TW202204624A - 用於治療丙酸血症之基因療法 - Google Patents
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| AU2017302013B2 (en) | 2016-07-29 | 2022-05-26 | The Regents Of The University Of California | Adeno-associated virus virions with variant capsid and methods of use thereof |
| KR102738752B1 (ko) * | 2016-12-30 | 2024-12-06 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 페닐케톤뇨증을 치료하기 위한 유전자 치료 |
| WO2018144709A2 (en) * | 2017-02-01 | 2018-08-09 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating citrullenemia |
| EP3585883A4 (en) | 2017-02-21 | 2021-04-14 | University of Florida Research Foundation, Incorporated | MODIFIED AAV CAPSID PROTEINS AND USES THEREOF |
| WO2018222503A1 (en) | 2017-05-31 | 2018-12-06 | The Regents Of The University Of California | Adeno-associated virus with variant capsid and methods of use thereof |
| CA3065946A1 (en) | 2017-06-05 | 2018-12-13 | Research Institute At Nationwide Children's Hospital | Enhanced modified viral capsid proteins |
| IL276859B2 (en) | 2018-02-27 | 2025-12-01 | Univ Pennsylvania | Novel adeno-associated virus (aav) vectors, aav vectors having reduced capsid deamidation and uses therefor |
| BR112021006052A2 (pt) | 2018-10-01 | 2021-09-08 | Ultragenyx Pharmaceutical Inc. | Terapia gênica para tratar acidemia propiônica |
| JP2023514204A (ja) * | 2020-02-14 | 2023-04-05 | ウルトラジェニックス ファーマシューティカル インコーポレイテッド | Ｃｄｋｌ５欠損障害を処置するための遺伝子治療 |
-
2021
- 2021-03-30 WO PCT/US2021/024892 patent/WO2021202532A1/en not_active Ceased
- 2021-03-30 JP JP2022559589A patent/JP2023520402A/ja active Pending
- 2021-03-30 EP EP21721256.2A patent/EP4127189A1/en active Pending
- 2021-03-30 US US17/906,902 patent/US20230129893A1/en active Pending
- 2021-03-31 AR ARP210100811A patent/AR121709A1/es not_active Application Discontinuation
- 2021-03-31 TW TW110111870A patent/TW202204624A/zh unknown
Also Published As
| Publication number | Publication date |
|---|---|
| US20230129893A1 (en) | 2023-04-27 |
| WO2021202532A1 (en) | 2021-10-07 |
| EP4127189A1 (en) | 2023-02-08 |
| JP2023520402A (ja) | 2023-05-17 |
| AR121709A1 (es) | 2022-06-29 |
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