531754A5 true JP2019531754A5 (https=) 2020-09-24
JP7108608B2 JP7108608B2 (ja) 2022-07-28

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JP2019522537A Expired - Fee Related JP7108608B2 (ja) 2016-10-31 2017-10-31 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正
JP2022083035A Pending JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

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JP2022083035A Pending JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

Country Status (6)

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US (1) US11020492B2 (https=)
EP (1) EP3532106A4 (https=)
JP (2) JP7108608B2 (https=)
AU (1) AU2017347928A1 (https=)
CA (1) CA3041668A1 (https=)
WO (1) WO2018081775A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11214789B2 (en) 2016-05-03 2022-01-04 Flodesign Sonics, Inc. Concentration and washing of particles with acoustics
KR102828669B1 (ko) * 2019-11-13 2025-07-02 더 리전트 오브 더 유니버시티 오브 캘리포니아 재조합 활성화 유전자 1 (rag1) 중증 복합 면역결핍증 (scid) 을 치료하기 위한 조혈 줄기 세포에서의 렌티바이러스 벡터
EP4087617A4 (en) * 2020-01-10 2024-05-01 Solid Biosciences Inc. VIRAL VECTOR FOR COMBINATION THERAPY

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