CA3119814A1 - Anellosomes for delivering protein replacement therapeutic modalities - Google Patents
Anellosomes for delivering protein replacement therapeutic modalities Download PDFInfo
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- CA3119814A1 CA3119814A1 CA3119814A CA3119814A CA3119814A1 CA 3119814 A1 CA3119814 A1 CA 3119814A1 CA 3119814 A CA3119814 A CA 3119814A CA 3119814 A CA3119814 A CA 3119814A CA 3119814 A1 CA3119814 A1 CA 3119814A1
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- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
- C12N15/09—Recombinant DNA-technology
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- C12N15/90—Stable introduction of foreign DNA into chromosome
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- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
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- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
- C12N15/09—Recombinant DNA-technology
- C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
- C12N15/79—Vectors or expression systems specially adapted for eukaryotic hosts
- C12N15/85—Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
- C12N15/86—Viral vectors
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
- C12N2750/00011—Details
- C12N2750/00022—New viral proteins or individual genes, new structural or functional aspects of known viral proteins or genes
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
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| MX2020003074A (es) | 2017-09-25 | 2020-09-14 | Agrospheres Inc | Composiciones y metodos para la produccion y la administracion expansible de productos biologicos. |
| MX2021006977A (es) * | 2018-12-12 | 2021-10-13 | Flagship Pioneering Innovations V Inc | Anellosomas y metodos de uso. |
| WO2021252955A1 (en) * | 2020-06-12 | 2021-12-16 | Flagship Pioneering Innovations V, Inc. | Tandem anellovirus constructs |
| MX2022016475A (es) * | 2020-06-17 | 2023-04-11 | Flagship Pioneering Innovations V Inc | Metodos de identificacion y caracterizacion de anellovirus y usos de los mismos. |
| CA3206361A1 (en) * | 2020-12-23 | 2022-06-30 | Flagship Pioneering Innovations V, Inc. | In vitro assembly of anellovirus capsids enclosing rna |
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| US20250027107A1 (en) * | 2021-10-18 | 2025-01-23 | Flagship Pioneering Innovations Vii, Llc | Dna compositions and related methods |
| WO2025080985A1 (en) | 2023-10-13 | 2025-04-17 | Flagship Pioneering Innovations V, Inc. | Tissue specific anellovector delivery |
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| NL9002008A (nl) * | 1990-09-12 | 1992-04-01 | Stichting Centr Diergeneeskund | Recombinant dna en rna en daarvan afgeleide produkten. |
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| US9676828B2 (en) * | 2010-06-23 | 2017-06-13 | Deutsches Krebsforschungszentrum | Rearranged TT virus molecules for use in diagnosis, prevention and treatment of cancer and autoimmunity |
| KR20200038236A (ko) * | 2017-06-13 | 2020-04-10 | 플래그쉽 파이어니어링 이노베이션스 브이, 인크. | 큐론을 포함하는 조성물 및 그의 용도 |
| CA3119339A1 (en) * | 2018-12-12 | 2020-06-18 | Flagship Pioneering Innovations V, Inc. | Anellosomes for delivering intracellular therapeutic modalities |
| MX2021006977A (es) * | 2018-12-12 | 2021-10-13 | Flagship Pioneering Innovations V Inc | Anellosomas y metodos de uso. |
| BR112021009379A2 (pt) * | 2018-12-12 | 2021-08-17 | Flagship Pioneering Innovations V, Inc | anelossomos para entrega de modalidades terapêuticas secretadas |
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| EP3894569A2 (en) | 2021-10-20 |
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| MX2021006945A (es) | 2021-08-24 |
| AU2019395418A1 (en) | 2021-06-03 |
| IL283781A (en) | 2021-07-29 |
| JP2022513459A (ja) | 2022-02-08 |
| KR20210125990A (ko) | 2021-10-19 |
| WO2020123795A2 (en) | 2020-06-18 |
| JP2024099833A (ja) | 2024-07-25 |
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