JP2014523748A5 - - Google Patents

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JP2014523748A5
JP2014523748A5 JP2014522973A JP2014522973A JP2014523748A5 JP 2014523748 A5 JP2014523748 A5 JP 2014523748A5 JP 2014522973 A JP2014522973 A JP 2014522973A JP 2014522973 A JP2014522973 A JP 2014522973A JP 2014523748 A5 JP2014523748 A5 JP 2014523748A5
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Japan
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composition
protein
stem cells
cell
cells
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JP2014522973A
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Japanese (ja)
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JP2014523748A (ja
JP6072788B2 (ja
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Priority claimed from PCT/US2012/048176 external-priority patent/WO2013016446A2/en
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Publication of JP2014523748A5 publication Critical patent/JP2014523748A5/ja
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JP2014522973A 2011-07-25 2012-07-25 嚢胞性線維症膜コンダクタンス制御因子（ｃｆｔｒ）遺伝子を改変するための方法および組成物 Expired - Fee Related JP6072788B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201161511434P 2011-07-25 2011-07-25
US61/511,434 2011-07-25
PCT/US2012/048176 WO2013016446A2 (en) 2011-07-25 2012-07-25 Methods and compositions for alteration of a cystic fibrosis transmembrane conductance regulator (cftr) gene

Publications (3)

Publication Number Publication Date
JP2014523748A JP2014523748A (ja) 2014-09-18
JP2014523748A5 true JP2014523748A5 (enExample) 2015-07-16
JP6072788B2 JP6072788B2 (ja) 2017-02-01

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JP2014522973A Expired - Fee Related JP6072788B2 (ja) 2011-07-25 2012-07-25 嚢胞性線維症膜コンダクタンス制御因子（ｃｆｔｒ）遺伝子を改変するための方法および組成物

Country Status (6)

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US (2) US9161995B2 (enExample)
EP (1) EP2737063B1 (enExample)
JP (1) JP6072788B2 (enExample)
AU (1) AU2012286901B2 (enExample)
CA (1) CA2841541C (enExample)
WO (1) WO2013016446A2 (enExample)

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WO2019051097A1 (en) 2017-09-08 2019-03-14 The Regents Of The University Of California RNA-GUIDED ENDONUCLEASE FUSION POLYPEPTIDES AND METHODS OF USING SAME
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