AU2017322483A1 - Methods and compositions for treatment of lafora disease - Google Patents
Methods and compositions for treatment of lafora disease Download PDFInfo
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- AU2017322483A1 AU2017322483A1 AU2017322483A AU2017322483A AU2017322483A1 AU 2017322483 A1 AU2017322483 A1 AU 2017322483A1 AU 2017322483 A AU2017322483 A AU 2017322483A AU 2017322483 A AU2017322483 A AU 2017322483A AU 2017322483 A1 AU2017322483 A1 AU 2017322483A1
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- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07K—PEPTIDES
- C07K2317/00—Immunoglobulins specific features
- C07K2317/70—Immunoglobulins specific features characterized by effect upon binding to a cell or to an antigen
- C07K2317/77—Internalization into the cell
-
- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07K—PEPTIDES
- C07K2319/00—Fusion polypeptide
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- Health & Medical Sciences (AREA)
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- Engineering & Computer Science (AREA)
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- Genetics & Genomics (AREA)
- Biochemistry (AREA)
- Molecular Biology (AREA)
- Immunology (AREA)
- Zoology (AREA)
- Wood Science & Technology (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
- Biomedical Technology (AREA)
- Biophysics (AREA)
- Pharmacology & Pharmacy (AREA)
- Veterinary Medicine (AREA)
- Animal Behavior & Ethology (AREA)
- Public Health (AREA)
- General Engineering & Computer Science (AREA)
- Biotechnology (AREA)
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- Chemical Kinetics & Catalysis (AREA)
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- Hospice & Palliative Care (AREA)
- Obesity (AREA)
- Hematology (AREA)
- Diabetes (AREA)
- Epidemiology (AREA)
- Psychiatry (AREA)
- Peptides Or Proteins (AREA)
- Enzymes And Modification Thereof (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Medicinal Preparation (AREA)
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201662385656P | 2016-09-09 | 2016-09-09 | |
| US62/385,656 | 2016-09-09 | ||
| US201762553048P | 2017-08-31 | 2017-08-31 | |
| US62/553,048 | 2017-08-31 | ||
| PCT/US2017/050787 WO2018049237A1 (en) | 2016-09-09 | 2017-09-08 | Methods and compositions for treatment of lafora disease |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| AU2017322483A1 true AU2017322483A1 (en) | 2019-04-04 |
Family
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Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| AU2017322483A Abandoned AU2017322483A1 (en) | 2016-09-09 | 2017-09-08 | Methods and compositions for treatment of lafora disease |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US10781433B2 (enExample) |
| EP (1) | EP3509614A4 (enExample) |
| JP (1) | JP2019535645A (enExample) |
| CN (1) | CN109963576A (enExample) |
| AU (1) | AU2017322483A1 (enExample) |
| CA (1) | CA3036524A1 (enExample) |
| WO (1) | WO2018049237A1 (enExample) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
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| JP6178785B2 (ja) | 2011-04-01 | 2017-08-09 | イェール ユニバーシティーＹａｌｅ Ｕｎｉｖｅｒｓｉｔｙ | 細胞浸透性抗ｄｎａ抗体およびｄｎａ修復を阻害するためのその使用 |
| WO2017218824A1 (en) | 2016-06-15 | 2017-12-21 | Yale University | Anti-guanosine antibody as a molecular delivery vehicle |
| US11590242B2 (en) | 2016-06-15 | 2023-02-28 | Yale University | Antibody-mediated autocatalytic, targeted delivery of nanocarriers to tumors |
| KR20220049568A (ko) * | 2019-08-22 | 2022-04-21 | 더 리전츠 오브 더 유니버시티 오브 캘리포니아 | 엔젤만 증후군의 치료를 위한 ube3a |
| KR102814185B1 (ko) | 2023-07-20 | 2025-06-12 | 제닉스큐어 주식회사 | 라포라병을 예방 또는 치료하기 위한 재조합 아데노 연관 바이러스 및 이를 포함하는 약학적 조성물 |
| WO2025018822A1 (ko) | 2023-07-20 | 2025-01-23 | 제닉스큐어 주식회사 | 라포라병을 예방 또는 치료하기 위한 재조합 아데노 연관 바이러스 및 이를 포함하는 약학적 조성물 |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| BRPI1011236A2 (pt) * | 2009-06-15 | 2019-07-09 | 4S3 Bioscience Inc | métodos e composições para tratamento de miopatia miotubular usando polipeptídeos quiméricos compreendendo polipeptídeos miotubularesih 1 (mtm1) |
| US20130273026A1 (en) | 2012-04-12 | 2013-10-17 | Integrative Enzymatics, Inc. | Composition and method for modulating inflammatory molecules with amylase |
| CN105189543A (zh) * | 2013-02-20 | 2015-12-23 | 瓦莱里昂治疗有限责任公司 | 治疗福布斯科里病的方法和组合物 |
| CA2901978A1 (en) * | 2013-02-20 | 2014-08-28 | Valerion Therapeutics, Llc | Methods and compositions for treatment of pompe disease |
| EP3711820A1 (en) * | 2014-01-13 | 2020-09-23 | Valerion Therapeutics, LLC | Internalizing moieties |
| CA2989294A1 (en) * | 2014-06-13 | 2015-12-17 | Valerion Therapeutics, Llc | Methods and compositions for treatment of glycogen storage diseases and glycogen metabolism disorders |
| CA2995673A1 (en) * | 2014-08-27 | 2016-03-03 | Valerion Therapeutics, Llc | Internalizing moieties for treatment of cancer |
-
2017
- 2017-09-08 CA CA3036524A patent/CA3036524A1/en not_active Abandoned
- 2017-09-08 US US16/332,331 patent/US10781433B2/en active Active
- 2017-09-08 JP JP2019513898A patent/JP2019535645A/ja active Pending
- 2017-09-08 CN CN201780069052.6A patent/CN109963576A/zh active Pending
- 2017-09-08 EP EP17849664.2A patent/EP3509614A4/en not_active Withdrawn
- 2017-09-08 WO PCT/US2017/050787 patent/WO2018049237A1/en not_active Ceased
- 2017-09-08 AU AU2017322483A patent/AU2017322483A1/en not_active Abandoned
Also Published As
| Publication number | Publication date |
|---|---|
| CA3036524A1 (en) | 2018-03-15 |
| JP2019535645A (ja) | 2019-12-12 |
| WO2018049237A1 (en) | 2018-03-15 |
| EP3509614A4 (en) | 2020-04-22 |
| CN109963576A (zh) | 2019-07-02 |
| US20190316104A1 (en) | 2019-10-17 |
| EP3509614A1 (en) | 2019-07-17 |
| US10781433B2 (en) | 2020-09-22 |
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