CN119156448A - 用于治疗SNCA相关疾病的SNCA-靶向siRNA组合物 - Google Patents

用于治疗SNCA相关疾病的SNCA-靶向siRNA组合物 Download PDF

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Publication number
CN119156448A
CN119156448A CN202380038419.3A CN202380038419A CN119156448A CN 119156448 A CN119156448 A CN 119156448A CN 202380038419 A CN202380038419 A CN 202380038419A CN 119156448 A CN119156448 A CN 119156448A
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phosphate
nucleotide
seq
snca
nucleotides
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CN202380038419.3A
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Chinese (zh)
Inventor
L·T·黄·党
M·K·施莱格尔
J·巴里
T·阮
A·卡斯托雷诺
K·苏
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Alnylam Pharmaceuticals Inc
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Alnylam Pharmaceuticals Inc
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CN202380038419.3A 2022-04-01 2023-03-31 用于治疗SNCA相关疾病的SNCA-靶向siRNA组合物 Pending CN119156448A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263326770P 2022-04-01 2022-04-01
US63/326,770 2022-04-01
US202263326813P 2022-04-02 2022-04-02
US63/326,813 2022-04-02
PCT/US2023/065196 WO2023192977A2 (en) 2022-04-01 2023-03-31 Snca-targeting sirna compositions for treating snca-associated disease

Publications (1)

Publication Number Publication Date
CN119156448A true CN119156448A (zh) 2024-12-17

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ID=88203639

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CN202380038419.3A Pending CN119156448A (zh) 2022-04-01 2023-03-31 用于治疗SNCA相关疾病的SNCA-靶向siRNA组合物

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US (2) US20250059541A1 (https=)
EP (1) EP4504938A2 (https=)
JP (1) JP2025513757A (https=)
KR (1) KR20240166577A (https=)
CN (1) CN119156448A (https=)
AU (1) AU2023241905A1 (https=)
CA (1) CA3254960A1 (https=)
CL (1) CL2024002960A1 (https=)
CO (1) CO2024012499A2 (https=)
IL (1) IL315594A (https=)
MX (1) MX2024011539A (https=)
TW (1) TW202407100A (https=)
WO (1) WO2023192977A2 (https=)

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CO2024012499A2 (es) 2024-10-10
CA3254960A1 (en) 2023-10-05
WO2023192977A2 (en) 2023-10-05
MX2024011539A (es) 2024-09-26
CL2024002960A1 (es) 2025-03-07
AU2023241905A1 (en) 2024-09-26
IL315594A (en) 2024-11-01
JP2025513757A (ja) 2025-04-30
EP4504938A2 (en) 2025-02-12
KR20240166577A (ko) 2024-11-26
TW202407100A (zh) 2024-02-16
US20250059541A1 (en) 2025-02-20
US20250115911A1 (en) 2025-04-10

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