JP2018534946A5 - - Google Patents

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Publication number
JP2018534946A5
JP2018534946A5 JP2018542687A JP2018542687A JP2018534946A5 JP 2018534946 A5 JP2018534946 A5 JP 2018534946A5 JP 2018542687 A JP2018542687 A JP 2018542687A JP 2018542687 A JP2018542687 A JP 2018542687A JP 2018534946 A5 JP2018534946 A5 JP 2018534946A5
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JP
Japan
Prior art keywords
fragment
seq
nucleic acid
acid sequence
polynucleotide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2018542687A
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English (en)
Japanese (ja)
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JP2018534946A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2016/059151 external-priority patent/WO2017075237A2/en
Publication of JP2018534946A publication Critical patent/JP2018534946A/ja
Publication of JP2018534946A5 publication Critical patent/JP2018534946A5/ja
Pending legal-status Critical Current

Links

JP2018542687A 2015-10-27 2016-10-27 キメラ転写後調節要素 Pending JP2018534946A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562246841P 2015-10-27 2015-10-27
US62/246,841 2015-10-27
PCT/US2016/059151 WO2017075237A2 (en) 2015-10-27 2016-10-27 Chimeric post-transcriptional regulatory element

Publications (2)

Publication Number Publication Date
JP2018534946A JP2018534946A (ja) 2018-11-29
JP2018534946A5 true JP2018534946A5 (cg-RX-API-DMAC7.html) 2019-12-05

Family

ID=58561919

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2018542687A Pending JP2018534946A (ja) 2015-10-27 2016-10-27 キメラ転写後調節要素

Country Status (6)

Country Link
US (2) US10190135B2 (cg-RX-API-DMAC7.html)
EP (1) EP3368672B1 (cg-RX-API-DMAC7.html)
JP (1) JP2018534946A (cg-RX-API-DMAC7.html)
CN (1) CN108291238A (cg-RX-API-DMAC7.html)
IL (1) IL259010A (cg-RX-API-DMAC7.html)
WO (1) WO2017075237A2 (cg-RX-API-DMAC7.html)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11713468B2 (en) 2017-08-02 2023-08-01 Dna Twopointo Inc. DNA vectors and elements for sustained gene expression in eukaryotic cells
CA3161115A1 (en) * 2018-12-07 2020-06-11 Celltheon Corporation Matrix attachment regions and uses in promoting gene expression
EP3983449A1 (en) 2019-06-11 2022-04-20 Shire Human Genetic Therapies, Inc. Adeno associated viral vector delivery of antibodies for the treatment of disease mediated dysregulated plasma kallikrein
JP7659550B2 (ja) 2019-10-23 2025-04-09 シャイアー ヒューマン ジェネティック セラピーズ インコーポレイテッド アデノ随伴ウイルスベクターに基づく遺伝性血管浮腫のための遺伝子治療
CN116829595A (zh) 2020-12-16 2023-09-29 武田药品工业株式会社 用于治疗由失调的血浆激肽释放酶介导的疾病的抗体的腺相关病毒载体递送

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6136597A (en) * 1997-09-18 2000-10-24 The Salk Institute For Biological Studies RNA export element
EP1706153A1 (en) * 2003-12-04 2006-10-04 Childrens Hospital of Los Angeles Research Institute Minimal lentiviral vector system
EP2914731B1 (en) * 2012-11-01 2019-09-11 California Institute of Technology Reversible gene expression
HUE052552T2 (hu) * 2014-04-09 2021-05-28 Dna Twopointo Inc Javított nukleinsav-konstrukciók eukarióta génexpresszióhoz
WO2015164759A2 (en) * 2014-04-25 2015-10-29 Bluebird Bio, Inc. Mnd promoter chimeric antigen receptors

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