JP2011511090A - 治療用タンパク質をコードする発現ベクターの硝子体内投与による光受容体のレスキュー方法 - Google Patents
治療用タンパク質をコードする発現ベクターの硝子体内投与による光受容体のレスキュー方法 Download PDFInfo
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| US2699008P | 2008-02-07 | 2008-02-07 | |
| US9322808P | 2008-08-29 | 2008-08-29 | |
| PCT/US2009/033275 WO2009100253A1 (en) | 2008-02-07 | 2009-02-05 | Rescue of photoreceptors by intravitreal administation of an expression vector encoding a therapeutic protein |
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| CN101980668A (zh) * | 2008-02-07 | 2011-02-23 | 赛拉基因公司 | 通过玻璃体内施用编码治疗用蛋白质的表达载体救援光感器 |
| GB201103062D0 (en) * | 2011-02-22 | 2011-04-06 | Isis Innovation | Method |
| SG10201704505TA (en) * | 2011-02-25 | 2017-06-29 | Riken | Method of producing retinal pigment epithelial cell sheet |
| JP6199965B2 (ja) * | 2012-07-11 | 2017-09-20 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | Ｒｐｇｒｘ連鎖性網膜変性のａａｖ媒介型遺伝子治療 |
| US20160256571A1 (en) * | 2013-09-30 | 2016-09-08 | Sanofi | Invention |
| MX379027B (es) * | 2013-12-06 | 2025-03-10 | Inst Nat Sante Rech Med | Metodos y composiciones farmaceuticas para la expresion de un polinucleotido de interes en el epitelio pigmentario retiniano de un sujeto. |
| WO2016164920A1 (en) * | 2015-04-09 | 2016-10-13 | Cornell University | Gene therapy to prevent reactions to allergens |
| KR102312253B1 (ko) * | 2015-12-04 | 2021-10-15 | 쏘흐본느 유니베흐시테 | 프로모터 및 이의 용도 |
| WO2017187272A1 (en) * | 2016-04-29 | 2017-11-02 | Gensight Biologics Sa | Optogenetic visual restoration using chrimson |
| PL239642B1 (pl) * | 2018-08-16 | 2021-12-20 | Pomorski Univ Medyczny W Szczecinie | Kompozycja do doszklistkowego podawania białka leczniczego |
| MX2023004602A (es) | 2020-10-22 | 2023-06-22 | Visgenx Inc | Constructos de elovl2 para terapia genica humana. |
| AU2023390868A1 (en) * | 2022-12-05 | 2025-06-19 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Pigment epithelium-derived factor peptides and use for treating retinal degeneration |
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| JP2002539176A (ja) * | 1999-03-15 | 2002-11-19 | カイロン コーポレイション | 眼の疾患を処置または予防するための組換え遺伝子送達ベクターの使用 |
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| US5932479A (en) | 1988-09-26 | 1999-08-03 | Auburn University | Genetic engineering of plant chloroplasts |
| WO2004005467A2 (en) | 2002-07-03 | 2004-01-15 | University Of Central Florida | Expression of human interferon in transgenic chloroplasts |
| CA2358296A1 (en) * | 1999-01-05 | 2000-07-13 | Anthony P. Adamis | Targeted transscleral controlled release drug delivery to the retina and choroid |
| US6943153B1 (en) * | 1999-03-15 | 2005-09-13 | The Regents Of The University Of California | Use of recombinant gene delivery vectors for treating or preventing diseases of the eye |
| CA2401855A1 (en) | 2000-02-29 | 2001-09-07 | Auburn University | Genetic engineering of drought tolerance via a plastid genome |
| AU2001276813A1 (en) | 2000-03-01 | 2001-10-08 | Auburn University | Pharmaceutical proteins, human therapeutics, human serum albumin, insulin, native cholera toxic b submitted on transgenics plastids |
| US7354760B2 (en) | 2001-12-26 | 2008-04-08 | University Of Central Florida Research Foundation, Inc. | Expression of protective antigens in transgenic chloroplasts |
| US20100172871A1 (en) * | 2005-02-17 | 2010-07-08 | Flannery John G | Muller Cell Specific Gene Therapy |
| US20060188481A1 (en) * | 2005-02-22 | 2006-08-24 | Saitama Medical School | Methods for prophylactically or therapeutically treating an animal for an ocular-related disorder |
| CN101305091A (zh) * | 2005-02-24 | 2008-11-12 | 斯克里普斯研究学院 | 分离的髓样骨髓细胞群及用其治疗的方法 |
| EP1885173A4 (en) | 2005-05-27 | 2009-02-18 | Univ Central Florida | CHLOROPLASTE DEVELOPED FOR THE EXPRESSION OF PHARMACEUTICAL PROTEINS |
| CN101980668A (zh) * | 2008-02-07 | 2011-02-23 | 赛拉基因公司 | 通过玻璃体内施用编码治疗用蛋白质的表达载体救援光感器 |
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| JP2002512627A (ja) * | 1997-06-11 | 2002-04-23 | アコーダ セラピーティックス | Ｃｎｓ神経再生組成物及びその使用方法 |
| JP2002539176A (ja) * | 1999-03-15 | 2002-11-19 | カイロン コーポレイション | 眼の疾患を処置または予防するための組換え遺伝子送達ベクターの使用 |
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| US8420619B2 (en) | 2013-04-16 |
| US20090202505A1 (en) | 2009-08-13 |
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| US20120316112A1 (en) | 2012-12-13 |
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| AU2009212309B2 (en) | 2014-04-03 |
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| AU2009212309A1 (en) | 2009-08-13 |
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| US8242093B2 (en) | 2012-08-14 |
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