CN110382695A - 通过crispr/cpf1介导的基因编辑来预防肌营养不良 - Google Patents

通过crispr/cpf1介导的基因编辑来预防肌营养不良 Download PDF

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CN110382695A
CN110382695A CN201780084906.8A CN201780084906A CN110382695A CN 110382695 A CN110382695 A CN 110382695A CN 201780084906 A CN201780084906 A CN 201780084906A CN 110382695 A CN110382695 A CN 110382695A
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composition
promoter
sequence
vector
dystrophin
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张宇
龙城祖
罗达·巴塞尔-达比
埃里克·奥尔松
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University of Texas System
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CN201780084906.8A 2016-11-28 2017-11-28 通过crispr/cpf1介导的基因编辑来预防肌营养不良 Pending CN110382695A (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662426853P 2016-11-28 2016-11-28
US62/426,853 2016-11-28
PCT/US2017/063468 WO2018098480A1 (en) 2016-11-28 2017-11-28 Prevention of muscular dystrophy by crispr/cpf1-mediated gene editing

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CN110382695A true CN110382695A (zh) 2019-10-25

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US (1) US20200046854A1 (https=)
EP (1) EP3545090A1 (https=)
JP (1) JP2019536782A (https=)
CN (1) CN110382695A (https=)
AU (1) AU2017364106A1 (https=)
CA (1) CA3044531A1 (https=)
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WO (1) WO2018098480A1 (https=)

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CN114214360A (zh) * 2021-12-27 2022-03-22 西安英创生物技术有限公司 先天性肌无力小鼠模型、其构建方法及应用
CN115279184A (zh) * 2020-03-04 2022-11-01 雷杰纳荣制药公司 B4galt1介导的功能的啮齿动物模型
CN118086408A (zh) * 2024-04-25 2024-05-28 华南理工大学 一种可实现靶向肌肉细胞基因编辑的仿病毒颗粒及其制备方法和应用
WO2025190277A1 (zh) * 2024-03-15 2025-09-18 迦进生物医药(上海)有限公司 治疗杜兴型肌营养不良症和贝克型肌营养不良症的药物

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