HK1243643A1 - 用於治疗和/或预防脑淀粉样变性的给药方案 - Google Patents
用於治疗和/或预防脑淀粉样变性的给药方案 Download PDFInfo
- Publication number
- HK1243643A1 HK1243643A1 HK18103256.3A HK18103256A HK1243643A1 HK 1243643 A1 HK1243643 A1 HK 1243643A1 HK 18103256 A HK18103256 A HK 18103256A HK 1243643 A1 HK1243643 A1 HK 1243643A1
- Authority
- HK
- Hong Kong
- Prior art keywords
- addnj
- period
- enzyme
- administration
- formulation
- Prior art date
Links
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
- A61K31/445—Non condensed piperidines, e.g. piperocaine
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/70—Carbohydrates; Sugars; Derivatives thereof
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/0012—Galenical forms characterised by the site of application
- A61K9/0053—Mouth and digestive tract, i.e. intraoral and peroral administration
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P25/00—Drugs for disorders of the nervous system
- A61P25/28—Drugs for disorders of the nervous system for treating neurodegenerative disorders of the central nervous system, e.g. nootropic agents, cognition enhancers, drugs for treating Alzheimer's disease or other forms of dementia
Landscapes
- Health & Medical Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Animal Behavior & Ethology (AREA)
- Pharmacology & Pharmacy (AREA)
- Medicinal Chemistry (AREA)
- General Health & Medical Sciences (AREA)
- Public Health (AREA)
- Veterinary Medicine (AREA)
- Chemical & Material Sciences (AREA)
- Epidemiology (AREA)
- Molecular Biology (AREA)
- Nutrition Science (AREA)
- Physiology (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Neurology (AREA)
- Neurosurgery (AREA)
- Biomedical Technology (AREA)
- Engineering & Computer Science (AREA)
- Hospice & Palliative Care (AREA)
- Psychiatry (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Organic Chemistry (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201461979408P | 2014-04-14 | 2014-04-14 | |
| US61/979,408 | 2014-04-14 | ||
| US14/684,967 US9675627B2 (en) | 2014-04-14 | 2015-04-13 | Dosing regimens for treating and/or preventing cerebral amyloidoses |
| US14/684,967 | 2015-04-13 | ||
| PCT/US2015/025733 WO2015160796A1 (en) | 2014-04-14 | 2015-04-14 | Dosing regimens for treating and/or preventing cerebral amyloidoses |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| HK1243643A1 true HK1243643A1 (zh) | 2018-07-20 |
Family
ID=53015935
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| HK18103256.3A HK1243643A1 (zh) | 2014-04-14 | 2015-04-14 | 用於治疗和/或预防脑淀粉样变性的给药方案 |
Country Status (10)
| Country | Link |
|---|---|
| US (2) | US9675627B2 (enExample) |
| EP (1) | EP3131547A1 (enExample) |
| JP (1) | JP6662789B2 (enExample) |
| KR (1) | KR20170003576A (enExample) |
| CN (1) | CN107148270A (enExample) |
| AU (1) | AU2015247859B2 (enExample) |
| CA (1) | CA2945707A1 (enExample) |
| HK (1) | HK1243643A1 (enExample) |
| SG (1) | SG11201610349SA (enExample) |
| WO (1) | WO2015160796A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| PL2490712T3 (pl) * | 2009-10-19 | 2015-12-31 | Amicus Therapeutics Inc | Sposób leczenia choroby Alzheimera przy zastosowaniu chaperonów farmakologicznych dla zwiększenia aktywności gangliozydaz |
| US9994589B2 (en) | 2015-12-14 | 2018-06-12 | Amicus Therapeutics, Inc. | Compounds and methods for the treatment of alzheimer's disease and/or cerebral amyloid angiopathy |
| US20220184185A1 (en) | 2018-07-25 | 2022-06-16 | Modernatx, Inc. | Mrna based enzyme replacement therapy combined with a pharmacological chaperone for the treatment of lysosomal storage disorders |
Family Cites Families (22)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4407957A (en) | 1981-03-13 | 1983-10-04 | Damon Corporation | Reversible microencapsulation of a core material |
| DK0585368T3 (da) | 1991-04-25 | 1998-03-16 | Univ Brown Res Found | Implanterbart biokompatibelt immunisolatorisk vehikel til afgivelse af udvalgte terapeutiske produkter |
| US5766846A (en) | 1992-07-10 | 1998-06-16 | Athena Neurosciences | Methods of screening for compounds which inhibit soluble β-amyloid peptide production |
| US5383851A (en) | 1992-07-24 | 1995-01-24 | Bioject Inc. | Needleless hypodermic injection device |
| US5569189A (en) | 1992-09-28 | 1996-10-29 | Equidyne Systems, Inc. | hypodermic jet injector |
| KR100291620B1 (ko) | 1992-09-29 | 2001-10-24 | 추후제출 | 부갑상선호르몬의활성단편의폐를통한전달방법 |
| FR2718357B1 (fr) | 1994-04-06 | 1997-10-03 | Defarges Alain Moreau | Perfectionnements apportés à un dispositif d'injection par jet sans aiguille. |
| US5599302A (en) | 1995-01-09 | 1997-02-04 | Medi-Ject Corporation | Medical injection system and method, gas spring thereof and launching device using gas spring |
| US5780014A (en) | 1995-04-14 | 1998-07-14 | Inhale Therapeutic Systems | Method and apparatus for pulmonary administration of dry powder alpha 1-antitrypsin |
| US5654007A (en) | 1995-06-07 | 1997-08-05 | Inhale Therapeutic Systems | Methods and system for processing dispersible fine powders |
| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| US20050031651A1 (en) | 2002-12-24 | 2005-02-10 | Francine Gervais | Therapeutic formulations for the treatment of beta-amyloid related diseases |
| CA2526173A1 (en) | 2003-05-22 | 2004-12-02 | The Hospital For Sick Children | Treatment of tay sachs or sandhoff diseases by enhancing hexosaminidase activity |
| CN104771402A (zh) | 2005-06-08 | 2015-07-15 | 阿米库斯治疗学公司 | 溶酶体酶编码基因突变相关的cns紊乱的治疗 |
| WO2007137072A2 (en) * | 2006-05-16 | 2007-11-29 | Amicus Therapeutics, Inc. | Assays for diagnosing and evaluating treatment options for fabry disease |
| EP2040548B1 (en) | 2006-06-23 | 2012-05-02 | Amicus Therapeutics, Inc. | Method for the treatment of neurological disorders by enhancing the activity of beta -glucocerebrosidase |
| WO2008134628A2 (en) | 2007-04-26 | 2008-11-06 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| WO2011011181A1 (en) | 2009-07-01 | 2011-01-27 | Amicus Therapeutics, Inc. | Pharmacological chaperones for the treatment of alzheimer's disease |
| PL2490712T3 (pl) * | 2009-10-19 | 2015-12-31 | Amicus Therapeutics Inc | Sposób leczenia choroby Alzheimera przy zastosowaniu chaperonów farmakologicznych dla zwiększenia aktywności gangliozydaz |
| CN107088225A (zh) * | 2011-03-11 | 2017-08-25 | 阿米库斯治疗学公司 | 治疗法布里病的给药方案 |
| EP2793872B1 (en) * | 2011-12-22 | 2021-03-10 | Centogene IP GmbH | Combination of a compound having the ability to rearrange a lysosomal enzyme and ambroxol and/or a derivative of ambroxol |
| ES2859761T3 (es) * | 2012-05-03 | 2021-10-04 | Amicus Therapeutics Inc | Pautas posológicas para el tratamiento de enfermedad de Pompe |
-
2015
- 2015-04-13 US US14/684,967 patent/US9675627B2/en active Active
- 2015-04-14 CN CN201580031471.1A patent/CN107148270A/zh active Pending
- 2015-04-14 JP JP2016562965A patent/JP6662789B2/ja not_active Expired - Fee Related
- 2015-04-14 HK HK18103256.3A patent/HK1243643A1/zh unknown
- 2015-04-14 KR KR1020167031756A patent/KR20170003576A/ko not_active Withdrawn
- 2015-04-14 WO PCT/US2015/025733 patent/WO2015160796A1/en not_active Ceased
- 2015-04-14 EP EP15719362.4A patent/EP3131547A1/en not_active Withdrawn
- 2015-04-14 CA CA2945707A patent/CA2945707A1/en not_active Abandoned
- 2015-04-14 AU AU2015247859A patent/AU2015247859B2/en not_active Ceased
- 2015-04-14 SG SG11201610349SA patent/SG11201610349SA/en unknown
-
2017
- 2017-06-12 US US15/619,785 patent/US20170273996A1/en not_active Abandoned
Also Published As
| Publication number | Publication date |
|---|---|
| SG11201610349SA (en) | 2017-01-27 |
| CN107148270A (zh) | 2017-09-08 |
| US20170273996A1 (en) | 2017-09-28 |
| AU2015247859B2 (en) | 2020-03-26 |
| KR20170003576A (ko) | 2017-01-09 |
| US9675627B2 (en) | 2017-06-13 |
| JP6662789B2 (ja) | 2020-03-11 |
| AU2015247859A1 (en) | 2016-12-01 |
| WO2015160796A1 (en) | 2015-10-22 |
| JP2017511372A (ja) | 2017-04-20 |
| CA2945707A1 (en) | 2015-10-22 |
| EP3131547A1 (en) | 2017-02-22 |
| US20160008383A1 (en) | 2016-01-14 |
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