CA3222824A1 - Antisense compounds and methods for targeting cug repeats - Google Patents
Antisense compounds and methods for targeting cug repeats Download PDFInfo
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- CA3222824A1 CA3222824A1 CA3222824A CA3222824A CA3222824A1 CA 3222824 A1 CA3222824 A1 CA 3222824A1 CA 3222824 A CA3222824 A CA 3222824A CA 3222824 A CA3222824 A CA 3222824A CA 3222824 A1 CA3222824 A1 CA 3222824A1
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- C—CHEMISTRY; METALLURGY
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- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
- C12N15/09—Recombinant DNA-technology
- C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
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US11512312B2 (en) | 2017-03-10 | 2022-11-29 | The Board Of Regents Of The University Of Texas System | Treatment of Fuchs' endothelial corneal dystrophy |
WO2019165183A1 (en) * | 2018-02-22 | 2019-08-29 | Entrada Therapeutics, Inc. | Compositions and methods for treating mitochondrial neurogastrointestinal encephalopathy |
GB201812972D0 (en) * | 2018-08-09 | 2018-09-26 | Univ Oxford Innovation Ltd | Cell-penetrating peptides |
EP4058032A4 (de) * | 2019-12-19 | 2024-01-10 | Entrada Therapeutics, Inc. | Zusammensetzungen zur verabreichung von antisense-verbindungen |
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2022
- 2022-06-22 WO PCT/US2022/034517 patent/WO2022271818A1/en active Application Filing
- 2022-06-22 IL IL309001A patent/IL309001A/en unknown
- 2022-06-22 CA CA3222824A patent/CA3222824A1/en active Pending
- 2022-06-22 KR KR1020247002577A patent/KR20240038967A/ko unknown
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- 2022-06-22 AU AU2022298774A patent/AU2022298774A1/en active Pending
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WO2022271818A1 (en) | 2022-12-29 |
IL309001A (en) | 2024-02-01 |
CO2023018002A2 (es) | 2024-02-05 |
KR20240038967A (ko) | 2024-03-26 |
AU2022298774A1 (en) | 2023-12-14 |
DOP2023000279A (es) | 2024-04-30 |
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