AU2020236735A1 - Gene therapy compositions and methods for treating parkinson's disease - Google Patents
Gene therapy compositions and methods for treating parkinson's disease Download PDFInfo
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- A61P25/14—Drugs for disorders of the nervous system for treating abnormal movements, e.g. chorea, dyskinesia
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- C12N2810/6072—Vectors comprising as targeting moiety peptide derived from defined protein from viruses negative strand RNA viruses
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| US5512421A (en) | 1991-02-19 | 1996-04-30 | The Regents Of The University Of California | Generation, concentration and efficient transfer of VSV-G pseudotyped retroviral vectors |
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| US5866552A (en) | 1996-09-06 | 1999-02-02 | The Trustees Of The University Of Pennsylvania | Method for expressing a gene in the absence of an immune response |
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| SE0302509D0 (sv) | 2003-09-19 | 2003-09-19 | Amersham Biosciences Ab | Matrix for separation of polyethers and method of separation |
| US7943374B2 (en) | 2005-08-21 | 2011-05-17 | Markus Hildinger | Super-size adeno-associated viral vector harboring a recombinant genome larger than 5.7 kb |
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| US20090214478A1 (en) | 2008-02-21 | 2009-08-27 | Alberto Auricchio | Method of treating ocular diseases by gene therapy |
| DK2307551T3 (en) | 2008-06-18 | 2017-03-20 | Oxford Biomedica (Uk) Ltd | CLEANING RETROVIRAL VECTORS |
| WO2011148194A1 (en) * | 2010-05-28 | 2011-12-01 | Oxford Biomedica (Uk) Ltd | Delivery of lentiviral vectors to the brain |
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| CN116024271A (zh) * | 2018-05-31 | 2023-04-28 | 康霖生物科技(杭州)有限公司 | 一种用于中枢神经系统疾病治疗的基因序列构建体 |
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