HUE031655T2 - Csontot targetáló alkálikus foszfatáz, készletek és eljárások alkalmazásukra - Google Patents

Csontot targetáló alkálikus foszfatáz, készletek és eljárások alkalmazásukra

Info

Publication number
HUE031655T2
HUE031655T2 HUE13002327A HUE13002327A HUE031655T2 HU E031655 T2 HUE031655 T2 HU E031655T2 HU E13002327 A HUE13002327 A HU E13002327A HU E13002327 A HUE13002327 A HU E13002327A HU E031655 T2 HUE031655 T2 HU E031655T2
Authority
HU
Hungary
Prior art keywords
amino acid
alkaline phosphatase
kits
methods
absent
Prior art date
Application number
HUE13002327A
Other languages
English (en)
Hungarian (hu)
Inventor
Philippe Crine
Guy Boileau
Thomas P Loisel
Isabelle Lemire
Pierre Leonard
Robert Heft
Hal Landy
Original Assignee
Alexion Pharma Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Alexion Pharma Inc filed Critical Alexion Pharma Inc
Publication of HUE031655T2 publication Critical patent/HUE031655T2/hu

Links

Classifications

    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N9/00Enzymes; Proenzymes; Compositions thereof; Processes for preparing, activating, inhibiting, separating or purifying enzymes
    • C12N9/14Hydrolases (3)
    • C12N9/16Hydrolases (3) acting on ester bonds (3.1)
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P1/00Drugs for disorders of the alimentary tract or the digestive system
    • A61P1/02Stomatological preparations, e.g. drugs for caries, aphtae, periodontitis
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P19/00Drugs for skeletal disorders
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P19/00Drugs for skeletal disorders
    • A61P19/08Drugs for skeletal disorders for bone diseases, e.g. rachitism, Paget's disease
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y301/00Hydrolases acting on ester bonds (3.1)
    • C12Y301/03Phosphoric monoester hydrolases (3.1.3)
    • C12Y301/03001Alkaline phosphatase (3.1.3.1)
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00Medicinal preparations containing peptides
    • CCHEMISTRY; METALLURGY
    • C07ORGANIC CHEMISTRY
    • C07KPEPTIDES
    • C07K2319/00Fusion polypeptide
    • C07K2319/33Fusion polypeptide fusions for targeting to specific cell types, e.g. tissue specific targeting, targeting of a bacterial subspecies
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2799/00Uses of viruses
    • C12N2799/02Uses of viruses as vector
    • C12N2799/021Uses of viruses as vector for the expression of a heterologous nucleic acid
    • C12N2799/025Uses of viruses as vector for the expression of a heterologous nucleic acid where the vector is derived from a parvovirus

Landscapes

  • Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Organic Chemistry (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • General Health & Medical Sciences (AREA)
  • Wood Science & Technology (AREA)
  • Zoology (AREA)
  • Genetics & Genomics (AREA)
  • Medicinal Chemistry (AREA)
  • Biochemistry (AREA)
  • General Engineering & Computer Science (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Animal Behavior & Ethology (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Molecular Biology (AREA)
  • Microbiology (AREA)
  • Biotechnology (AREA)
  • Biomedical Technology (AREA)
  • Rheumatology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Peptides Or Proteins (AREA)
  • Materials For Medical Uses (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Cereal-Derived Products (AREA)
  • Adornments (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Measuring Or Testing Involving Enzymes Or Micro-Organisms (AREA)
  • Immobilizing And Processing Of Enzymes And Microorganisms (AREA)
HUE13002327A 2007-05-11 2008-05-12 Csontot targetáló alkálikus foszfatáz, készletek és eljárások alkalmazásukra HUE031655T2 (hu)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US91758907P 2007-05-11 2007-05-11

Publications (1)

Publication Number Publication Date
HUE031655T2 true HUE031655T2 (hu) 2017-07-28

Family

ID=40001639

Family Applications (2)

Application Number Title Priority Date Filing Date
HUE13002327A HUE031655T2 (hu) 2007-05-11 2008-05-12 Csontot targetáló alkálikus foszfatáz, készletek és eljárások alkalmazásukra
HUS1600005C HUS1600005I1 (hu) 2007-05-11 2016-01-15 Csontra irányuló lúgos foszfatáz, kitek és eljárások alkalmazásukra

Family Applications After (1)

Application Number Title Priority Date Filing Date
HUS1600005C HUS1600005I1 (hu) 2007-05-11 2016-01-15 Csontra irányuló lúgos foszfatáz, kitek és eljárások alkalmazásukra

Country Status (25)

Country Link
US (1) US20100297119A1 (OSRAM)
EP (3) EP2158319B1 (OSRAM)
JP (1) JP5732603B2 (OSRAM)
AT (1) ATE536413T1 (OSRAM)
AU (1) AU2008250945B2 (OSRAM)
BR (2) BR122019000505B1 (OSRAM)
CA (1) CA2687001C (OSRAM)
CY (1) CY2016005I2 (OSRAM)
DE (1) DE202008018131U1 (OSRAM)
DK (3) DK2158319T3 (OSRAM)
ES (3) ES2471915T3 (OSRAM)
FR (1) FR16C0007I2 (OSRAM)
HR (1) HRP20140416T1 (OSRAM)
HU (2) HUE031655T2 (OSRAM)
IL (1) IL202057A0 (OSRAM)
LT (1) LTC2368999I2 (OSRAM)
LU (1) LU92976I2 (OSRAM)
ME (1) ME01828B (OSRAM)
NL (1) NL300798I2 (OSRAM)
NO (1) NO2016002I2 (OSRAM)
PL (3) PL2158319T4 (OSRAM)
PT (3) PT2368999E (OSRAM)
RS (1) RS53302B (OSRAM)
SI (2) SI2662448T1 (OSRAM)
WO (1) WO2008138131A1 (OSRAM)

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DE602005027461D1 (de) 2004-04-21 2011-05-26 Enobia Pharma Inc Konjugate zur zuführung an knochen und verfahren zu deren verwendung beim hinführen von proteinen zum knochen
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US8784833B2 (en) * 2006-06-27 2014-07-22 Saint Louis University Prenatal enzyme replacement therapy for hypophosphatasia
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SG185079A1 (en) * 2010-04-30 2012-12-28 Alexion Pharma Internat Sarl Methods, compositions, and kits for the treatment of matrix mineralization disorders
KR102066996B1 (ko) 2010-07-28 2020-01-17 글리크닉 인코포레이티드 순차적으로 다중화된 면역글로불린 fc 조성물을 제조하기 위한 천연 인간 단백질 단편들의 융합 단백질
CA2823066A1 (en) 2010-12-27 2012-07-05 Alexion Pharma International Sarl Compositions comprising natriuretic peptides and methods of use thereof
KR20140084201A (ko) * 2011-10-19 2014-07-04 알렉시온 파마 홀딩 알칼리성 포스파타제 및/또는 나트륨이뇨 펩티드를 포함하는 조성물 및 그의 사용 방법
US10052366B2 (en) 2012-05-21 2018-08-21 Alexion Pharmaceuticsl, Inc. Compositions comprising alkaline phosphatase and/or natriuretic peptide and methods of use thereof
KR20150058236A (ko) 2012-08-20 2015-05-28 글리크닉 인코포레이티드 항원 결합 및 다가 fc 감마 수용체 결합 활성을 가진 분자
AU2015209783B2 (en) * 2014-01-24 2020-10-01 Am-Pharma B.V. Chimeric alkaline phosphatase-like proteins
WO2016007873A1 (en) 2014-07-11 2016-01-14 The Regents Of The University Of Michigan Compositions and methods for treating craniosynostosis
RU2708068C2 (ru) 2014-12-05 2019-12-04 Алексион Фармасьютикалз, Инк. Лечение судорог с использованием рекомбинантной щелочной фосфатазы
AU2016211447B2 (en) 2015-01-28 2021-09-23 Alexion Pharmaceuticals, Inc. Methods of treating a subject with an alkaline phosphatase deficiency
MX394116B (es) 2015-07-24 2025-03-19 Gliknik Inc Proteinas de fusion de fragmentos de proteina humana para crear composiciones de fc de inmunoglobulina multimerizada de forma ordenada con union al complemento aumentada.
RU2745528C2 (ru) * 2015-08-17 2021-03-26 Алексион Фармасьютикалз, Инк. Производство щелочных фосфатаз
EP3355904A4 (en) * 2015-09-28 2019-06-12 Alexion Pharmaceuticals, Inc. IDENTIFICATION OF EFFECTIVE DOSE SHEETS FOR TISSUE-SPECIFIC ALKALINE PHOSPHATASE ENZYMERSAT THERAPY OF HYPOPHOSPHATASIA
US11400140B2 (en) 2015-10-30 2022-08-02 Alexion Pharmaceuticals, Inc. Methods for treating craniosynostosis in a patient
WO2017155569A1 (en) * 2016-03-08 2017-09-14 Alexion Pharmaceuticals, Inc. Methods for treating hypophosphatasia in children
WO2017171871A1 (en) * 2016-04-01 2017-10-05 Alexion Pharmaceuticals, Inc. Methods for treating hypophosphatasia in adolescents and adults
US10898549B2 (en) 2016-04-01 2021-01-26 Alexion Pharmaceuticals, Inc. Methods for treating hypophosphatasia in adolescents and adults
EP3436052A4 (en) * 2016-04-01 2019-10-09 Alexion Pharmaceuticals, Inc. TREATMENT OF MUSCLE WEAKNESS WITH ALKALINE PHOSPHATASES
US10988744B2 (en) 2016-06-06 2021-04-27 Alexion Pharmaceuticals, Inc. Method of producing alkaline phosphatase
AU2017279538A1 (en) 2016-06-07 2019-01-03 Gliknik Inc. Cysteine-optimized stradomers
WO2018004517A1 (en) 2016-06-27 2018-01-04 Alexion Pharmaceuticals, Inc. Methods for treating hypophosphatasia in children and adolescents
EP3500289B1 (en) 2016-08-18 2024-10-09 Alexion Pharmaceuticals, Inc. Asfotase alfa for use in treating tracheobronchomalacia
MX2019006189A (es) * 2016-11-30 2019-11-18 Purdue Research Foundation Regeneracion osea dirigida a una fractura mediante estimulacion del receptor de la hormona paratiroidea.
CN110022898B (zh) 2016-12-09 2023-07-04 格利克尼克股份有限公司 用多价Fc化合物治疗炎性疾病的方法
IL317014A (en) 2016-12-09 2025-01-01 Gliknik Inc Production optimization of GL-2045, a multimerization sterol.
EP3592372A4 (en) * 2017-03-09 2021-01-13 Alexion Pharmaceuticals, Inc. GLYCOPROTEIN MANUFACTURING PROCESS
BR112019020506A2 (pt) * 2017-03-31 2020-08-04 Alexion Pharmaceuticals, Inc. métodos para o tratamento de hipofosfatasia (hpp) em adultos e adolescentes
EP3687565A1 (en) 2017-09-27 2020-08-05 Alexion Pharmaceuticals, Inc. Methods of improving cardiovascular function and treating cardiovascular disease using a recombinant ectonucleotide pyrophosphatase phosphodiesterase (npp1)
US11338020B2 (en) 2018-01-09 2022-05-24 Synthetic Biologics, Inc. Alkaline phosphatase agents for treatment of neurodevelopmental disorders
JP7214962B2 (ja) * 2018-01-17 2023-01-31 東ソー株式会社 アルカリホスファターゼ高発現動物細胞
WO2019183208A1 (en) 2018-03-20 2019-09-26 Synthetic Biologics, Inc. Intestinal alkaline phosphatase formulations
US11654184B2 (en) 2018-03-20 2023-05-23 Theriva Biologics, Inc. Alkaline phosphatase agents for treatment of radiation disorders
EP3773684A1 (en) 2018-03-30 2021-02-17 Alexion Pharmaceuticals, Inc. Manufacturing of glycoproteins
CN110499284A (zh) * 2018-05-17 2019-11-26 西安组织工程与再生医学研究所 Wnt信号通路激活剂在制备治疗基因ALPL敲除小鼠牙硬组织矿化异常产品中的应用
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WO2020033867A2 (en) 2018-08-10 2020-02-13 Alexion Pharmaceuticals, Inc. Methods of treating neurofibromatosis type 1 and related conditions with alkaline phosphatase
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KR20220111693A (ko) * 2019-12-09 2022-08-09 알렉시온 파마슈티칼스, 인코포레이티드 알칼리성 포스파타제 폴리펩티드 및 이의 이용 방법
JP2023510195A (ja) 2020-01-03 2023-03-13 ザ ユナイテッド ステイツ オブ アメリカ, アズ リプレゼンテッド バイ ザ セクレタリー, デパートメント オブ ヘルス アンド ヒューマン サービシーズ 歯周の健康を促進するために局所投与されるtnap
AU2021338361A1 (en) * 2020-09-03 2023-04-06 Chen, Irvin S.Y Soluble alkaline phosphatase constructs and expression vectors including a polynucleotide encoding for soluble alkaline phosphatase constructs
KR102571967B1 (ko) * 2021-01-21 2023-08-30 주식회사 마라나노텍코리아 Alp 측정용 바이오 센서
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Also Published As

Publication number Publication date
NO2016002I1 (no) 2016-02-02
EP2368999A1 (en) 2011-09-28
LTPA2016004I1 (lt) 2016-02-25
BR122019000505B1 (pt) 2022-01-18
CA2687001C (en) 2019-02-12
PT2662448T (pt) 2017-03-29
PT2368999E (pt) 2014-05-26
BR122019000505A2 (pt) 2021-12-14
EP2662448A1 (en) 2013-11-13
EP2368999B1 (en) 2014-03-12
BRPI0811198A2 (pt) 2014-10-21
CY2016005I1 (el) 2016-08-31
FR16C0007I1 (OSRAM) 2016-04-15
LTC2368999I2 (lt) 2017-09-25
NL300798I1 (OSRAM) 2016-03-16
SI2368999T1 (sl) 2014-07-31
DE202008018131U1 (de) 2011-12-30
ES2619332T3 (es) 2017-06-26
US20100297119A1 (en) 2010-11-25
HK1162589A1 (en) 2012-08-31
PT2158319E (pt) 2012-03-06
NO2016002I2 (no) 2016-02-02
EP2158319A4 (en) 2010-07-21
BRPI0811198B1 (pt) 2021-03-09
JP2010526543A (ja) 2010-08-05
CA2687001A1 (en) 2008-11-20
SI2662448T1 (sl) 2017-05-31
EP2158319B1 (en) 2011-12-07
ME01828B (me) 2014-12-20
JP5732603B2 (ja) 2015-06-10
IL202057A0 (en) 2011-08-01
DK2158319T3 (da) 2012-03-19
HRP20140416T1 (hr) 2014-06-20
EP2662448B1 (en) 2016-12-21
RS53302B (sr) 2014-08-29
AU2008250945A1 (en) 2008-11-20
PL2158319T3 (pl) 2012-05-31
NL300798I2 (OSRAM) 2016-03-16
AU2008250945B2 (en) 2013-12-12
HUS1600005I1 (hu) 2016-02-29
AU2008250945A2 (en) 2009-12-24
BRPI0811198B8 (pt) 2021-05-25
DK2662448T3 (en) 2017-03-20
FR16C0007I2 (fr) 2017-01-27
PL2368999T3 (pl) 2014-08-29
LU92976I2 (en) 2016-04-11
HK1141047A1 (en) 2010-10-29
CY2016005I2 (el) 2016-08-31
WO2008138131A4 (en) 2008-12-31
PL2662448T3 (pl) 2017-07-31
ES2471915T3 (es) 2014-06-27
PL2158319T4 (pl) 2016-04-29
BRPI0811198A8 (pt) 2018-08-14
HK1191372A1 (en) 2014-07-25
EP2158319A1 (en) 2010-03-03
ES2380546T3 (es) 2012-05-16
ATE536413T1 (de) 2011-12-15
DK2368999T3 (da) 2014-05-26
WO2008138131A1 (en) 2008-11-20
WO2008138131A9 (en) 2009-08-06

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