AU2013234042B2 - Methods and materials for treatment of Pompe's disease - Google Patents

Methods and materials for treatment of Pompe's disease Download PDF

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Publication number
AU2013234042B2
AU2013234042B2 AU2013234042A AU2013234042A AU2013234042B2 AU 2013234042 B2 AU2013234042 B2 AU 2013234042B2 AU 2013234042 A AU2013234042 A AU 2013234042A AU 2013234042 A AU2013234042 A AU 2013234042A AU 2013234042 B2 AU2013234042 B2 AU 2013234042B2
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amino acid
mannose
seq
polypeptide
molecular complex
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AU2013234042A1 (en
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Kathleen Camilla Telesphore Alida Maria Piens
Gwenda Noella Pynaert
Jan Robert Ludo Stout
Wouter Vervecken
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Oxyrane UK Ltd
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    • C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/01003—Glucan 1,4-alpha-glucosidase (3.2.1.3), i.e. glucoamylase
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    • A61K38/00—Medicinal preparations containing peptides
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    • A61K47/64—Drug-peptide, drug-protein or drug-polyamino acid conjugates, i.e. the modifying agent being a peptide, protein or polyamino acid which is covalently bonded or complexed to a therapeutically active agent
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    • C12N9/2405—Glucanases
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    • C12N9/14—Hydrolases (3)
    • C12N9/48—Hydrolases (3) acting on peptide bonds (3.4)
    • C12N9/50—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25)
    • C12N9/58—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25) derived from fungi
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    • C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/0102—Alpha-glucosidase (3.2.1.20)
    • A—HUMAN NECESSITIES
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    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C07K14/435—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • C07K14/575—Hormones
    • C07K14/65—Insulin-like growth factors, i.e. somatomedins, e.g. IGF-1, IGF-2
    • C—CHEMISTRY; METALLURGY
    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K2319/00—Fusion polypeptide
    • C07K2319/70—Fusion polypeptide containing domain for protein-protein interaction

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AU2013234042A 2012-03-15 2013-03-14 Methods and materials for treatment of Pompe's disease Ceased AU2013234042B2 (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261611485P 2012-03-15 2012-03-15
US61/611,485 2012-03-15
PCT/IB2013/000912 WO2013136189A2 (en) 2012-03-15 2013-03-14 Methods and materials for treatment of pompe's disease

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AU2013234042A1 AU2013234042A1 (en) 2014-10-23
AU2013234042B2 true AU2013234042B2 (en) 2017-11-02

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AU2013234042A Ceased AU2013234042B2 (en) 2012-03-15 2013-03-14 Methods and materials for treatment of Pompe's disease

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US (2) US9249399B2 (https=)
EP (2) EP3628326B1 (https=)
JP (1) JP6194324B2 (https=)
KR (2) KR102028228B1 (https=)
CN (1) CN104379162B (https=)
AU (1) AU2013234042B2 (https=)
BR (1) BR112014022624A2 (https=)
CA (1) CA2867237C (https=)
RU (1) RU2644258C2 (https=)
WO (1) WO2013136189A2 (https=)

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