CN105934515B - 用于治疗糖原贮积病的腺相关病毒载体 - Google Patents

用于治疗糖原贮积病的腺相关病毒载体 Download PDF

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CN105934515B
CN105934515B CN201480074046.6A CN201480074046A CN105934515B CN 105934515 B CN105934515 B CN 105934515B CN 201480074046 A CN201480074046 A CN 201480074046A CN 105934515 B CN105934515 B CN 105934515B
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raav
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CN105934515A (zh
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J·J·周
B·J·伯恩
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University of Florida Research Foundation Inc
United States Department of Health and Human Services
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    • C12N2830/42—Vector systems having a special element relevant for transcription being an intron or intervening sequence for splicing and/or stability of RNA

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CN201480074046.6A 2013-11-26 2014-11-25 用于治疗糖原贮积病的腺相关病毒载体 Active CN105934515B (zh)

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US201361908861P 2013-11-26 2013-11-26
US61/908,861 2013-11-26
PCT/US2014/067415 WO2015081101A1 (en) 2013-11-26 2014-11-25 Adeno-associated virus vectors for treatment of glycogen storage disease

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US (3) US9644216B2 (enExample)
EP (2) EP3415620B1 (enExample)
JP (1) JP6649265B2 (enExample)
CN (1) CN105934515B (enExample)
AU (1) AU2014354839B2 (enExample)
CA (1) CA2930872C (enExample)
ES (1) ES2690643T3 (enExample)
IL (1) IL245659B (enExample)
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CN114717264A (zh) 2014-11-14 2022-07-08 沃雅戈治疗公司 治疗肌萎缩性侧索硬化(als)的组合物和方法
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WO2019172286A1 (ja) 2018-03-09 2019-09-12 第一三共株式会社 糖原病Ｉａ型治療薬
CN112424359A (zh) 2018-05-15 2021-02-26 沃雅戈治疗公司 用于治疗帕金森氏病的组合物和方法
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JP2022500436A (ja) * 2018-09-13 2022-01-04 モダーナティエックス・インコーポレイテッドModernaTX, Inc. 糖原病を処置するためのグルコース−６−ホスファターゼをコードするポリヌクレオチド
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JP2016538885A (ja) 2016-12-15
CN105934515A (zh) 2016-09-07
BR112016011997A2 (pt) 2017-09-26
US20190017069A1 (en) 2019-01-17
JP6649265B2 (ja) 2020-02-19
US10113183B2 (en) 2018-10-30
WO2015081101A1 (en) 2015-06-04
EP3074510B1 (en) 2018-08-01
AU2014354839A1 (en) 2016-06-09
AU2014354839B2 (en) 2020-06-04
MX2016006774A (es) 2016-10-13
CA2930872C (en) 2022-05-31
EP3074510A1 (en) 2016-10-05
US11060110B2 (en) 2021-07-13
MX375360B (es) 2025-03-06
IL245659A0 (en) 2016-06-30
US20160376608A1 (en) 2016-12-29
WO2015081101A8 (en) 2016-06-16
US20170233763A1 (en) 2017-08-17
CA2930872A1 (en) 2015-06-04
IL245659B (en) 2020-01-30
EP3415620B1 (en) 2021-03-31
EP3415620A1 (en) 2018-12-19
ES2690643T3 (es) 2018-11-21

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