JP6662789B2 - 脳アミロイドーシスを処置及び／又は予防する投与計画 - Google Patents
脳アミロイドーシスを処置及び／又は予防する投与計画 Download PDFInfo
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- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
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- A—HUMAN NECESSITIES
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- A—HUMAN NECESSITIES
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P25/00—Drugs for disorders of the nervous system
- A61P25/28—Drugs for disorders of the nervous system for treating neurodegenerative disorders of the central nervous system, e.g. nootropic agents, cognition enhancers, drugs for treating Alzheimer's disease or other forms of dementia
Landscapes
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- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Organic Chemistry (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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| US14/684,967 | 2015-04-13 | ||
| PCT/US2015/025733 WO2015160796A1 (en) | 2014-04-14 | 2015-04-14 | Dosing regimens for treating and/or preventing cerebral amyloidoses |
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| JP2017511372A5 JP2017511372A5 (enExample) | 2019-05-09 |
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| PL2490712T3 (pl) * | 2009-10-19 | 2015-12-31 | Amicus Therapeutics Inc | Sposób leczenia choroby Alzheimera przy zastosowaniu chaperonów farmakologicznych dla zwiększenia aktywności gangliozydaz |
| US9994589B2 (en) | 2015-12-14 | 2018-06-12 | Amicus Therapeutics, Inc. | Compounds and methods for the treatment of alzheimer's disease and/or cerebral amyloid angiopathy |
| US20220184185A1 (en) | 2018-07-25 | 2022-06-16 | Modernatx, Inc. | Mrna based enzyme replacement therapy combined with a pharmacological chaperone for the treatment of lysosomal storage disorders |
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| US4407957A (en) | 1981-03-13 | 1983-10-04 | Damon Corporation | Reversible microencapsulation of a core material |
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| US5766846A (en) | 1992-07-10 | 1998-06-16 | Athena Neurosciences | Methods of screening for compounds which inhibit soluble β-amyloid peptide production |
| US5383851A (en) | 1992-07-24 | 1995-01-24 | Bioject Inc. | Needleless hypodermic injection device |
| US5569189A (en) | 1992-09-28 | 1996-10-29 | Equidyne Systems, Inc. | hypodermic jet injector |
| KR100291620B1 (ko) | 1992-09-29 | 2001-10-24 | 추후제출 | 부갑상선호르몬의활성단편의폐를통한전달방법 |
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| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| US20050031651A1 (en) | 2002-12-24 | 2005-02-10 | Francine Gervais | Therapeutic formulations for the treatment of beta-amyloid related diseases |
| CA2526173A1 (en) | 2003-05-22 | 2004-12-02 | The Hospital For Sick Children | Treatment of tay sachs or sandhoff diseases by enhancing hexosaminidase activity |
| CN104771402A (zh) | 2005-06-08 | 2015-07-15 | 阿米库斯治疗学公司 | 溶酶体酶编码基因突变相关的cns紊乱的治疗 |
| WO2007137072A2 (en) * | 2006-05-16 | 2007-11-29 | Amicus Therapeutics, Inc. | Assays for diagnosing and evaluating treatment options for fabry disease |
| EP2040548B1 (en) | 2006-06-23 | 2012-05-02 | Amicus Therapeutics, Inc. | Method for the treatment of neurological disorders by enhancing the activity of beta -glucocerebrosidase |
| WO2008134628A2 (en) | 2007-04-26 | 2008-11-06 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| WO2011011181A1 (en) | 2009-07-01 | 2011-01-27 | Amicus Therapeutics, Inc. | Pharmacological chaperones for the treatment of alzheimer's disease |
| PL2490712T3 (pl) * | 2009-10-19 | 2015-12-31 | Amicus Therapeutics Inc | Sposób leczenia choroby Alzheimera przy zastosowaniu chaperonów farmakologicznych dla zwiększenia aktywności gangliozydaz |
| CN107088225A (zh) * | 2011-03-11 | 2017-08-25 | 阿米库斯治疗学公司 | 治疗法布里病的给药方案 |
| EP2793872B1 (en) * | 2011-12-22 | 2021-03-10 | Centogene IP GmbH | Combination of a compound having the ability to rearrange a lysosomal enzyme and ambroxol and/or a derivative of ambroxol |
| ES2859761T3 (es) * | 2012-05-03 | 2021-10-04 | Amicus Therapeutics Inc | Pautas posológicas para el tratamiento de enfermedad de Pompe |
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- 2015-04-14 HK HK18103256.3A patent/HK1243643A1/zh unknown
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- 2015-04-14 WO PCT/US2015/025733 patent/WO2015160796A1/en not_active Ceased
- 2015-04-14 EP EP15719362.4A patent/EP3131547A1/en not_active Withdrawn
- 2015-04-14 CA CA2945707A patent/CA2945707A1/en not_active Abandoned
- 2015-04-14 AU AU2015247859A patent/AU2015247859B2/en not_active Ceased
- 2015-04-14 SG SG11201610349SA patent/SG11201610349SA/en unknown
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2017
- 2017-06-12 US US15/619,785 patent/US20170273996A1/en not_active Abandoned
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|---|---|
| SG11201610349SA (en) | 2017-01-27 |
| CN107148270A (zh) | 2017-09-08 |
| US20170273996A1 (en) | 2017-09-28 |
| AU2015247859B2 (en) | 2020-03-26 |
| KR20170003576A (ko) | 2017-01-09 |
| US9675627B2 (en) | 2017-06-13 |
| AU2015247859A1 (en) | 2016-12-01 |
| WO2015160796A1 (en) | 2015-10-22 |
| HK1243643A1 (zh) | 2018-07-20 |
| JP2017511372A (ja) | 2017-04-20 |
| CA2945707A1 (en) | 2015-10-22 |
| EP3131547A1 (en) | 2017-02-22 |
| US20160008383A1 (en) | 2016-01-14 |
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