JP2022548031A - 脂質ナノ粒子によって送達されるｃｒｉｓｐｒ／ｃａｓシステムを使用する動物における転写調節 - Google Patents

脂質ナノ粒子によって送達されるｃｒｉｓｐｒ／ｃａｓシステムを使用する動物における転写調節 Download PDF

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JP2022548031A
JP2022548031A JP2022516060A JP2022516060A JP2022548031A JP 2022548031 A JP2022548031 A JP 2022548031A JP 2022516060 A JP2022516060 A JP 2022516060A JP 2022516060 A JP2022516060 A JP 2022516060A JP 2022548031 A JP2022548031 A JP 2022548031A
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protein
sequence
chimeric
guide rnas
seq
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JP2022548031A5 (https=
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チャーリーン ハント，
スザンヌ ハートフォード，
グオチュン ゴン，
ブライアン ザンブロウィッツ，
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Regeneron Pharmaceuticals Inc
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JP2022516060A 2019-09-13 2020-09-11 脂質ナノ粒子によって送達されるｃｒｉｓｐｒ／ｃａｓシステムを使用する動物における転写調節 Pending JP2022548031A (ja)

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US201962900080P 2019-09-13 2019-09-13
US62/900,080 2019-09-13
US202063042762P 2020-06-23 2020-06-23
US63/042,762 2020-06-23
PCT/US2020/050491 WO2021050940A1 (en) 2019-09-13 2020-09-11 Transcription modulation in animals using crispr/cas systems delivered by lipid nanoparticles

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