CN114616002A - 使用由脂质纳米颗粒递送的crispr/cas系统在动物中进行的转录调控 - Google Patents

使用由脂质纳米颗粒递送的crispr/cas系统在动物中进行的转录调控 Download PDF

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CN114616002A
CN114616002A CN202080075542.9A CN202080075542A CN114616002A CN 114616002 A CN114616002 A CN 114616002A CN 202080075542 A CN202080075542 A CN 202080075542A CN 114616002 A CN114616002 A CN 114616002A
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protein
sequence
lipid nanoparticle
chimeric
seq
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查琳·亨特
苏珊娜·哈特福德
国春·龚
布莱恩·扎姆布罗维兹
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Regeneron Pharmaceuticals Inc
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Regeneron Pharmaceuticals Inc
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CN202080075542.9A 2019-09-13 2020-09-11 使用由脂质纳米颗粒递送的crispr/cas系统在动物中进行的转录调控 Pending CN114616002A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962900080P 2019-09-13 2019-09-13
US62/900,080 2019-09-13
US202063042762P 2020-06-23 2020-06-23
US63/042,762 2020-06-23
PCT/US2020/050491 WO2021050940A1 (en) 2019-09-13 2020-09-11 Transcription modulation in animals using crispr/cas systems delivered by lipid nanoparticles

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US (1) US20210079394A1 (https=)
EP (1) EP4028063A1 (https=)
JP (1) JP2022548031A (https=)
KR (1) KR20220062079A (https=)
CN (1) CN114616002A (https=)
AU (1) AU2020346056A1 (https=)
CA (1) CA3153980A1 (https=)
WO (1) WO2021050940A1 (https=)

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US20210079394A1 (en) 2021-03-18
KR20220062079A (ko) 2022-05-13
EP4028063A1 (en) 2022-07-20
JP2022548031A (ja) 2022-11-16

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